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Pharming Technologies B.V.

๐Ÿ‡ณ๐Ÿ‡ฑNetherlands
Ownership
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Employees
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Market Cap
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Website

Leniolisib for Immune Dysregulation in CVID

Phase 2
Recruiting
Conditions
Common Variable Immunodeficiency (CVID)
Interventions
First Posted Date
2025-03-26
Last Posted Date
2025-04-08
Lead Sponsor
Pharming Technologies B.V.
Target Recruit Count
20
Registration Number
NCT06897358
Locations
๐Ÿ‡บ๐Ÿ‡ธ

Lahey Hospital & Medical Center, Burlington, Massachusetts, United States

Leniolisib for Immune Dysregulation in PIDs

Phase 2
Recruiting
Conditions
Primary Immunodeficiency Disorders (PIDs)
Interventions
First Posted Date
2024-08-12
Last Posted Date
2024-11-12
Lead Sponsor
Pharming Technologies B.V.
Target Recruit Count
12
Registration Number
NCT06549114
Locations
๐Ÿ‡บ๐Ÿ‡ธ

National Institute of Health, Bethesda, Maryland, United States

An Open-Label Study to Assess the Safety & Efficacy of Leniolisib in Japanese Patients With APDS

Phase 3
Recruiting
Conditions
APDS Gene Mutation
Interventions
First Posted Date
2024-02-08
Last Posted Date
2024-02-08
Lead Sponsor
Pharming Technologies B.V.
Target Recruit Count
3
Registration Number
NCT06249997
Locations
๐Ÿ‡ฏ๐Ÿ‡ต

Hiroshima University Hospital, Hiroshima, Hiroshima City, Japan

๐Ÿ‡ฏ๐Ÿ‡ต

Tokyo Medical And Dental University Hospital, Tokyo, Bunkyo-ku, Japan

Pediatric Patients Aged 1 to 6 Years With APDS

Phase 3
Active, not recruiting
Conditions
APDS
Interventions
First Posted Date
2023-01-20
Last Posted Date
2025-04-23
Lead Sponsor
Pharming Technologies B.V.
Target Recruit Count
16
Registration Number
NCT05693129
Locations
๐Ÿ‡บ๐Ÿ‡ธ

University of California Los Angeles, Los Angeles, California, United States

๐Ÿ‡บ๐Ÿ‡ธ

National Institutes of Health, Bethesda, Maryland, United States

๐Ÿ‡บ๐Ÿ‡ธ

The University of North Carolina, Chapel Hill, North Carolina, United States

and more 7 locations

Pediatric Patients Aged 4 to 11 Years with APDS

Phase 3
Active, not recruiting
Conditions
APDS
Interventions
First Posted Date
2022-06-30
Last Posted Date
2025-03-12
Lead Sponsor
Pharming Technologies B.V.
Target Recruit Count
15
Registration Number
NCT05438407
Locations
๐Ÿ‡ฏ๐Ÿ‡ต

Institute of Science Tokyo Hospital, Tokyo, Japan

๐Ÿ‡ฏ๐Ÿ‡ต

Kyoto University Hospital, Kyoto, Japan

๐Ÿ‡บ๐Ÿ‡ธ

University of California Los Angeles, Los Angeles, California, United States

and more 4 locations

Prevention of Acute Kidney Injury in Patients With NSTEMI

Phase 2
Terminated
Conditions
Non-ST Elevation Myocardial Infarction (NSTEMI)
Interventions
Drug: conestat alfa or placebo
First Posted Date
2021-06-03
Last Posted Date
2024-04-03
Lead Sponsor
Pharming Technologies B.V.
Target Recruit Count
29
Registration Number
NCT04912141
Locations
๐Ÿ‡จ๐Ÿ‡ญ

Fondazione Istituto Cardiocentro Ticino, Lugano, Switzerland

๐Ÿ‡จ๐Ÿ‡ญ

University Hospital Geneva, Geneva, Switzerland

๐Ÿ‡จ๐Ÿ‡ญ

University Hospital Basel, Basel, Switzerland

and more 1 locations

Prevention of Severe SARS-CoV-2 Infection in Hospitalized Patients With COVID-19

Phase 2
Completed
Conditions
Confirmed Coronavirus Disease
Interventions
First Posted Date
2020-08-28
Last Posted Date
2024-02-16
Lead Sponsor
Pharming Technologies B.V.
Target Recruit Count
38
Registration Number
NCT04530136
Locations
๐Ÿ‡บ๐Ÿ‡ธ

Virtua Marlton Hospital, Marlton, New Jersey, United States

๐Ÿ‡บ๐Ÿ‡ธ

Virtua Voorhees Hospital, Voorhees, New Jersey, United States

๐Ÿ‡บ๐Ÿ‡ธ

Virtua Memorial Hospital, Mount Holly, New Jersey, United States

and more 1 locations

Patient Registry to Evaluate the Real-world Safety of Ruconestยฎ

Completed
Conditions
Hereditary Angioedema
Interventions
First Posted Date
2018-10-05
Last Posted Date
2024-04-05
Lead Sponsor
Pharming Technologies B.V.
Target Recruit Count
152
Registration Number
NCT03697187
Locations
๐Ÿ‡บ๐Ÿ‡ธ

The US Hereditary Angioedema Association, Fairfax, Virginia, United States

Extension to the Study of Efficacy of CDZ173 in Patients with APDS/PASLI

Phase 2
Terminated
Conditions
Activated PI3Kdelta Syndrome (APDS); PASLI Disease
Interventions
First Posted Date
2016-08-09
Last Posted Date
2025-03-12
Lead Sponsor
Pharming Technologies B.V.
Target Recruit Count
37
Registration Number
NCT02859727
Locations
๐Ÿ‡ท๐Ÿ‡บ

Pharming Investigative Site, Moscow, Russian Federation

A Phase 2 HAE Prophylaxis Study With Recombinant Human C1 Inhibitor

Phase 2
Completed
Conditions
Hereditary Angioedema
Interventions
Biological: Recombinant human C1 inhibitor
Other: Placebo
First Posted Date
2014-09-25
Last Posted Date
2017-12-08
Lead Sponsor
Pharming Technologies B.V.
Target Recruit Count
32
Registration Number
NCT02247739
Locations
๐Ÿ‡บ๐Ÿ‡ธ

Washington University Division of Allergy and Immunology, Saint Louis, Missouri, United States

๐Ÿ‡จ๐Ÿ‡ฟ

Faculty Hospital by St. Anna Brno, Department of clinical Immunology and Allergology, Brno, Czechia

๐Ÿ‡ฒ๐Ÿ‡ฐ

PHI University Clinic of Dermatology, Skopje, Macedonia, The Former Yugoslav Republic of

and more 7 locations
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