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Changes in Myocardial Iron After Iron Administration

Phase 4
Completed
Conditions
Iron-deficiency
Heart Failure
Interventions
Drug: Ferric carboymaltose
Drug: Placebo (Normal saline)
Diagnostic Test: Cardiac magnetic resonance
Registration Number
NCT03398681
Lead Sponsor
Fundación para la Investigación del Hospital Clínico de Valencia
Brief Summary

Recent studies have shown that treatment with intravenous iron in patients with iron deficiency (ID) and heart failure with reduced ejection fraction (HFrEF) improves symptomatology, functional capacity, quality of life, and decreases hospitalizations regardless of anemia. In addition, a decrease in myocardial iron content has been observed in patients with chronic HFrEF. This preliminary evidence has led to postulate that myocardial iron deficiency could play a direct role in the pathogenesis and progression of the disease.

The investigators hypothesize that the repletion of myocardial iron would explain part of the benefit of this treatment. Thus, the investigators postulate that cardiac magnetic resonance (CMR) (T2\* and T1-mapping sequences) will be sensible enough to detect changes in myocardial iron content as a result of intravenous iron administration, and that such changes will correlate with simultaneous changes in parameters of heart failure severity.

In this double-blind 1:1 randomized study controlled by placebo the investigators aim to determine the changes in myocardial iron content after treatment with intravenous ferric carboxymaltose (FCM) by CMR at 7 and 30 days in patients with stable HFrEF and ID.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
53
Inclusion Criteria
  • Patients with ambulatory chronic heart failure
  • Older than 18 years
  • Patients in NYHA class II-III on optimal background therapy (as determined by the investigator) for at least 4 weeks with no dose changes of HF drugs during the last 2 weeks (with the exception of diuretics)
  • Elevated natriuretic peptides levels (NT-proBNP >400 pg/ml) at the screening visit
  • Left ventricle ejection fraction <50% documented in the last 12 months
  • Iron deficiency defined as: serum ferritin level <100 μg/L or ferritin level 100-299 μg/L when TSAT is less than 20%, and hemoglobin <15 g/dL (all at screening)
  • Participant is willing and able to give informed consent for participation in the study
Exclusion Criteria
  • Known sensitivity to any of the products to be administered per protocol.
  • History of acquired iron overload.
  • Severe valve disease, or being scheduled for cardiac surgery within the next 30 days.
  • Acute myocardial infarction or acute coronary syndrome, transient ischemic attack, or stroke within the last 3 months prior to randomization.
  • Coronary artery bypass graft, percutaneous intervention (e.g. cardiac, cerebrovascular, and aortic; diagnostic catheters are allowed), or major surgery, including thoracic and cardiac surgery, within the last 3 months prior to randomization.
  • Ischemic heart disease scheduled for revascularization procedures within the next 30 days.
  • HF scheduled for cardiac resynchronization therapy within the next 30 days.
  • Patients with active bleeding in the last 30 days.
  • Known active infection or active malignancy.
  • Subject at an immediate need of transfusion or hemoglobin ≥15 g/dL.
  • Anemia due to reasons other than iron deficiency
  • Immunosuppressive therapy or renal dialysis
  • History of erythropoietin, intravenous iron therapy, and blood transfusion in the previous 12 weeks.
  • Oral iron therapy at doses >100 mg/day in previous 1 week prior to randomization.
  • Subjects with an immediate need for transfusion.
  • Pregnant or breastfeeding women.
  • Subject of childbearing potential who is not willing to use adequate contraceptive precautions during the study and for up to 5 days after the last scheduled dose of study medication.
  • Subject currently enrolled in or has not yet completed at least 30 days since ending other investigational device or drug study, or subject is receiving other investigational agent(s).
  • Any kind of disorder that compromises the ability of the subject to give written informed consent and/or to comply with study procedures.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Intravenous ferric carboxymaltoseCardiac magnetic resonanceFerric Carboxymaltose solution \[Ferinject® (FCM), Vifor Pharma (Glattbrugg, Switzerland)\] will be given as a perfusion of 20 mL (which is the amount of FCM that is equivalent to 1000 mg of iron) diluted in a sterile saline solution (0.9% weight/volume (w/v) NaCl) administered over at least 15 min.
Intravenous ferric carboxymaltoseFerric carboymaltoseFerric Carboxymaltose solution \[Ferinject® (FCM), Vifor Pharma (Glattbrugg, Switzerland)\] will be given as a perfusion of 20 mL (which is the amount of FCM that is equivalent to 1000 mg of iron) diluted in a sterile saline solution (0.9% weight/volume (w/v) NaCl) administered over at least 15 min.
Normal salinePlacebo (Normal saline)Normal saline (0.9% weight/volume (w/v) NaCl) administered as per the instructions for active therapy.
Normal salineCardiac magnetic resonanceNormal saline (0.9% weight/volume (w/v) NaCl) administered as per the instructions for active therapy.
Primary Outcome Measures
NameTimeMethod
Changes in myocardial iron content assessed by CMR T2*7 and 30 days
Changes in myocardial iron content assessed by CMR T1-mapping7 and 30 days
Secondary Outcome Measures
NameTimeMethod
Clinical events: time to first hospitalization for any cardiovascular reason.30 days

Time to first hospitalization for any cardiovascular reason.

Clinical events: time to first hospitalization due to worsening heart failure.30 days

Time to first hospitalization due to worsening heart failure.

Serum creatinine30 days

Laboratory tests: serum creatinine

Hepcidin30 days

Laboratory tests: hepcidin.

Urea30 days

Laboratory tests: urea

Changes in left ventricular systolic function evaluated with cardiac magnetic resonance7 and 30 days

Changes in left ventricular systolic function evaluated with cardiac magnetic resonance

6-minute walking test7 and 30 days

Changes in functional capacity assessed by distance walked in 6 minutes (6-minute walking test)

New York Heart Association (NYHA) class.7 and 30 days

Changes in functional capacity assessed by New York Heart Association (NYHA) class.

The Kansas City quality of life questionnaire (KCCQ)7 and 30 days

Quality of life assessed by The Kansas City quality of life questionnaire (KCCQ). KCCQ is a 23-item, self-administered instrument that quantifies physical function, symptoms (frequency, severity and recent change), social function, self-efficacy and knowledge, and quality of life. Scores are transformed to a range of 0-100, in which higher scores reflect better health status.

Antigen carbohydrate 125 (CA125)30 days

Laboratory tests, biomarkers: antigen carbohydrate 125 (CA125)

Amino-terminal pro-brain natriuretic peptide (NT-proBNP)30 days

Laboratory tests, biomarkers: amino-terminal pro-brain natriuretic peptide (NT-proBNP)

Galectin-330 days

Laboratory tests, biomarkers: galectin-3

ST-230 days

Laboratory tests, biomarkers: ST-2

High-sensitivity troponin (hsTnT)30 days

Laboratory tests, biomarkers: high-sensitivity troponin (hsTnT)

Cystatin C30 days

Laboratory tests, biomarkers: cystatin C

Hemoglobin30 days

Laboratory tests: hemoglobin

Neutrophil gelatinase-associated lipocalin (NGAL)30 days

Laboratory tests, biomarkers: neutrophil gelatinase-associated lipocalin (NGAL)

Ferritin30 days

Laboratory tests: ferritin

soluble transferrin receptor (sTfR)30 days

Laboratory tests: soluble transferrin receptor (sTfR)

Estimated glomerular filtration rate (eGFR)30 days

Laboratory tests: estimated glomerular filtration rate (eGFR)

Transferrin saturation (TSAT)30 days

Laboratory tests: transferrin saturation (TSAT)

Clinical events: all-cause hospitalizations30 days

All-cause hospitalizations

Clinical events: cardiovascular hospitalizations.30 days

Cardiovascular hospitalizations

Clinical events: heart failure hospitalizations.30 days

Heart failure hospitalizations

Clinical events: time to first hospitalization for any reason.30 days

Time to first hospitalization for any reason.

Trial Locations

Locations (6)

Hospital General de Valencia

🇪🇸

Valencia, Spain

Hospital General de Castellón

🇪🇸

Castellón De La Plana, Castellón, Spain

Hospital de Manises

🇪🇸

Manises, Valencia, Spain

ERESA

🇪🇸

Valencia, Spain

Hospital la Fe

🇪🇸

Valencia, Spain

Fundación Investigación Hospital Clínico Universitario de Valencia. Instituto de Investigación Sanitaria INCLIVA.

🇪🇸

Valencia, Spain

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