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Stop study.

Conditions
haemophilia, prophylaxis, adherence, bleeds, arthropathy.hemofilie, profylaxe, therapietrouw, bloedingen, arthropathie.
Registration Number
NL-OMON25201
Lead Sponsor
niversity Medical Center Utrecht (UMC Utrecht)
Brief Summary

/A

Detailed Description

Not available

Recruitment & Eligibility

Status
Pending
Sex
Not specified
Target Recruitment
90
Inclusion Criteria

1. Severe haemophilia A (factor VIII < 0.01 IU/ml);

2. Born between January 1st 1970 and January 1st 1988;

Exclusion Criteria

1. History of inhibitory activity of more than 5 BU at any time or less than 5 BU for more than one year;

2. Inadequate access to treatment during the first years of life (i.e. no access to unlimited replacement therapy during the first 4 years of life, e.g. in case of immigration);

Study & Design

Study Type
Observational non invasive
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
1. Joint status according to Haemophilia Joint Health Score (HJHS) and Pettersson score;<br /><br>2. Annual number of joint bleeds;<br /><br>3. Figure 8 walk test.
Secondary Outcome Measures
NameTimeMethod
1. Clotting factor consumption;<br /><br>2. Orthopaedic surgery;<br /><br>3. Hospital admissions in the third decade of life;<br /><br>4. Major soft tissue bleeds.
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