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Safety and Pharmacokinetics of Oral Controlled-ileocolonic-release Nicotinamide (CICR-NAM)

Registration Number
NCT05258474
Lead Sponsor
University Hospital Schleswig-Holstein
Brief Summary

Double-blind, randomised, placebo-controlled phase I trial with single-ascending and multiple-ascending dose to evaluate safety and pharmacokinetics of oral controlled-ileocolonic-release nicotinamide (CICR-NAM) compared to immediate-release nicotinamide and placebo in healthy subjects and in patients with inflammatory bowel diseases.

Detailed Description

Nicotinamide (NAM) has been implicated in the restoration and maintenance of a healthy gut microbiome. Conventional NAM formulations are designed for systemic NAM supplementation and therefore release NAM in the stomach and upper small intestine for maximum absorption. In contrast, the novel CICR-NAM tablets (controlled-ileocolonic-release nicotinamide) start releasing in the lower small intestine for topical delivery of NAM to the microbiota and the mucosa in the ileum and colon, also leading to a reduced systemic exposure. This clinical Phase I trial investigates the safety and tolerability of CICR-NAM in single- and multiple-ascending doses (1, 2 and 4 g). At the beginning of the trial, single-dose pharmacokinetics (PK) of 1 g of conventional immediate-release NAM and CICR-NAM are compared. At the end of the trial, patients with inflammatory bowel diseases (IBD) receive a medium multiple dose (2 g for 4 weeks) to compare their exposure, PK and safety data with those of healthy subjects at the same dose level.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
49
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
SEQUENTIAL
Arm && Interventions
GroupInterventionDescription
healthy subjectscontrolled-ileocolonic-release nicotinamide (SAD/MAD/MD)healthy subjects (single-ascending and multiple-ascending doses)
healthy subjectsPlacebo controlled-ileocolonic-release nicotinamide (SAD/MAD)healthy subjects (single-ascending and multiple-ascending doses)
IBD-patientscontrolled-ileocolonic-release nicotinamide (SAD/MAD/MD)inflammatory bowel disease patients (multiple dose)
healthy subjectsPlacebo Immediate-release nicotinamide (SAD)healthy subjects (single-ascending and multiple-ascending doses)
healthy subjectsImmediate-release nicotinamide (SAD)healthy subjects (single-ascending and multiple-ascending doses)
Primary Outcome Measures
NameTimeMethod
Blood ureaup to 60 days

Urea in mmol/L

Blood ALTup to 60 days

Alanine transaminase (ALT) in U/l

Haemoglobinup to 60 days

Haemoglobin (Hb) in %

Blood creatinineup to 60 days

Blood Creatinine in mmol/L

Treatment-Emergent Adverse Events [Safety and Tolerability]up to 60 days

Adverse Events (AEs) during treatment period

Glomerular filtration rateup to 60 days

Glomerular filtration rate (GFR, automatically calculated by the laboratory based on creatinine values) GFR in ml/min/1.73m2

Blood uric acidup to 60 days

Uric acid in mmol/L

Treatment-Emergent Serious Adverse Events [Safety and Tolerability]up to 60 days

Serious Adverse Events (SAEs) during treatment period

White blood cellsup to 60 days

White blood cell (WBC) count as x10\^9/l

Blood ASTup to 60 days

Aspartate transaminase (AST) in U/l

Blood GGTup to 60 days

Gamma glutamyl transferase (GGT) in U/l

Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (1)

University Medical Center Schleswig-Holstein

🇩🇪

Kiel, Germany

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