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Single-Ascending Dose Study of BIIB054 in Healthy Participants and Early Parkinson's Disease

Phase 1
Completed
Conditions
Healthy
Parkinson's Disease
Interventions
Drug: Placebo
Registration Number
NCT02459886
Lead Sponsor
Biogen
Brief Summary

The primary objective of the study is to evaluate the safety and tolerability of a range of single BIIB054 doses, administered as a single intravenous (IV) infusion, in healthy participants and participants with early Parkinson's disease (PD). Secondary objectives of the study are to assess the serum pharmacokinetics (PK) profile of BIIB054 after single-dose administration and to evaluate the immunogenicity of BIIB054 after single-dose administration.

Detailed Description

Only healthy participants will be enrolled in Cohorts 1 through 6. Only participants with early PD will be enrolled in Cohort 7

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
66
Inclusion Criteria
  1. All women of childbearing potential and all men must practice effective contraception during the study and for 6 months after their last dose of study treatment.

  2. Must have a body mass index from 19 to 32 kg/m2, inclusive.

  3. Must be in good health as determined by the Investigator, based on medical history, physical examination, and 12-lead ECG.

    For cohort 7 only:

  4. Diagnosis of idiopathic PD

Key

Exclusion Criteria
  1. History of cardiovascular disease.
  2. Subject smokes more than 5 cigarettes or the equivalent in tobacco daily.
  3. Surgery within 3 months prior to Day -1 (other than minor cosmetic surgery and minor dental surgery, as determined by the Investigator).
  4. History or positive test result for hepatitis C, hepatitis B, or human immunodeficiency virus (HIV).
  5. Female subjects who are pregnant, currently breastfeeding, or attempting to conceive during the study.

NOTE: Other protocol defined Inclusion/Exclusion criteria may apply.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Cohort 2PlaceboSingle IV ascending dose infusion with staggered participant dosing
Cohort 1BIIB054Single intravenous (IV) low dose infusion with staggered participant dosing
Cohort 1PlaceboSingle intravenous (IV) low dose infusion with staggered participant dosing
Cohort 2BIIB054Single IV ascending dose infusion with staggered participant dosing
Cohort 3PlaceboSingle IV ascending dose infusion with staggered participant dosing
Cohort 4BIIB054Single IV ascending dose infusion with staggered participant dosing
Cohort 6PlaceboSingle IV ascending dose infusion with staggered participant dosing
Cohort 7PlaceboSingle IV ascending dose infusion with staggered participant dosing
Cohort 3BIIB054Single IV ascending dose infusion with staggered participant dosing
Cohort 4PlaceboSingle IV ascending dose infusion with staggered participant dosing
Cohort 5PlaceboSingle IV ascending dose infusion with staggered participant dosing
Cohort 7BIIB054Single IV ascending dose infusion with staggered participant dosing
Cohort 5BIIB054Single IV ascending dose infusion with staggered participant dosing
Cohort 6BIIB054Single IV ascending dose infusion with staggered participant dosing
Primary Outcome Measures
NameTimeMethod
Columbia Suicide Severity Rating Scale (C-SSRS)20 Weeks

The Columbia Suicide Severity Rating Scale, or C-SSRS, is a suicidal ideation rating scale created by researchers at Columbia University to evaluate suicidality.

Adverse events/serious adverse events (AEs/SAEs),20 Weeks

After a range of single BIIB054 doses administered as a single IV infusion in healthy participants and participants with early Parkinson's Disease, clinical laboratory test data, vital signs, neurological and physical examination findings, 12-lead electrocardiogram (ECG) data, and brain magnetic resonance imaging (MRI) findings will be used in the evaluation of AEs/SAEs.

Montreal Cognitive Assessment (MoCA)20 Weeks

The Montreal Cognitive Assessment MoCA is a brief cognitive screening tool for Mild Cognitive Impairment.

Secondary Outcome Measures
NameTimeMethod
Evaluate serum BIIB054 concentrations and PK parameters20 Weeks

Area under the concentration-time curve (AUC) from time zero extrapolated to infinity (0-∞), AUC from time 0 to time of the last measurable concentration (AUC0-tlast), maximum concentration (Cmax), time to Cmax (Tmax), elimination half-life (t1/2), and clearance (Cl), will be used to assess the serum PK profile of BIIB054 after single-dose administration.

evaluation of anti-BIIB054 antibodies in serum20 Weeks

evaluate the immunogenicity of BIIB054 after single-dose administration

Trial Locations

Locations (1)

Research Site

πŸ‡ΊπŸ‡Έ

Spokane, Washington, United States

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