MedPath

Domatinostat in Combination With Avelumab in Patients With Advanced Merkel Cell Carcinoma Progressing on Anti-PD-(L)1

Phase 2
Completed
Conditions
Merkel Cell Carcinoma
Interventions
Registration Number
NCT04393753
Lead Sponsor
4SC AG
Brief Summary

This phase II trial studies how well domatinostat (4SC-202) works in combination with avelumab in adult patients with advanced unresectable and/or metastatic Merkel Cell Carcinoma that have progressed on a previous therapy with an anti-PD-(L)1 antibody

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
19
Inclusion Criteria
  • Histologically confirmed Merkel Cell Carcinoma (MCC)
  • ECOG performance status ≤ 1
  • MCC in an advanced, unresectable stage III or metastatic stage IV (includes patients who refused surgical resection or are not eligible for such surgical resection)
  • Progressing on previous anti-PD-(L)1 antibody monotherapy within the last 12 weeks before planned first administration of study medication
Exclusion Criteria
  • History of serious anti-PD-(L)1 therapy-related adverse reactions prohibiting further avelumab treatment
  • More than one line of previous systemic anti-neoplastic therapy other than anti-PD-(L)1 antibody monotherapy
  • Palliative radiation therapy of single lesions within 2 weeks before planned administration of study medication
  • Presence of significant active or chronic disease (infections, immunodeficiencies, cardiovascular, psychiatric disorders)

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
domatinostat and avelumabdomatinostat in combination with avelumabSingle arm study of Domatinostat tablets in combination with avelumab infusion
Primary Outcome Measures
NameTimeMethod
Objective Response Rate (ORR)up to 24 months

Objective Response Rate (ORR) defined as the percentage of patients having a confirmed CR or PR according to RECIST v1.1

Secondary Outcome Measures
NameTimeMethod
Durable Response Rate (DRR)up to 24 months

Durable Response Rate (DRR), defined as the percentage of patients having a RECIST v1.1 response lasting ≥ 6 months

Duration of Response (DoR)up to 24 months

Duration of Response (DoR), defined as the time from an initial objective response (CR or PR) according to RECIST v1.1 until disease progression or death due to any cause

Disease Control Rate (DCR)up to 24 months

Disease Control Rate (DCR), defined as the proportion of patients with either an objective response (CR, PR) or stable disease (SD) according to RECIST v1.1.

Durable Disease Control Rate (dDCR)up to 24 months

Durable Disease Control Rate (dDCR), defined as the percentage of patients having a RECIST v1.1 disease control lasting ≥ 6 months

Best Overall response (BOR)up to 24 months

Best Overall response (BOR), defined as the best response (PD, SD, PR, CR) according to RECIST v1.1 over the course of a patient's participation in the study, assessed up to 2 years

Overall Survival (OS)up to 36 months

Overall Survival (OS), defined as the time from the first administration of study medication until death due to any cause

OS Rateup to 12 months

OS Rate, defined as the percentage of patients alive at 6 and at 12 months after first administration of study drug

Progression Free Survival (PFS)up to 24 months

Progression Free Survival (PFS), defined as the time from first dosing (Day +1) to the date of PD or death from any cause (whichever comes first)

PFS Rateup to 24 months

PFS Rate, defined as the percentage of patients without PD at 6 and 12 months after first administration of study drug

Safety and Tolerabilityup to 24 months

Safety and Tolerability of the study medication (determined by number, frequency, duration and severity of AEs using CTCAE v5.0, physical examination, laboratory tests, vital signs, and ECGs)

Health related Quality of Life (HrQoL)up to 24 months

The impact of treatment on the patient's QoLwill be assessed with the questionnaires "Functional Assessment of Cancer Therapy - Melanoma (FACT-M)" where QoL is assessed on a scale 0-240 (higher score means better status of health), with "EQ-5D-5L" which is a multi attribute utility instrument for measuring health-related QoL as EQ5D index with a score 0-1 (higher score means better status of health) and with the European Organization for Research and Treatment of Cancer Quality of Life Questionnaire (EORTC-QLQ-C30) with a score 0-100 per subscale (n=9 per item (n=6), higher score means better QoL.

Plasma concentration of domatinostat and avelumabup to 48 weeks

Single trough values of domatinostat and avelumab at pre-defined time points

Avelumab anti-drug antibodies (ADA)up to 48 weeks

Avelumab anti-drug antibodies (ADA)

Trial Locations

Locations (22)

Netherlands Cancer Institute Amsterdam

🇳🇱

Amsterdam, Netherlands

Istituto Nazionale Tumori Fondazione G.Pascale

🇮🇹

Naples, Italy

IOV - Istituto Oncologico Veneto IRCCS

🇮🇹

Padova, Italy

Bordeaux Hôpital Saint Andre

🇫🇷

Bordeaux, France

CHU Nantes - Hotel Dieu

🇫🇷

Nantes, France

Hôpital Ambroise Paré - Boulogne-Billancourt

🇫🇷

Boulogne-Billancourt, France

Universitätsklinikum Heidelberg

🇩🇪

Heidelberg, Germany

UZ Leuven

🇧🇪

Leuven, Belgium

Universitätsklinikum Dresden

🇩🇪

Dresden, Germany

Helios Klinikum Erfurt

🇩🇪

Erfurt, Germany

Hôpital Saint-Louis

🇫🇷

Paris, France

Universitätsklinikum Essen

🇩🇪

Essen, Germany

Universitätsklinikum Leipzig

🇩🇪

Leipzig, Germany

Instituto Tumori Giovanni Paolo II IRCCS Ospedale Oncologico Bari

🇮🇹

Bari, Italy

Technische Universität München

🇩🇪

München, Germany

Universitätsklinikum Köln

🇩🇪

Köln, Germany

Universitätsklinikum Schleswig-Holstein, Campus Lübeck

🇩🇪

Lübeck, Germany

Fondazione del Piemonte per l'Oncologia

🇮🇹

Torino, Italy

Hospital Universitari Vall d'Hebron

🇪🇸

Barcelona, Spain

Academic Hospital Maastricht

🇳🇱

Maastricht, Netherlands

Universitätsklinikum Schleswig-Holstein Kiel

🇩🇪

Kiel, Germany

Universitätsklinikum Tübingen

🇩🇪

Tübingen, Germany

© Copyright 2025. All Rights Reserved by MedPath