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Trends in Modern Phase 1 Oncology Trials

Completed
Conditions
Cancer
Registration Number
NCT03676270
Lead Sponsor
Institut Bergonié
Brief Summary

Overview of response rate published in recent oncology phase I trials

Detailed Description

Critics have raised a fundamental ethical challenge about phase 1 cancer research. They point to an expected paucity of benefits, since approximately 5% of patients in phase 1 trials are reported to have tumor shrinkage.

Objective was to conduct a search of the literature using PubMed to identify articles about phase 1 trials that were published from January 1, 2014, through June 30, 2015. The primary end point was the response rate according to Response Evaluation Criteria in Solid Tumors (RECIST) criteria.

Clinically relevant trials' characteristics were investigated as candidate factors associated with the RR: Funding source (Academic / Industrial), First-in man trial (Yes / No), Expansion cohort (Yes / No), Number of targeted organs (Single / Multiple), Therapy (Single / Combination), Treatment (MAB-Immuno / ITK / Chimioth-HT-other), Biological eligibility criterion (Yes / No), as well as the number of assessable patients, which for ease of clinical interpretation was transformed into a qualitative variable (0-25 / 26 - 50 / 51+).

The RR was described according to the individual trials' characteristics. Associations with trials's characteristics were investigated using statistical modeling.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
6915
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Response Rateup to 6 months after treatment initiation

Number of reported responses (complete \[CR\] and partial \[PR\]) divided by the number of reported assessable patients

Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (1)

Insitut Bergonié

🇫🇷

Bordeaux, France

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