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Pre-therapeutic Identification of Dihydropyrimidine Dehydrogenase Gene (DPD) Deficiency for Predicting Toxicity to Fluoropyrimidines

Not Applicable
Terminated
Conditions
Colorectal Cancer
Intravenous 5 Fluorouracile
Interventions
Genetic: Blood sample for phenotypic and pharmacogenetic analysis.
Registration Number
NCT01547923
Lead Sponsor
Institut Cancerologie de l'Ouest
Brief Summary

The aim of this study is to demonstrate the medical and financial benefit of pre-therapeutic screening of DPD deficiency for predicting toxicity to fluoropyrimidines.

Detailed Description

The fluoropyrimidines, of which 5-Fluorouracil is the most important, represent a family of medication that is used in particular in cancerology. They are molecules widely used in cancerology since they can be found in nearly 45% of chemotherapy protocols and in the treatment of about 50% of cancers (colorectum, oesophagus, stomach, breast, upper digestive and respiratory tracts). They are not only used in metastatic situations but also more and more in adjuvant situations, in other words for patients treated for a localised tumour, presenting a risk of relapse. A severe toxic risk cannot be tolerated in these conditions, and the doctor should assure the maximum level of safety for his patients. These medicines are the cause of 3% of grade IV toxicity from the first or second administration, and for 0.3% of deaths. To this one can add on a total of 20 to 25% grade III-IV toxic events.

Anticancer treatment is mostly administered by body size and in the best of cases after a few basic biological examinations such as a haemogram and renal status, without taking into consideration any individual particularities, whether genetic or epigenetic. Among potential toxicity risk factors one can find individual metabolic differences linked to genetic modifications of metabolism enzymes as well as differences in the chemical receptors and transporters.

For fluoropyrimidines, a polymorphism was found for the dihydropyrimidine dehydrogenase gene (DPD), a major catabolism enzyme. A deficit of this enzyme is a major counter-indication for the use of these medicines.

Early determination of DPD status would allow identification of patients at risk and would thus help in subsequent dose adjustment or selection of other treatment modalities.

Recruitment & Eligibility

Status
TERMINATED
Sex
All
Target Recruitment
1142
Inclusion Criteria
  • colorectal cancer, histologically confirmed, with all types included (including adjuvant cases), requiring treatment with intravenous 5-fluorouracil.
  • anterior chemotherapy authorised, with the exception of chemotherapy containing a derivate of 5-Fluorouracil
  • Age > or = 18 years
  • WHO Performance status < or = 2
  • Haematologic and hepatic parameters : neutrophils > or = 1000 /mm3, platelets > or = 100000/mm3, Total bilirubin < or = 2 x ULN, AST and ALT < or = 3 x ULN, APL < or = 5 x ULN
  • Complete initial assessment before first treatment administration for imaging and pharmacogenetic, within 15 days for biology, and within 7 days for clinical examination.
  • Signed written informed consent
Exclusion Criteria
  • Prior chemotherapy with fluoropyrimidines
  • Symptomatic or uncontrolled ventral nervous system metastases
  • Psychiatric Disease disrupting the trial understanding and the enlightened and voluntary consent character
  • Patient who is pregnant or breast feeding
  • Woman not consenting to use adequate contraceptive precautions during the study
  • Patient who can not submit itself to the formal follow-up for psychological, social, family or geographical reasons
  • Significant serious pathology or any instable medical condition (cardiac pathology uncontrolled, myocardial infarction within 6 months before enrollment, systemic active uncontrolled infection)
  • any investigational agent within 4 weeks before enrollment

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
A : pre-therapeutic screening for DPD deficiencyBlood sample for phenotypic and pharmacogenetic analysis.Prior to treatment by fluoropyrimidines,a DPD deficiency is identified by a joint phenotypic-pharmacogenetic approach.
B : no pretherapeutic research of DPD deficiencyBlood sample for phenotypic and pharmacogenetic analysis.For patients included in this arm, a blood sample will be taken prior to treatment by fluoropyrimidines but not analysed. If grade 3 or 4 toxicity levels are encountered during treatment, DPD deficiency will be detected.
Primary Outcome Measures
NameTimeMethod
Number and nature of grade IV toxicity.Up to 4 weeks.

The percentage of severe toxicity (grade IV) will be analyzed in each arm. We expect a reduction of the early, severe, grade IV acute side-effects from 3% to 0.6% in the detected group with adapted doses.

Secondary Outcome Measures
NameTimeMethod
Number of grade III-IV toxic events.Up to 6 months.

We expect a reduction of the number of grade III-IV toxic events, whenever they occur, from 25% to 5% in the detected group with adapted doses.

Mortality rate.up to 6 months.

The current mortality rate of 3 per thousand patients will be cut to 0 in the detected group with adapted doses.

Medical-financial study of pre-therapeutic screening.Up to 6 months.

We will carry out a comparison of the prevention costs and the costs related to treating patients with toxicity. Direct costs and indirect costs will be taken into account.

Trial Locations

Locations (22)

ICO René Gauducheau

🇫🇷

St Herblain, France

ICO Paul Papin

🇫🇷

Angers, France

CHU Morvan

🇫🇷

Brest, France

CHU Côte de Nacre

🇫🇷

Caen, France

Pôle Santé Léonard de Vinci

🇫🇷

Chambray-les-Tours, France

Clinique des Cèdres

🇫🇷

Cornebarrieu, France

CH Sarthe et Loir

🇫🇷

La Flèche, France

Centre Hospitalier Les oudairies

🇫🇷

La Roche Sur Yon, France

Centre Antoine Lacassagne

🇫🇷

Nice, France

Institut Claudius Regaud

🇫🇷

Toulouse, France

Hôpital Purpan

🇫🇷

Toulouse, France

CHU Trousseau

🇫🇷

Tours, France

HEGP

🇫🇷

Paris, France

Centre Oscar Lambret

🇫🇷

Lille, France

Centre d'oncologie de Gentilly

🇫🇷

Nancy, France

CHU Hotel Dieu

🇫🇷

Nantes, France

Centre Hospitalier Lyon Sud

🇫🇷

Pierre Bénite, France

CHU Jean Minjoz

🇫🇷

Besançon, France

Centre Hospitalier

🇫🇷

Saumur, France

Hôpital Henri Mondor

🇫🇷

Créteil, France

Centre François Baclesse

🇫🇷

Caen, France

Centre Hospitalier du Haut Anjou

🇫🇷

Chateau-Gontier, France

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