MedPath

Combination Chemotherapy With or Without Bone Marrow Transplantation in Treating Patients With Acute Promyelocytic Leukemia

Phase 3
Conditions
Leukemia
Registration Number
NCT00002701
Lead Sponsor
European Organisation for Research and Treatment of Cancer - EORTC
Brief Summary

RATIONALE: Drugs used in chemotherapy use different ways to stop cancer cells from dividing so they stop growing or die. Bone marrow transplantation may be able to replace immune cells that were destroyed by chemotherapy to kill tumor cells. It is not yet known which regimen of combination chemotherapy with or without bone marrow transplantation is more effective in treating promyelocytic leukemia

PURPOSE: Randomized phase III trial to compare the effectiveness of different combination chemotherapy regimens with or without bone marrow transplantation in treating patients who have promyelocytic leukemia.

Detailed Description

OBJECTIVES:

* Determine the complete remission (CR) rate in patients with acute promyelocytic leukemia treated with induction comprising tretinoin (ATRA) and idarubicin (IDA).

* Determine the presence of the promyelocyte-retinoic acid receptor alpha (PML-RARa) transcript using polymerase chain reaction (PCR) in patients with CR after 3 sequential consolidation regimens comprising cytarabine (ARA-C) plus IDA, followed by mitoxantrone plus etoposide, and then IDA, ARA-C, and thioguanine.

* Determine the percentage of patients who complete the protocol, including PML-RARa-positive patients treated with post-consolidation bone marrow transplantation (BMT) and PML-RARa-negative patients treated with maintenance comprising mercaptopurine (MP) plus methotrexate (MTX) vs ATRA only vs MP plus MTX alternating with ATRA vs observation only.

* Compare the disease-free survival (DFS) and overall survival of these patients treated with these regimens.

* Determine the rate and type of grade 4 toxicity, treatment-related mortality, and time to granulocyte and platelet recovery associated with each phase of treatment in these patients.

* Determine the DFS and overall survival of PML-RARa-positive patients who are ineligible for BMT and are treated with maintenance comprising MP plus MTX alternating with ATRA.

* Compare the quality of life of patients treated with these regimens.

OUTLINE: This is a randomized, multicenter study.

* Induction: Patients receive oral tretinoin (ATRA) twice daily beginning on day 1 and continuing for 30-90 days and idarubicin (IDA) IV over 15 minutes on days 2, 4, and 8. ATRA is discontinued before day 90 in the presence of complete remission (CR) at day 30 or 60, unacceptable toxicity, or disease progression or in the absence of at least a partial remission at day 60. Patients who achieve CR during induction proceed to consolidation.

* Consolidation:

* First consolidation: Within 2 weeks after achieving CR, patients receive cytarabine (ARA-C) IV over 6 hours followed 3 hours later by IDA IV over 15 minutes on days 1-4.

* Second consolidation:Within 4-6 weeks after initiation of first consolidation, patients receive mitoxantrone IV over 30 minutes and etoposide IV over 1 hour (beginning 12 hours after initiation of mitoxantrone infusion) on days 1-5.

* Third consolidation:Within 4-6 weeks after initiation of second consolidation, patients receive ARA-C subcutaneously every 8 hours and oral thioguanine every 8 hours on days 1-5 and IDA IV over 15 minutes on day 1.

Patients proceed to group A if they are promyelocyte-retinoic acid receptor alpha (PML-RARa)-negative after recovery from third consolidation. Patients proceed to allogeneic bone marrow transplantation (BMT) on group B if they are PML-RARa-positive, achieve CR, are under age 55, and have an HLA-A, -B, and -DR identical, chronic myelomonocytic leukemia nonreactive, family donor after recovery from third consolidation. Patients proceed to autologous BMT on group B if they are PML-RARa-positive, achieve CR, and have no identical family donor or are age 55 and over after recovery from third consolidation. Patients proceed to arm III of group A if they are PML-RARa-positive and ineligible for BMT after recovery from third consolidation.

* Group A (maintenance): Patients are stratified according to participating center and initial white blood cell count. Patients are randomized to 1 of 4 treatment arms.

* Arm I: Patients receive oral mercaptopurine (MP) daily and oral methotrexate (MTX) weekly.

* Arm II: Beginning 3 months after recovery from third consolidation, patients receive oral ATRA on days 1-15.

Treatment on arms I and II continues every 3 months for 2 years in the absence of disease progression or unacceptable toxicity.

* Arm III: Patients receive 1 course of arm I treatment, alternated by 1 course of arm II treatment. Alternating treatment continues every 3 months for 2 years in the absence of disease progression or unacceptable toxicity.

* Arm IV: Patients undergo observation only.

* Group B: Eligible patients receive conditioning comprising cyclophosphamide (CTX) IV for 2 days followed by total body irradiation or oral busulfan on days -9 to -6 and CTX on days -5 to -2. Autologous or allogeneic bone marrow is infused on day 0 (within 4 months after initiation of third consolidation).

Quality of life is assessed at baseline, after induction, after each consolidation regimen, and then every 3 months beginning after treatment on group A or B.

Patients are followed every 3 months.

PROJECTED ACCRUAL: A total of 750 patients will be accrued for this study within 7.5 years.

Recruitment & Eligibility

Status
UNKNOWN
Sex
All
Target Recruitment
750
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (71)

Universitair Ziekenhuis Antwerpen

🇧🇪

Edegem, Belgium

Federico II University Medical School

🇮🇹

Naples (Napoli), Italy

Ospedale S. Gennora USL 42

🇮🇹

Naples (Napoli), Italy

Azienda Ospedaliera di Padova

🇮🇹

Padova (Padua), Italy

Ibn-i Sina Hospital, Ankara University

🇹🇷

Ankara, Turkey

Leiden University Medical Center

🇳🇱

Leiden, Netherlands

Azienda Ospedaliera Di Parma

🇮🇹

Parma, Italy

I.R.C.C.S. Policlinico San Matteo

🇮🇹

Pavia, Italy

Algemeen Ziekenhuis Middelheim

🇧🇪

Antwerp, Belgium

Hopital Universitaire Erasme

🇧🇪

Brussels, Belgium

U.Z. Gasthuisberg

🇧🇪

Leuven, Belgium

University Hospital Rebro

🇭🇷

Zagreb, Croatia

Hopital Edouard Herriot

🇫🇷

Lyon, France

Centre Hospitalier Regional de Lille

🇫🇷

Lille, France

Centre Antoine Lacassagne

🇫🇷

Nice, France

Hotel Dieu de Paris

🇫🇷

Paris, France

Centre Medico-Chirurgical Foch

🇫🇷

Suresnes, France

Hopital Necker

🇫🇷

Paris, France

Institut Gustave Roussy

🇫🇷

Villejuif, France

Klinikum Duisburg

🇩🇪

Duisburg, Germany

Klinikum Grosshadern

🇩🇪

Munich (Muenchen), Germany

Ospedale Civile Alessandria

🇮🇹

Alessandria, Italy

Ospedale Civile Avellino

🇮🇹

Avellino, Italy

Ospedale Santa Croce

🇮🇹

Cuneo, Italy

Centro Trapianti di Midollo Osseo

🇮🇹

Cremona, Italy

Ospedali Riuniti Foggia

🇮🇹

Foggia, Italy

Ospedale Maggiore Ca Granda

🇮🇹

Milano (Milan), Italy

Istituto Scientifico H.S. Raffaele

🇮🇹

Milano, Italy

Innsbruck Universitaetsklinik

🇦🇹

Innsbruck, Austria

Centre Hospitalier Peltzer-La Tourelle

🇧🇪

Verviers, Belgium

Institut Jules Bordet

🇧🇪

Brussels (Bruxelles), Belgium

CHU Sart-Tilman

🇧🇪

Liege, Belgium

University Hospital - Rotterdam Dijkzigt

🇳🇱

Rotterdam, Netherlands

A.Z. St. Jan

🇧🇪

Brugge, Belgium

C.H.U. Saint-Pierre

🇧🇪

Brussels (Bruxelles), Belgium

Medical School/University of Zagreb

🇭🇷

Zagreb (Agram), Croatia

Onkologicka Klinka A Onkologicka Lab

🇨🇿

Prague, Czech Republic

Leyenburg Ziekenhuis

🇳🇱

's-Gravenhage (Den Haag, The Hague), Netherlands

Groot Ziekengasthuis 's-Hertogenbosch

🇳🇱

's-Hertogenbosch, Netherlands

Academisch Medisch Centrum

🇳🇱

Amsterdam, Netherlands

Academisch Ziekenhuis Groningen

🇳🇱

Groningen, Netherlands

University Medical Center Nijmegen

🇳🇱

Nijmegen, Netherlands

Ospedale Gen. Provinciale Santa Maria Goretti

🇮🇹

Latina, Italy

Ospedale Torrette University Ancona

🇮🇹

Ancona, Italy

Universita Degli Studi di Bari Policlinico

🇮🇹

Bari, Italy

Ospedale Regionale A. Di Summa

🇮🇹

Brindisi, Italy

Ospedale Oncologico A. Businco

🇮🇹

Cagliari, Italy

Ospedale Ferrarotto

🇮🇹

Catania, Italy

Ospedale Regionale A. Pugliese

🇮🇹

Catanzaro, Italy

Policlinico di Careggi

🇮🇹

Firenze (Florence), Italy

Ospedale S. Antonio Abate

🇮🇹

Gallarate Varese, Italy

Ospedale San Martino/Cliniche Universitarie Convenzionate

🇮🇹

Genoa (Genova), Italy

Ospedale Maggiore Lodi

🇮🇹

Lodi, Italy

Ospedale Di Montefiascone

🇮🇹

Montefiascone, Italy

Azienda Ospedaliera "A. Cardarelli"

🇮🇹

Naples (Napoli), Italy

Ospedale Nuovo Pellegrini

🇮🇹

Naples (Napoli), Italy

Ospedale San Francesco

🇮🇹

Nuoro, Italy

Policlinico - Cattedra di Ematologia

🇮🇹

Palermo, Italy

Ospedale Cervello

🇮🇹

Palermo, Italy

Policlinico Monteluce

🇮🇹

Perugia, Italy

Ospedale San Salvatore

🇮🇹

Pesaro, Italy

Ospedale Civile Pescara

🇮🇹

Pescara, Italy

Ospedale San Carlo

🇮🇹

Potenza, Italy

Ospedale San Eugenio

🇮🇹

Rome, Italy

Azienda Policlinico Umberto Primo

🇮🇹

Rome, Italy

Policlinico A. Gemelli - Universita Cattolica del Sacro Cuore

🇮🇹

Rome, Italy

Ospedale Casa Sollievo della Sofferenza

🇮🇹

San Giovanni - Rotondo, Italy

Istituto di Ematologia Universita - University di Sassari

🇮🇹

Sassari, Italy

Ospedal SS Annunziata

🇮🇹

Taranto, Italy

Cattedra di Immunologia Clinica

🇮🇹

Turin (TO), Italy

Ospedale Molinette

🇮🇹

Turin (Torino), Italy

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