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AZD0305 as Monotherapy or in Combination With Anticancer Agents in Participants With Relapsed/Refractory Multiple Myeloma

Phase 1
Recruiting
Conditions
Multiple Myeloma
Interventions
Registration Number
NCT06106945
Lead Sponsor
AstraZeneca
Brief Summary

This is a Phase I/II, modular, open-label, multicenter, dose escalation, and dose expansion/optimization study to evaluate the safety, tolerability, PK, immunogenicity, pharmacodynamics, and preliminary efficacy of AZD0305 in participants with RRMM.

Detailed Description

This is a Phase I/II, modular, open-label, multicenter, dose escalation, and dose expansion/optimization study to evaluate the safety, tolerability, PK, immunogenicity, pharmacodynamics, and preliminary efficacy of AZD0305 in participants with RRMM. This study will follow a modular protocol design evaluating AZD0305 as monotherapy and in combination with other anticancer agents.

The study includes dose escalation and dose expansion phases. This study will enroll subjects with RRMM who received at least 3 prior lines of treatment including at least one proteasome inhibitor (PI), one immunomodulator (IMiD), and an anti-CD38 antibody.

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
108
Inclusion Criteria
  • Participants must be at least 18 years of age or the legal age of consent in the jurisdiction in which the study is taking place.

  • Eastern Cooperative Oncology group (ECOG) performance status of ≤ 2.

  • Documentation of Multiple Myeloma (MM) as defined by International Myeloma Working Group (IMWG) Diagnostic Criteria for Multiple Myeloma. Site should ensure that Multiple Myeloma diagnosis is confirmed in accordance with the IMWG Diagnostic Criteria.

  • Participants must have one or more of the following measurable disease criteria:

    1. Serum M-protein level ≥ 0.5 g/dL.
    2. Urine M-protein level ≥ 200 mg/24h.
    3. Serum immunoglobulin free light chain ≥ 10 mg/dL and abnormal serum immunoglobulin kappa lambda free light chain ratio.
  • Adequate organ and bone marrow function assessment at screening according to the hematological, hepatic, and renal parameters listed in the CSP.

  • Participants must have received at least 3 prior lines of treatment which include a proteasome inhibitor (e.g., bortezomib), an immunomodulator (e.g., lenalidomide), and an anti-CD38 antibody (e.g., daratumumab).

Principal

Exclusion Criteria
  • Participants exhibiting clinical signs of central nervous system involvement of MM.
  • Participants with known COPD, or previous history of ILD.
  • Participants with known moderate or severe persistent asthma within the past 5 years, or uncontrolled asthma of any classification.
  • Participants who have severe cardiovascular disease which is not adequately controlled.
  • Participants who have a history of immunodeficiency disease.
  • Participants with peripheral neuropathy ≥ Grade 2.
  • Primary refractory MM.
  • Participants who have previously received anti-GPRC5D or MMAE-containing treatment.
  • Participants who have previously received allogenic stem cell transplant, or participant has received autologous stem cell transplant within 3 months before the first dose of study intervention.

Study & Design

Study Type
INTERVENTIONAL
Study Design
SEQUENTIAL
Arm && Interventions
GroupInterventionDescription
AZD0305 monotherapyAZD0305Module 1: Phase Ia: Dose Escalation Phase Ib: Dose Expansion/Optimization AZD0305 will be prescribed at specified dose levels.
Primary Outcome Measures
NameTimeMethod
Occurrence of dose-limiting toxicity (DLT), as defined in the protocol (Phase Ia dose escalation only)From first dose of study treatment until the end of Cycle 1

A DLT is defined as any toxicity that occurs from the first dose of study treatment up to and including the planned end of Cycle 1 (the DLT assessment period) that is assessed as unrelated to the disease or disease-related processes under investigation and which includes, any death not clearly due to the underlying disease or extraneous causes, pre-defined haematological and non-haematological toxicities

Incidence and severity of Adverse Events (AEs) and Serious Adverse Events (SAEs)From time of Informed consent to 30 days post end of treatment

Number of patients with adverse events and serious adverse events by system organ class and preferred term

Secondary Outcome Measures
NameTimeMethod
Phase Ia: Overall Survival (OS)From first dose of AZD0305 to death (approximately 2 years)

The time from the date of the first dose of study treatment until death due to any cause

Phase Ia: Pharmacokinetics of AZD0305: Time to maximum plasma concentration of the study drug (tmax)From the first dose of study intervention, at predefined intervals throughout the administration of AZD0305 (approximately 2 years)

Time to maximum observed plasma concentration of the study drug

Phase Ia: Pharmacokinetics of AZD0305: Terminal elimination half-life (t 1/2)From the first dose of study intervention, at predefined intervals throughout the administration of AZD0305 (approximately 2 years)

Terminal elimination half-life

Phase Ia: Immunogenicity of AZD0305From the first dose of study intervention, at predefined intervals throughout the administration of AZD0305 (approximately 2 years)

The number and percentage of participants who develop ADAs

Phase Ib: Pharmacokinetics of AZD0305: Time to maximum plasma concentration of the study drug (tmax)From randomization, at predefined intervals throughout the administration of AZD0305 (approximately 2 years)

Time to maximum observed plasma concentration of the study drug

Phase Ia: Pharmacokinetics of AZD0305: Area Under the concentration-time curve (AUC)From the first dose of study intervention, at predefined intervals throughout the administration of AZD0305 (approximately 2 years)

Area under the plasma concentration-time curve

Phase Ia: Progression free Survival (PFS)From first dose of AZD0305 to progressive disease or death in the absence of disease progression (approximately 2 years)

The time from first dose until IMWG defined disease progression or death

Phase Ib: Progression free Survival (PFS)From randomization to progressive disease or death in the absence of disease progression (approximately 2 years)

The time from randomization until IMWG defined disease progression or death

Phase Ib: Pharmacokinetics of AZD0305: Maximum plasma concentration of the study drug (Cmax)From randomization, at predefined intervals throughout the administration of AZD0305 (approximately 2 years)

Maximum observed plasma concentration of the study drug

Phase Ib: Pharmacokinetics of AZD0305: ClearanceFrom randomization, at predefined intervals throughout the administration of AZD0305 (approximately 2 years

A pharmacokinetic measurement of the volume of plasma from which the study drug is completely removed per unit time

Phase Ib: Immunogenicity of AZD0305From randomization, at predefined intervals throughout the administration of AZD0305 (approximately 2 years)

The number and percentage of participants who develop ADAs

Phase Ia: Objective Response Rate (ORR)From first dose of AZD0305 to progressive disease or Initiation of subsequent MM therapy (approximately 2 years)

The percentage of patients with a confirmed investigator assessed sCR, CR, VGPR or PR according to IMWG criteria

Phase Ia: Duration of response (DoR)From the first documented response to confirmed progressive disease or death (approximately 2 years)

The time from the date of first response until date of disease progression or death in the absence of disease progression

Phase Ia: Pharmacokinetics of AZD0305: Maximum plasma concentration of the study drug (Cmax)From the first dose of study intervention, at predefined intervals throughout the administration of AZD0305 (approximately 2 years)

Maximum observed plasma concentration of the study drug

Phase Ib: Objective Response Rate (ORR)From randomization to progressive disease or Initiation of subsequent MM therapy (approximately 2 years)

The percentage of patients with a confirmed investigator assessed sCR, CR, VGPR or PR according to IMWG criteria

Phase Ib: Overall Survival (OS)From randomization to death (approximately 2 years)

The time from randomization until death due to any cause

Phase Ib: Pharmacokinetics of AZD0305: Area Under the concentration-time curve (AUC)From randomization, at predefined intervals throughout the administration of AZD0305 (approximately 2 years)

Area under the plasma concentration-time curve

Phase Ia: Pharmacokinetics of AZD0305: ClearanceFrom the first dose of study intervention, at predefined intervals throughout the administration of AZD0305 (approximately 2 years)

A pharmacokinetic measurement of the volume of plasma from which the study drug is completely removed per unit time

Phase Ib: Duration of response (DoR)From randomization to confirmed progressive disease or death (approximately 2 years)

The time from date of first response until date of disease progression or death in the absence of disease progression

Phase Ib: Pharmacokinetics of AZD0305: Terminal elimination half-life (t 1/2)From randomization, at predefined intervals throughout the administration of AZD0305 (approximately 2 years)

Terminal elimination half-life

Trial Locations

Locations (1)

Research Site

🇪🇸

Salamanca, Spain

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