A gene therapy clinical trial for chronic granulomatous disease targeting the patient's hematopoietic stem cells
Phase 1
Recruiting
- Conditions
- chronic granulomatous disease
- Registration Number
- JPRN-UMIN000008235
- Lead Sponsor
- ational Center for Child Heath and Development
- Brief Summary
Not available
- Detailed Description
Not available
Recruitment & Eligibility
- Status
- Recruiting
- Sex
- Male
- Target Recruitment
- 5
Inclusion Criteria
Not provided
Exclusion Criteria
Severe cardiorespiratory failure positive for HIV severe allegy no anticipation for long-term live survival
Study & Design
- Study Type
- Interventional
- Study Design
- Not specified
- Primary Outcome Measures
Name Time Method cure or mitigation of severe infections
- Secondary Outcome Measures
Name Time Method a long-term protective effect on severe infections