Development and evaluation of Gaucher disease (GD) - specific patient reported outcome measurement (PROM) in Japan.
Not Applicable
- Conditions
- Gaucher Disease
- Registration Number
- JPRN-UMIN000042872
- Lead Sponsor
- Takeda Pharmaceutical Company Limited
- Brief Summary
Three main themes emerged from qualitative analysis of patient interviews: treatment status, patient burden, and social support systems. Commonly used words and the relationships between words identified through the hierarchical cluster and co-occurrence network analyses supported these themes and topics. These themes and topics were specific to patients with types 2 and 3 GD and will be used to inform the development of a HRQOL questionnaire specifically for patients with all GD types
- Detailed Description
Not available
Recruitment & Eligibility
- Status
- Complete: follow-up complete
- Sex
- All
- Target Recruitment
- 8
Inclusion Criteria
Not provided
Exclusion Criteria
Patients: - Patients who have cognitive disabilities, - Patients who lack of fluency in Japanese. Caregivers: - Persons with cognitive disabilities - Persons with lack of fluency in Japanese
Study & Design
- Study Type
- Observational
- Study Design
- Not specified
- Primary Outcome Measures
Name Time Method
- Secondary Outcome Measures
Name Time Method