MedPath

Simplified IMmunosuppressive Protocol Utilizing Low Dose EnvarsusXR

Registration Number
NCT04773392
Lead Sponsor
University of Southern California
Brief Summary

The purpose of this study is to determine if the combination of once-daily tacrolimus extended-release (EnvarsusXR) and Azathioprine is non inferior with respect to the composite outcome of acute rejection, graft and patient survival as compared to a combination of twice-daily immediate release tacrolimus and mycophenolate mofetil/mycophenolic acid.

Detailed Description

While short-term graft outcomes in kidney transplantation have improved, this requires adherence to a complex medication regimen. The current twice-daily immunosuppressive regimen, immediate release tacrolimus and mycophenolate mofetil/mycophenolic acid, has reduced rejection rates significantly, but frequently cause neurologic and gastrointestinal side effects which impact recipient quality of life. These side effects often require dose adjustments and studies have shown inferior outcomes when multiple changes are made to the immunosuppressive regimen. Furthermore, patients taking twice-daily medications have poorer compliance and yet adherence to these medications is critical to mitigate the risk of allograft rejection. Acute and chronic rejection are important causes of graft failure and patient survival.

Immediate release (IR) tacrolimus based immunosuppressive regimens have become the standard of care at most US centers. With the introduction of a once-daily tacrolimus formulation, kidney transplant recipients can now be on a combination regimen (EnvarsusXR and azathioprine) that permits all immunosuppressive medications to be taken once a day instead of twice . Previous studies suggest that therapeutic goals with EnvarsusXR may be achieved at a lower dose than the currently recommended dose. This once a day medication schedule has the potential to simplify the immunosuppressive regimen by reducing adverse side effects and facilitating compliance.

The investigators seek to demonstrate that a once-daily regimen, including EnvarsusXR and azathioprine, will be at least equally effective with respect to acute rejection, graft and patient survival as compared to the standard, twice-daily, immediate release tacrolimus and mycophenolate mofetil/mycophenolic acid. The investigators will also assess graft function, medication complications and side effects in each arm.

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
80
Inclusion Criteria
  • De- Novo Kidney transplant patients between 18 and 85 years old
  • Cold ischemia time (CIT) < 24 hours for 3-6 HLA mismatches between donor and recipient and CIT >24 hours for HLA mismatch of less than 3 between donor and recipient
  • Most recent pre-transplant cPRA (calculated panel reactive antibody) ≤ 20%
Exclusion Criteria
  • Repeat kidney transplant recipients
  • cPRA >20%
  • rATG (rabbit anti-thymocyte globulin) induction >6mg/kg at time of induction
  • Crossmatches deemed positive by accepting physician
  • Presence of pre-formed anti-HLA (anti-Human Leukocyte Antigen) DSA (Donor-Specific Antibody) as defined by MFI (mean fluorescence intensity) approaching 3000 using flow cytometry/Luminex-based, specific anti-HLA antibody testing.
  • Receipt of desensitization protocols
  • History of skin cancer
  • Recipient of multi-organ or dual kidney transplants
  • For any condition, in which the investigator's opinion makes the subject unsuitable for study

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Twice-daily RegimenTwice-daily TacrolimusTwice-daily regimen of immediate release tacrolimus, mycophenolate mofetil (MMF)/mycophenolic acid (MPA) plus daily methylprednisolone or prednisone.
Twice-daily RegimenMethylprednisolone, prednisoneTwice-daily regimen of immediate release tacrolimus, mycophenolate mofetil (MMF)/mycophenolic acid (MPA) plus daily methylprednisolone or prednisone.
Twice-daily RegimenInduction Immunosuppression with Basiliximab or Rabbit Anti Thymoglobulin (rATG)Twice-daily regimen of immediate release tacrolimus, mycophenolate mofetil (MMF)/mycophenolic acid (MPA) plus daily methylprednisolone or prednisone.
Once-daily RegimenOnce-daily envarsus XROnce-daily regimen of Envarsus, azathioprine plus methylprednisolone or prednisone.
Twice-daily RegimenMycophenolate mofetil (MMF) or Mycophenolic acid (MPA)Twice-daily regimen of immediate release tacrolimus, mycophenolate mofetil (MMF)/mycophenolic acid (MPA) plus daily methylprednisolone or prednisone.
Once-daily RegimenInduction Immunosuppression with Basiliximab or Rabbit Anti Thymoglobulin (rATG)Once-daily regimen of Envarsus, azathioprine plus methylprednisolone or prednisone.
Once-daily RegimenAzathioprineOnce-daily regimen of Envarsus, azathioprine plus methylprednisolone or prednisone.
Once-daily RegimenMethylprednisolone, prednisoneOnce-daily regimen of Envarsus, azathioprine plus methylprednisolone or prednisone.
Primary Outcome Measures
NameTimeMethod
To compare the composite incidence of biopsy proven acute rejection, graft survival and patient survival12 months

Biopsies will be performed for unexplained rise in serum creatinine or proteinuria and the development of donor specific antibodies. Biopsies will be assessed by a pathologist using standard Banff classification of renal allograft pathology. Graft loss will be defined as return to chronic dialysis or graft removal.

Secondary Outcome Measures
NameTimeMethod
Cancer3, 6, and 12 months

Incidence of cancers

Diabetes3, 6, and 12 months

Incidence of new onset diabetes measured by HgbA1c

Renal allograft functionEvery month, for a duration of 12 months

Estimated glomerular filtration rate (eGFR)

ProteinuriaEvery month, for a duration of 12 months

Urinalysis

Donor-specific antibodies (DSA)3, 6, and 12 months

Donor-specific anti-HLA antibodies, with a MFI (mean fluorescence intensity) \>1000, measured by flow cytometry/Luminex-based assay

Cytomegalovirus (CMV)3, 6, and 12 months

CMV PCR

Liver Function3, 6, and 12 months

Alanine aminotransferase, aspartate aminotransferase and alkaline phosphatase

Gastrointestinal side effects3, 6, and 12 months

GI side effects will be assessed by the Gastrointestinal Symptoms Rating Scale (GSRS) is a 15 item questionnaire addressing reflux, abdominal pain, indigestion, diarrhea and constipation. The GSRS has a seven-point graded Likert-type scale where 1 represents absence of troublesome symptoms and 7 represents very troublesome symptoms.

Dyspepsia and quality of life3, 6, and 12 months

The Quality of Life in Reflux and Dyspepsia (QOLRAD) is a 25 item instrument depicting problems with emotions, vitality, sleep, eating/drinking, and physical/social functioning in adult patients with reflux disease. The questions are rated on a seven-point graded Likert scale; lower values indicate a more severe impact on daily functioning.

Tremor3, 6, and 12 months

Tremor will be assessed by Quality of life in Essential Tremor Questionnaire, (QUEST) a 30-item scale developed specifically for patients with essential tremor to measure items impacting perceived quality of life (QOL). The items are rated on a five-point scale (score 0-4), corresponding to the frequency (never, rarely, sometimes, frequently, always) with which tremor was perceived to currently impact a function or to be associated with various feelings and attitudes

Perception of quality of life3, 6, and 12 months

The Short Form (36) Healthy Survey (SF-36) is a multi-purpose survey designed to capture adult patients' perceptions of their own health and well-being.Each scale is directly transformed into a 0-100 scale on the assumption that each question carries equal weight. The lower the score the more disability. The higher the score the less disability.

Electrolytes3, 6, and 12 months

Dose of magnesium, potassium and phosphorus needed to replete electrolytes

Adverse Events3, 6, and 12 months

An adverse event can be any unfavorable and unintended sign, symptom, or disease temporally associated with the use the product, whether or not related to the product.

Dose changes3, 6, and 12 months

Frequency of dose changes made in Envarsus, tacrolimus and MMF/MPA. Dosage changes will be adjusted for Tacrolimus drug levels as per protocol. MMF/MPA will be adjusted depending on gastrointestinal tolerability and bone marrow suppression.

BK Viremia3, 6, 12 months

BK quantitative serum assay

Trial Locations

Locations (1)

University of Southern California

🇺🇸

Los Angeles, California, United States

University of Southern California
🇺🇸Los Angeles, California, United States
Melissa Ramos, BSN
Contact
323-442-7983
Melissa.Ramos@med.usc.edu
Santhi Voora, MD
Principal Investigator
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