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A Randomized, Controlled Trial of Ganaxolone in Adult Uncontrolled Partial-Onset Seizures

Phase 2
Completed
Conditions
Partial Epilepsy
Catamenial Epilepsy
Interventions
Other: Placebo
Drug: Ganaxolone
Registration Number
NCT00465517
Lead Sponsor
Marinus Pharmaceuticals
Brief Summary

The study will evaluate the effectiveness and safety of an investigational drug-ganaxolone - on partial seizure frequency in adults with epilepsy taking a maximum of 3 antiepileptic medications (AEDs). The study will also evaluate the effectiveness of ganaxolone in females with catamenial epilepsy.

Catamenial epilepsy refers to a relationship between seizure frequency and a woman's menstrual cycle, where the number of seizures increases around the time of a woman's menstrual cycle.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
147
Inclusion Criteria

Not provided

Read More
Exclusion Criteria

Not provided

Read More

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
non-active drugPlaceboplacebo
ganaxoloneGanaxoloneactive study drug
Primary Outcome Measures
NameTimeMethod
Mean Weekly Log-transformed Seizure Frequency During Weeks 1 Through 10Week 1 through Week 10

Weekly seizure frequency, analyzed as mean weekly log-transformed seizure frequency \[including partial-onset seizures (POS) with or without secondary generalization, but not non-motor simple partial seizure (SPS)\] during Weeks 1 through 10.

Secondary Outcome Measures
NameTimeMethod
Number of Responders During Weeks 3 Through 10Baseline and at Week 3 through Week 10

Responders were defined as participants experiencing ≥50% of reduction in mean weekly seizure frequency from the Baseline. Baseline was defined as the Day 0 assessment before study drug infusion.

Percent Change From Baseline in Mean Weekly Seizure Frequency During Weeks 1 Through 10Baseline and at Week 1 through Week 10

Summary of percent change from Baseline in mean weekly seizure frequency is presented. Baseline was defined as the Day 0 assessment before study drug infusion. Change from Baseline was calculated by subtracting Baseline value from the post-dose visit value.

Number of Responders During Weeks 1 Through 10Baseline and at Week 1 through Week 10

Responders were defined as participants experiencing ≥50% of reduction in mean weekly seizure frequency from the Baseline. Baseline was defined as the Day 0 assessment before study drug infusion.

Number of Seizure-free Participants Up to Week 2Up to Week 2

Number of seizure-free participants is presented.

Number of Seizure-free Days During Week 1 Through 10Week 1 through Week 10

Summary of Seizure-Free days is presented.

Mean Weekly Log-transformed Seizure Frequency During Weeks 3 Through 10Week 3 through Week 10

Weekly seizure frequency, analyzed as mean weekly log-transformed seizure frequency \[including POS with or without secondary generalization, but not non-motor SPS\] during the Weeks 3 through 10

Change From Baseline in Mean Weekly Seizure Frequency During Weeks 3 Through 10Baseline and at Week 3 through Week 10

Summary of change from Baseline in mean weekly seizure frequency is presented. Baseline was defined as the Day 0 assessment before study drug infusion. Change from Baseline was calculated by subtracting Baseline value from the post-dose visit value.

Percent Change From Baseline in Mean Weekly Seizure Frequency During Weeks 3 Through 10Baseline and at Week 3 through Week 10

Summary of percent change from Baseline in mean weekly seizure frequency is presented. Baseline was defined as the Day 0 assessment before study drug infusion. Change from Baseline was calculated by subtracting Baseline value from the post-dose visit value.

Change From Baseline in Mean Weekly Seizure Frequency During Weeks 1 Through 10Baseline and at Week 1 through Week 10

Summary of change from Baseline in mean weekly seizure frequency is presented. Baseline was defined as the Day 0 assessment before study drug infusion. Change from Baseline was calculated by subtracting Baseline value from the post-dose visit value.

Mean Weekly Seizure Frequency for Each Week After Dosing During Weeks 1 to 10Weeks 1, 2, 3, 4, 5, 6, 7, 8, 9 and 10

Mean weekly Seizure Frequency for each week post-dosing During Weeks 1 to 10 is presented.

Percent Change From Baseline in Mean Weekly Seizure Frequency by Subtype During Weeks 1 Through 10Baseline and at Week 1 through Week 10

Seizure subtypes included Complex partial seizures (CPS), Generalized tonic-clonic seizure (GTCS), and Simple partial seizure (SPS)-motor. Percent Change from Baseline in Mean Weekly Seizure frequency by seizure subtype is presented. Baseline was defined as the Day 0 assessment before study drug infusion. Change from Baseline was calculated by subtracting Baseline value from the post-dose visit value.

Number of Seizure-free Participants During Weeks 1 Through 10Week 1 through Week 10

Number of seizure-free participants is presented.

Number of Seizure-free Participants During Weeks 3 Through 10Week 3 through Week 10

Number of seizure-free participants is presented.

Number of Seizure-free Days Up to Week 2Up to Week 2

Summary of Seizure-Free days is presented.

Number of Seizure-free Days During Week 3 Through 10Week 3 through Week 10

Summary of Seizure-Free days is presented.

Trial Locations

Locations (27)

SUNY Upstate Medical University

🇺🇸

Syracuse, New York, United States

University of Southern California Adult Comprehensive Epilepsy Center

🇺🇸

Los Angeles, California, United States

Neurosciences Institute at Albany Medical Center

🇺🇸

Albany, New York, United States

Overlook Hospital and Hackensack Medical Center

🇺🇸

Hackensack, New Jersey, United States

Barrow Neurological Institute

🇺🇸

Phoenix, Arizona, United States

2799 West Grand blvd. CFP 071

🇺🇸

Detroit, Michigan, United States

Vanderbilt University Medical Ctr

🇺🇸

Nashville, Tennessee, United States

University of Alabama

🇺🇸

Birmingham, Alabama, United States

Mid-Atlantic Epilepsy and Sleep Center

🇺🇸

Bethesda, Maryland, United States

Arkansas Epilepsy Program

🇺🇸

Little Rock, Arkansas, United States

University of California-Davis

🇺🇸

Sacramento, California, United States

Anchutz Outpatient Pavillion Neurosciences Clinic/ University of Colorado Hospital

🇺🇸

Aurora, Colorado, United States

Yale University School of Medicine

🇺🇸

New Haven, Connecticut, United States

University of Florida McKnight Brain Institute

🇺🇸

Gainesville, Florida, United States

Southern Illinois University Medical Center

🇺🇸

Springfield, Illinois, United States

Intercoastal Medicine

🇺🇸

Sarasota, Florida, United States

Emory HealthCare

🇺🇸

Atlanta, Georgia, United States

University of Iowa Hospitals and Clinics

🇺🇸

Iowa City, Iowa, United States

University of Kentucky, Dept. of Neurology

🇺🇸

Lexington, Kentucky, United States

Minnesota Epilepsy Group, PA

🇺🇸

Saint Paul, Minnesota, United States

Comprehensive Epilepsy Care Center for Children and Adults

🇺🇸

Chesterfield, Missouri, United States

Ohio State University Medical Center

🇺🇸

Columbus, Ohio, United States

Drexel University / Hahneman Hospital

🇺🇸

Philadelphia, Pennsylvania, United States

Riddle Health Care Center for Neuroscience

🇺🇸

Media, Pennsylvania, United States

Neurological Clinic of Texas, P.A.

🇺🇸

Dallas, Texas, United States

Virginia Commonwealth University

🇺🇸

Richmond, Virginia, United States

Thomas Jefferson University

🇺🇸

Philadelphia, Pennsylvania, United States

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