MedPath

Safety and Tolerability of A3907 in Primary Sclerosing Cholangitis

Phase 2
Active, not recruiting
Conditions
Primary Sclerosing Cholangitis
Interventions
Registration Number
NCT05642468
Lead Sponsor
Albireo, an Ipsen Company
Brief Summary

This study will test a drug called A3907 to see how safe and tolerated it is for treating people with Primary Sclerosing Cholangitis (PSC).

Detailed Description

This study will test a drug called A3907 to see how safe and tolerated it is for treating people with Primary Sclerosing Cholangitis (PSC). Detailed Description: The primary goal of this study in participants with PSC with and without a Clinically Relevant Stricture (CRS) who are treated with A3907 is to assess the safety and tolerability of A3907 following repeat doses. Secondary goals include evaluation of the pharmacokinetic properties of A3907 (the study of how the body interacts with A3907 for the entire duration of exposure) and changes in safety parameters via laboratory testing such as liver enzymes, bile acid levels and markers of bile acid synthesis

Recruitment & Eligibility

Status
ACTIVE_NOT_RECRUITING
Sex
All
Target Recruitment
18
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
30 mg (Arm 2)Ritivixibat30mg (3x10 mg tablets) A3907 administered orally once daily for 12 weeks.
30 mg BID (Arm 3)Ritivixibat30mg (3x10 mg tablets) A3907 administered orally Bi-daily for 12 weeks.
30 mg BID for CRS (Arm 4)Ritivixibat30mg (3x10 mg tablets) A3907 administered orally Bi-daily for 12 weeks.
10 mg (Arm 1)Ritivixibat10mg tablet A3907 administered orally once daily for 12 weeks.
Primary Outcome Measures
NameTimeMethod
Treatment related adverse eventsFrom baseline through week 12

Number of participants with treatment related adverse events as assessed by CTCAE v 5.0

Secondary Outcome Measures
NameTimeMethod
Maximum observed plasma concentration and Area under the Plasma Concentration versus Time Curve (AUC) of A3907From baseline through week 12
Change in serum and urine individual and total bile acid levelsFrom baseline through week 12

Measurement to see change in serum and urine individual and total bile acid levels

Change in ALT, AST, gamma-glutamyltransferase (GGT), ALP and bilirubin levelsFrom baseline through week 12

Measurement to see change in ALT, AST, gamma-glutamyltransferase (GGT), ALP and bilirubin levels

Change in serum C4 levelFrom baseline through week 12

Measurement to see change in 7α-hydroxy-4-cholesten-3-one (C4) and fibroblast growth factor 19 (FGF-19)

Trial Locations

Locations (8)

Centrum Medyczne INTER-MED

🇵🇱

Częstochowa, Poland

Uniwersyteckie Centrum Kliniczne im. Prof. Kornela Gibinskiego

🇵🇱

Katowice, Poland

ID Clinic Arkadiusz Pisula

🇵🇱

Mysłowice, Poland

Hopital Saint Antoine

🇫🇷

Paris, France

ASST Grande Ospedale Metropolitano Niguarda

🇮🇹

Milan, Italy

ASST di Monza - Azienda Ospedaliera San Gerardo

🇮🇹

Monza, Italy

Azienda Ospedale Università Padova

🇮🇹

Padova, Italy

Hospital Clinic de Barcelona

🇪🇸

Barcelona, Spain

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