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Comparison of Prophylaxis and On-demand Treatment in Children With Moderate to Severe Hemophilia A

Not Applicable
Completed
Conditions
Hemophilia A
Prophylaxis
Interventions
Other: prophylaxis treatment, on demand treatment
Registration Number
NCT02362581
Lead Sponsor
Chulalongkorn University
Brief Summary

Comparison of prophylaxis and on-demand treatment in children with moderate to severe hemophilia A.

This study determines to compare the efficacy of prophylaxis and on-demand treatment in moderate to severe hemophilia A children in King Chulalongkorn Memorial Hospital, Bangkok, Thailand

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
15
Inclusion Criteria
  • Age between 6 months to 18 years
  • Diagnosis severe and moderate hemophilia A
Exclusion Criteria
  • platelet < 100,000/mm3
  • No factor VIII inhibitor

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
On demand treatment, prophylaxis treatmentprophylaxis treatment, on demand treatmentOn demand treatment arm:Patients received factorVIII concentrate(Hemofil M) when they had bleeding episodes. Prophylaxis arm: patients received factorVIII concentrate (Hemofil M) 30-35 unit/kg once a week
Primary Outcome Measures
NameTimeMethod
Number of admission daysone year
Number of bleeding episodes require treatmentone year
number of school days lostone year
Secondary Outcome Measures
NameTimeMethod
Joint scoresone year
Amount of Facter VIII concentration usedone year
Quality of life scoreone year

Trial Locations

Locations (1)

pediatric Hemato-oncology department, King Chulalongkorn Memorial Hospital

🇹🇭

Pratumwan, Bangkok, Thailand

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