MedPath

REGISTRY - an Observational Study of the European Huntington's Disease Network (EHDN)

Completed
Conditions
Huntington Disease
Huntington's Disease
Registration Number
NCT01590589
Lead Sponsor
European Huntington's Disease Network
Brief Summary

This is a multi-centre, multi-national, prospective, observational study of Huntington's disease (HD) with a control group of volunteers to:

* obtain natural history data on many HD mutation carriers and individuals who are part of an HD family

* relate phenotypical characteristics (genetic modifiers / wet and dry biomarkers)

* expedite identification and recruitment of participants for clinical trials

* develop and validate sensitive and reliable outcome measures for detecting onset and change over the natural course of premanifest and manifest HD which may also be potential outcome measures for use in future clinical trials and clinical care

* plan for future research studies

Detailed Description

REGISTRY integrates prospectively and systematically collected clinical research data (e.g. phenotypical clinical features, family history, demographical characteristics) with access to biological specimens (e.g. blood, urine) obtained from individuals with manifest HD, unaffected individuals known to carry the HD mutation or at risk of carrying the HD mutation, and control research participants (e.g. spouses, siblings or offspring of HD mutation carriers known not to carry the HD mutation).

REGISTRY is an open-ended study and eligible subjects are assessed at annual study visits on the phenotypical characteristics of HD regardless of whether they display clinical symptoms and signs of the disease and of individuals who are part of an HD family (irrespective of their mutation carrier status). At each study visit, general clinical, motor function, behavior, cognitive, Health Economics, Quality of Life assessments are administered. In addition, participants are given the option to consent to the donation of biosamples for the purposes of mutation (CAG repeat length) testing and for research to identify biological modifiers and markers of HD. Biological specimens and phenotypical data are made available to qualified scientists whose projects are reviewed and approved by the Scientific and Bioethical Advisory Committee (SBAC) of EHDN. Successful applicants agree to accept the EHDN policies surrounding the use of the data/materials provided and publication of results (see data sharing and publication policies of EHDN, attached). Research projects should aim to advance scientific knowledge towards establishing clinically effective treatments that delay onset and/or slow the progression of the disease.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
10000
Inclusion Criteria

The following individuals may be eligible to participate

  • Individuals, confirmed HD mutation carrier
  • Manifest HD, without mutation (CAG) testing
  • HD family member at-risk, without CAG testing
  • HD family member, non-HD mutation carrier
  • REGISTRY-CONTROL participants: companion/individual without HD history
  • REGISTRY-COMPANION (any of the above).
Exclusion Criteria
  • Participants who are unable to understand the study protocol or unable to give informed consent, and have no legal representative.
  • Participants with choreic movement disorder other than HD. (EHDN provides a Registry-like tool to record findings in patients affected with choreatic movement disorders other than HD under the label "Neuroacanthocytosis"; www.euro-hd.net/html/na/registry).

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Phenotypical characteristics of HD13 years

The goal of the project is to collect longitudinal data on the phenotypical characteristics of HD gene mutation carriers.

Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (140)

CHU Rouen Charles Nicolle, Service de Neurologie

🇫🇷

Rouen cedex, France

Hôpital Civil, Service de Neurologie

🇫🇷

Strasbourg cedex, France

Hôpital Purpan, INSERM U825, Pôle Neurosciences

🇫🇷

Toulouse cedex 03, France

Ruhruniversität Bochum, Neurologie

🇩🇪

Bochum, Germany

Universitätsklinikum Freiburg, Neurologie

🇩🇪

Freiburg, Germany

Universitätsklinikum Aachen, Neurologische Klinik

🇩🇪

Aachen, Germany

Praxis

🇩🇪

Marburg, Germany

Charité - Universitätsmedizin Berlin, Klinik und Poliklinik für Neurologie, Klinik für Psychiatrie und Psychotherapie

🇩🇪

Berlin, Germany

Psychatrium Gruppe AöR, Haus 2/1

🇩🇪

Heiligenhafen, Germany

Schwerpunktpraxis Huntington, Neurologie-Psychiatrie

🇩🇪

Itzehoe, Germany

Isar-Amper-Klinikum - Klinik Taufkirchen (Vils)

🇩🇪

Taufkirchen, Germany

University Hospital of Ulm, Dept. of Neurology

🇩🇪

Ulm, Germany

University of Bari, Dept. of Neurological and Psychiatric Sciences

🇮🇹

Bari, Italy

Università di Genova, Dept. of Neurosciences

🇮🇹

Genova, Italy

Università di Napoli Federico II, Dip. Scienze Neurologiche Edificio 17

🇮🇹

Napoli, Italy

Università Cattolica del Sacro Cuore "A.Gemelli", Istituto di Neurologia / CNR, Istituto di Farmacologia Traslazionale

🇮🇹

Rome, Italy

University of Florence, Dip. di Scienze Neurologiche e Psichiatriche

🇮🇹

Florence, Italy

Fondazione IRCCS Istituto Neurologico Carlo Besta, I Neurologia

🇮🇹

Milano, Italy

IRCCS Neuromed, U.O. Neurogenetica

🇮🇹

Pozzilli (IS), Italy

UMC Groningen, Neurology

🇳🇱

Groningen, Netherlands

Medisch Spectrum Twente, Dept. of Neurology

🇳🇱

Enschede, Netherlands

NKS Olaviken Alderpsykiatriske sykehus, Poliklinikk og Huntington Klinikk

🇳🇴

Bergen, Norway

Leiden University Medical Centre (LUMC), Neurology K5-Q

🇳🇱

Leiden, Netherlands

MUMC, Dept. Neurology

🇳🇱

Maastricht, Netherlands

Rikshospitalet, Dept. of Medical Genetics

🇳🇴

Oslo, Norway

St. Olavs Hospital HF, Neurology

🇳🇴

Trondheim, Norway

Specialistic Hospital in Gdansk, Dept. of Neurology

🇵🇱

Gdansk, Poland

Medical University of Warsaw, Dept. of Neurology

🇵🇱

Warsaw, Poland

Institute of Psychiatry and Neurology, First Dept. of Neurology

🇵🇱

Warsaw, Poland

Hospital dos Capuchos, Centro Hospitalar Lisboa Central, Neurology Dept.

🇵🇹

Lisbon, Portugal

Hospital de São João, Neurology Dept.

🇵🇹

Porto, Portugal

Poznan University of Medical Sciences, Dept. of Social Medicine

🇵🇱

Poznan, Poland

Centro Hospitalar de Trás-os-Montes e Alto Douro, Neurology Dept.

🇵🇹

Vila Real, Portugal

Hospital Bellvitge, Neurología

🇪🇸

Barcelona, Spain

Hospital de Coimbra, Neurology Dept.

🇵🇹

Coimbra, Portugal

Hospital Infanta Cristina, Neurología

🇪🇸

Badajoz, Spain

Huntington's Disease Society of Russia

🇷🇺

Moscow, Russian Federation

Hospital Fernando Fonseca, Neurology Dept.

🇵🇹

Lisbon, Portugal

Hospital Son Dureta, Neurology

🇪🇸

Palma de Mallorca, Spain

Hospital Clínico de Madrid, Servicio de Neurología

🇪🇸

Madrid, Spain

Hospital de Fuenlabrada, Neurology

🇪🇸

Madrid, Spain

Centro Ramón y Cajal, Neurología

🇪🇸

Madrid, Spain

Hospital Virgen de la Arrixaca, Neurology

🇪🇸

Murcia, Spain

Hospital Vall d'Hebrón, Neurología, 3ª planta, consultas externas

🇪🇸

Barcelona, Spain

Hospital Clínic i Provincial, Neurología

🇪🇸

Barcelona, Spain

Fundación Jiménez Díaz, Neurology

🇪🇸

Madrid, Spain

Hospital Central de Oviedo, Neurología

🇪🇸

Oviedo, Spain

Hospital Virgen del Camino, Medical Genetics

🇪🇸

Pamplona, Spain

Hospital Universitario Virgen del Rocío, Servicio de Neurología

🇪🇸

Sevilla, Spain

Hospital Virgen de la Salud, Neurology

🇪🇸

Toledo, Spain

Hospital La Fe, Consultas Externas de Neurología

🇪🇸

Valencia, Spain

Hospital Donostia. Universidad del Pais Vasco, Neurociencias

🇪🇸

San Sebastián, Spain

Hospital Virgen Macarena, Neurología

🇪🇸

Sevilla, Spain

Hospital Clinico Universario, Department of Neurology

🇪🇸

Zaragoza, Spain

Sahlgren University Hospital, Dept. of Clinical Genetics

🇸🇪

Göteborg, Sweden

Neuroenheten Utsikten

🇸🇪

Stockholm, Sweden

The Barberry Centre, Dept. of Psychiatry

🇬🇧

Birmingham, United Kingdom

Frenchay Hospital, Neurology Dept.

🇬🇧

Bristol, United Kingdom

Scottish Huntington Association, Units 105/106

🇬🇧

Glasgow, United Kingdom

Leicestershire Partnership NHS Trust, EMD South School, OSL house

🇬🇧

Leicester, United Kingdom

Guy's Hospital, Dept. of Neurology

🇬🇧

London, United Kingdom

Centrum extrapyramidových onemocnění, Neurologická klinika, 1. LFUK

🇨🇿

Praha 2, Czechia

Hôpital La Pitié Salpétrière, Génétique & Inserm U679

🇫🇷

Paris, France

CHU d'Angers, Service de Neurologie Charcot

🇫🇷

Angers cedex 9, France

The Finnish Parkinson Association, Suvituuli

🇫🇮

Turku, Finland

Clinique Neurologique Hôpital Roger Salengro CHRU, Neurologie et Pathologie du Mouvement

🇫🇷

Lille cedex, France

Universitätsklinik Innsbruck, Neurologie

🇦🇹

Innsbruck, Austria

Turku University Hospital, Dept. of Neurology

🇫🇮

Turku, Finland

Hôpital Henri Mondor, Service de Neurologie

🇫🇷

Créteil cedex, France

CHU La Timone, Service de Neurologie (9e étage)

🇫🇷

Marseille cedex 5, France

Reha-Zentrum Dinslaken im Gesundheitszentrum Lang, Tagesklinik

🇩🇪

Dinslaken, Germany

Universtität Erlangen, Abteilung für Molekulare Neurologie

🇩🇪

Erlangen, Germany

Neurologische Klinik mit Klinischer Neurophysiologie, Medizinische Hochschule Hannover

🇩🇪

Hannover, Germany

Universität Marburg, Neurologie

🇩🇪

Marburg, Germany

Technische Universität München, Abteilung Neurologie

🇩🇪

München, Germany

Azienda Ospedaliera Spedali Civili di Brescia, Clinica Neurologica

🇮🇹

Brescia, Italy

Azienda Ospedaliera Universitarie Pisana, Dip. di Neuroscienze - UO Neurologia

🇮🇹

Pisa, Italy

Krakowska Akademia Neurologii

🇵🇱

Krakow, Poland

Universitätsklinikum Hamburg-Eppendorf, Neurologische Abteilung

🇩🇪

Hamburg, Germany

UCL-St Luc, Centre de génétique humaine

🇧🇪

Brussels, Belgium

Universitair Ziekenhuis Gasthuisberg, Dienst Neurologie

🇧🇪

Leuven, Belgium

University Hospital of Copenhagen - Rigshospitalet, Dept. of Neurology

🇩🇰

Copenhagen Ø, Denmark

The Family Federation of Finland Väestöliitto, Department of Medical Genetics

🇫🇮

Helsinki, Finland

Kuopio University Hospital, Neurology

🇫🇮

Kuopio, Finland

Ålands Hälso- och Sjukvård, Långvårdsenheten

🇫🇮

Mariehamn, Finland

Suomen Terveystalo

🇫🇮

Tampere, Finland

CHU d'Amiens - Hôpital Nord, Service de Neurologie

🇫🇷

Amiens cedex, France

Complejo Hospitalario Universitario de Albacete, Neurología

🇪🇸

Albacete, Spain

Universitätsklinik für Psychiatrie, Neuropsychiatrische Ambulanz

🇦🇹

Graz, Austria

Institute of Pathology and Genetics (IPG)

🇧🇪

Gosselies, Belgium

Hôpital Pellegrin, Service de Génétique Médicale (ESF 3e étage)

🇫🇷

Bordeaux cedex, France

HU Clermont-Ferrand - Hôpital Gabriel Montpied, Service de Neurologie

🇫🇷

Clermont-Ferrand, France

Fakultní nemocnice Olomouc, Neurologická klinika

🇨🇿

Olomouc, Czechia

Helsinki University Hospital, Dept. of Neurology

🇫🇮

HUS, Finland

Oulu University Hospital (OUH), Dept. of Neurology

🇫🇮

Oulu, Finland

Universitätsklinikum Carl Gustav Carus an der Technischen Universität Dresden, Klinik und Poliklinik für Neurologie

🇩🇪

Dresden, Germany

Universitätsklinikum Münster, Klinik und Poliklinik für Neurologie

🇩🇪

Münster, Germany

Università di Bologna, Dip. di Scienze Neurologiche - Clinica Neurologica

🇮🇹

Bologna, Italy

Azienda Ospedaliera S. Andrea, UOC Neurologia e Centro Neurologico Terapie Sperimentali CENTERS

🇮🇹

Rome, Italy

Ulleval University Hospital, Medical Genetics

🇳🇴

Oslo, Norway

Medical University of Silesia, Dept. of Neurology

🇵🇱

Katowice, Poland

Hospital de Santa Maria, Centro de Estudos Egas Moniz, Neurology Dept.

🇵🇹

Lisbon, Portugal

Hospital Geral de Santo António, Neurology Dept.

🇵🇹

Porto, Portugal

Fondazione IRCCS Istituto Neruologico Carlo Besta, SOSD Genetics of Neurodegenerative and Metabolic Diseases

🇮🇹

Milano, Italy

Hospital General Yagüe, Neurology

🇪🇸

Burgos, Spain

Hospital General de Segovia, Neurología

🇪🇸

Segovia, Spain

Skåne Universitetssjukhus, Neurologiska kliniken

🇸🇪

Lund, Sweden

Uppsala University Hospital, Neurology

🇸🇪

Uppsala, Sweden

Neurologische Klinik des Inselspitals, Praxis

🇨🇭

Bern, Switzerland

University Hospital Zurich, Dept. of Neurology

🇨🇭

Zurich, Switzerland

Clinical Genetics Centre, Ground Floor, Ashgrove House

🇬🇧

Aberdeen, United Kingdom

Queen Margaret Hospital

🇬🇧

Fife, United Kingdom

Chapel Allerton Hospital, Yorkshire Regional Genetics Service

🇬🇧

Hull, United Kingdom

The Walton Centre for Neurology and Neurosurgery

🇬🇧

Liverpool, United Kingdom

Churchill Hospital, Dept. of Clinical Genetics

🇬🇧

Oxford, United Kingdom

Southampton General Hospital and University of Southampton, Neurology / Wellcome Trust Clinical Research Facility

🇬🇧

Southampton, United Kingdom

Bucknall Hospital, Neuropsychiatry Service

🇬🇧

Stoke-on-Trent, United Kingdom

Victoria Centre

🇬🇧

Swindon, United Kingdom

St George's Hospital Medical School, South West Thames Regional Genetics Unit

🇬🇧

London, United Kingdom

Chapel Allerton Hospital

🇬🇧

Leeds, United Kingdom

Hospital Puerta del Mar, Neurología

🇪🇸

Cádiz, Spain

Hospital Universitario Mutua de Terrassa, Neurologia - Investigación

🇪🇸

Terrassa - Barcelona, Spain

Norrlands Universitet Sjukhus, Dept. of Neurology

🇸🇪

Umeå, Sweden

Blandford Hospital

🇬🇧

Blandford Forum, United Kingdom

Cardiff University, Life Sciences Building

🇬🇧

Cardiff, United Kingdom

Royal Devon and Exeter Foundation Trust Hospital, Department of Neurology

🇬🇧

Exeter, United Kingdom

Gloucestershire Royal Hospital, Neurology Dept.

🇬🇧

Gloucester, United Kingdom

Derriford Hospital, Dept. of Clinical Neuropsychology

🇬🇧

Plymouth, United Kingdom

Poole Hospital Foundation Trust, Brain Injury Service

🇬🇧

Poole, United Kingdom

Karolinska University Hospital - Huddinge Division, Neurology

🇸🇪

Stockholm, Sweden

CHUV - Centre Hospitalier Universitaire Vaudois, Département de Neurologie

🇨🇭

Lausanne, Switzerland

Cambridge Centre for Brain Repair, Forvie Site

🇬🇧

Cambridge, United Kingdom

Ninewells Hospital and Medical School, Human Genetics Unit

🇬🇧

Dundee, United Kingdom

Lancashire Teaching Hospitals NHS Foundation Trust, Neurosciences Directorate, Royal Preston Hospital

🇬🇧

Preston, United Kingdom

Sheffield Children's Hospital, Dept. of Clinical Genetics

🇬🇧

Sheffield, United Kingdom

University of Manchester, Genetic Medicine, St. Mary's Hospital

🇬🇧

Manchester, United Kingdom

Molecular Medicine Centre, Western General Hospital, Dept. of Clinical Genetics

🇬🇧

Edinburgh, United Kingdom

The Royal Hospital for Neuro-disability, Research and Development

🇬🇧

London, United Kingdom

Institute of Human Genetics, International Centre for Life

🇬🇧

Newcastle upon Tyne, United Kingdom

National Hospital for Neurology and Neurosurgery, Dept. for Neurology

🇬🇧

London, United Kingdom

© Copyright 2025. All Rights Reserved by MedPath