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A Safety Study of SGN-CD33A in AML Patients

Phase 1
Completed
Conditions
Acute Myelogenous Leukemia
Acute Myeloid Leukemia
Acute Promyelocytic Leukemia
Interventions
Registration Number
NCT01902329
Lead Sponsor
Seagen Inc.
Brief Summary

This study will examine the safety profile of vadastuximab talirine (SGN-CD33A) administered as a single agent and in combination with a hypomethylating agent (HMA). The main purpose of the study is to find the maximum tolerated dose (MTD, which is the highest dose that does not cause unacceptable side effects) of SGN-CD33A in patients with acute myeloid leukemia (AML). The MTD will be determined by observing the dose-limiting toxicities (the side effects that prevent further increases in dose) of SGN-CD33A. In addition, the pharmacokinetic profile and anti-leukemia activity of SGN-CD33A will be assessed.

Detailed Description

This study will explore SGN-CD33A as a monotherapy and in combination with a hypomethylating agent (HMA; i.e., azacitidine or decitabine). Initial study treatment with SGN-CD33A includes a maximum of 2 cycles of treatment for monotherapy and 4 cycles for combination cohorts. Patients who achieve documented CR or CRi (Monotherapy) or clinical benefit (Combination) during the first part of the study are eligible to continue treatment.

Additional monotherapy cohorts may include patients with relapsed acute promyelocytic leukemia, relapsed patients with nucleophosmin-1 gene mutation (absence of fms-like tyrosine kinase 3 mutation) (NPM1-mutated, FLT-3 wild type), alternate dosing schedules (fractionated dosing on Days 1 and 4), treatment naive patients with AML who declined intensive therapy, and patients who have relapsed after post-allogeneic stem cell transplant.

Patients in the combination cohort will be treated with azacitidine or decitabine per institutional practice prior to SGN-CD33A dosing. Expansion cohorts may be added for further evaluation of safety, pharmacokinetics, pharmacodynamics, and antitumor activity.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
195
Inclusion Criteria
  • Acute myeloid leukemia, positive for CD33
  • Eastern Cooperative Oncology Group status of 0 or 1
  • Adequate baseline renal and hepatic function
  • Central venous access
  • Either achieved complete remission (greater than 12 weeks in duration) with initial induction/consolidation and have experienced relapse of disease or declined treatment with high-dose induction/consolidation
  • Bone marrow blasts greater than or equal to 5% for relapsed patients, or greater than or equal to 20% for untreated patients
Exclusion Criteria
  • Inadequate lung function
  • Prior allogeneic stem cell transplant, except for a specific cohort
  • High-dose chemotherapy within 4 weeks of study drug
  • Antileukemia treatment within 14 days of study drug (other than hydroxyurea or 6-mercaptopurine)

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
SGN-CD33A + HMAHMASGN-CD33A with hypomethylating agent
SGN-CD33A + HMASGN-CD33ASGN-CD33A with hypomethylating agent
SGN-CD33A MonotherapySGN-CD33ASGN-CD33A
Primary Outcome Measures
NameTimeMethod
Incidence of adverse eventsThrough 1 month following last dose
Incidence of laboratory abnormalitiesThrough 1 month following last dose
Secondary Outcome Measures
NameTimeMethod
Rate of complete remissionUp to 3 months
Incidence of antitherapeutic antibodiesThrough 1 month following last dose
Relapse-free survivalUp to approximately 3 years
Overall survivalUp to approximately 3 years
Blood concentrations of SGN-CD33A and metabolitesThrough 3 weeks after dosing
Duration of complete remissionUp to approximately 3 years

Trial Locations

Locations (14)

Winship Cancer Institute / Emory University School of Medicine

🇺🇸

Atlanta, Georgia, United States

Massachusetts General Hospital

🇺🇸

Boston, Massachusetts, United States

Dana Farber Cancer Institute

🇺🇸

Boston, Massachusetts, United States

Fred Hutchinson Cancer Research Center

🇺🇸

Seattle, Washington, United States

MD Anderson Cancer Center / University of Texas

🇺🇸

Houston, Texas, United States

University of Alabama at Birmingham

🇺🇸

Birmingham, Alabama, United States

H. Lee Moffitt Cancer Center & Research Institute

🇺🇸

Tampa, Florida, United States

City of Hope National Medical Center

🇺🇸

Duarte, California, United States

Memorial Sloan Kettering Cancer Center

🇺🇸

New York, New York, United States

University of Michigan Comprehensive Cancer Center

🇺🇸

Ann Arbor, Michigan, United States

Hackensack University Medical Center

🇺🇸

Hackensack, New Jersey, United States

Cleveland Clinic, The

🇺🇸

Cleveland, Ohio, United States

Charles A. Sammons Cancer Center / Baylor University Medical Center

🇺🇸

Dallas, Texas, United States

University of Utah

🇺🇸

Salt Lake City, Utah, United States

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