MedPath

Age-Related Eye Disease Study 2 (AREDS2)

Phase 3
Completed
Conditions
Cataract
Age-related Macular Degeneration
Interventions
Dietary Supplement: Lutein/zeaxanthin
Dietary Supplement: DHA/EPA
Drug: Lutein/zeaxanthin and DHA/EPA
Registration Number
NCT00345176
Lead Sponsor
National Eye Institute (NEI)
Brief Summary

Oral supplementation with the Age-Related Eye Disease Study (AREDS) formulation (antioxidant vitamins C and E, beta carotene, and zinc) has been shown to reduce the risk of progression to advanced age-related macular degeneration (AMD). Observational data suggest that increased dietary intake of lutein + zeaxanthin (carotenoids), omega-3 long-chain polyunsaturated fatty acids (docosahexaenoic acid \[DHA\] + eicosapentaenoic acid \[EPA\]), or both might further reduce this risk. AREDS2 was designed to test whether adding lutein + zeaxanthin, DHA + EPA, or lutein + zeaxanthin and DHA + EPA to the AREDS formulation might further reduce the risk of progression to advanced AMD. A secondary goal was to test the effects of eliminating beta carotene and reducing zinc dose in the AREDS formulation.

Detailed Description

AREDS2 was a randomized, double-masked, placebo-controlled, 2x2 factorial trial evaluating the risks and benefits of adding lutein (10 mg) + zeaxanthin (2 mg), DHA (350 mg) + EPA (650 mg), or both to the AREDS formulation, which consisted of vitamins C (500 mg), vitamin E (400 international units), beta carotene (15 mg), zinc (80 mg as zinc oxide), and copper (2 mg as cupric oxide) for the treatment of progression to advanced AMD. The study enrolled 4,203 participants aged 50 to 85 years, with sufficiently clear ocular media to allow accurate assessment of AMD from fundus photographs. Subjects were enrolled on the basis of the AREDS Simplified Severity Scale for defining risk categories for development of advanced age-related macular degeneration. All participants were offered additional treatment with the original AREDS formulation (now considered standard of care) and 3 variations of this formula. These are: (1) no beta-carotene; (2) lower amount of zinc (25 mg); and (3) no beta-carotene and lower amount of zinc (25 mg). Eligible participants were followed for a minimum of five years.

Multiple ancillary studies were conducted using the parent study (AREDS2) data to explore:

1. Effects of oral supplementation of omega-3 fatty acids, lutein/zeaxanthin, zinc, and beta-carotene on cognitive function

1. Outcome is measured with a battery of tests administered over the telephone at baseline, and at years 2 and 4 of the study.

2. Primary outcome is the change in the composite score for the results of the cognitive function testing from baseline over time.

2. Effects of oral supplementation of omega-3 fatty acids, lutein/zeaxanthin on cardiovascular disease

a. Primary measure of cardiovascular morbidity and mortality

3. Effects of oral supplementation of omega-3 fatty acids, lutein/zeaxanthin on the peripheral retina

a. Primary outcome is the development of peripheral drusen, geographic atrophy, reticular pigmentary changes, and pseudoreticular drusen.

4. Association of genotype polymorphisms with age-related macular degeneration and cataract

a. Whole genome sequencing will be completed. Evaluation of association genetic associations with disease will be conducted using AREDS controls.

5. Association of genotype polymorphisms with progression of age-related macular degeneration

a. Whole genome sequencing is conducted. Progression from early to late and severe stages of AMD will be examined with the genotype data to evaluate the risks of progression associated with the genotype polymorphisms.

6. Association of genotype polymorphisms with dietary intake a. Whole genome sequencing is conducted. Progression from early to late and severe stages of AMD will be examined regarding potential interaction of the dietary intake with the genotype data to evaluate the risks of progression.

7. Association of genotype polymorphisms with AREDS2 supplements a. Interaction of genetic polymorphisms with AREDS2 supplements for progression to late AMD will be evaluated using the data from the whole genome sequencing project.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
4203
Inclusion Criteria
  • Men and women between the ages of 50 and 85 years
  • Macular status ranges from large drusen in both eyes or large drusen in one eye and advanced AMD (neovascular AMD or geographic atrophy) in the fellow eye
Exclusion Criteria
  • Ocular media not clear enough to allow good fundus photography

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Lutein/ZeaxanthinLutein/zeaxanthinlutein (10mg)/zeaxanthin (2 mg)
DHA/EPADHA/EPADHA (350 mg)/EPA (650 mg)
Lutein/Zeaxanthin + DHA/EPALutein/zeaxanthin and DHA/EPAlutein (10 mg)/zeaxanthin (2 mg) + DHA (350 mg)/EPA (650 mg)
Primary Outcome Measures
NameTimeMethod
Development of Advanced AMD in People at Moderate to High Risk for Progression.5 years of follow-up

Defined as central geographic atrophy or retinal features of choroidal neovascularization detected on central grading of the stereoscopic fundus photographs or a history of treatment for advanced AMD after study enrollment.

Secondary Outcome Measures
NameTimeMethod
Adverse Events5 years of follow-up

Safety outcomes included serious adverse events and mortality.

Progression to Cataract Surgery5 years of follow-up

The study examined the effects of lutein/zeaxanthin on progression to cataract surgery with data collected during regular telephone contacts and the annual study visits.

Progression to Moderate Vision Loss5 years of follow-up

Loss defined as \>/= 3 lines of letters from baseline or treatment for choroidal neovascularization

Trial Locations

Locations (84)

Retina Associates of Cleveland

🇺🇸

Youngstown, Ohio, United States

Massachusetts Eye and Ear Infirmary

🇺🇸

Boston, Massachusetts, United States

Case Western Reserve University

🇺🇸

Cleveland, Ohio, United States

Southern California Desert Retina Consultants, MC

🇺🇸

Palm Springs, California, United States

Center for Retina and Macular Disease

🇺🇸

Winter Haven, Florida, United States

VA Northern California Health Care System

🇺🇸

Martinez, California, United States

Ophthalmic Consultants of Boston

🇺🇸

Boston, Massachusetts, United States

University of Rochester Eye Institute

🇺🇸

Rochester, New York, United States

Retina-Vitreous Associates Medical Group

🇺🇸

Beverly Hills, California, United States

University Health Care - Mason Eye Institute

🇺🇸

Columbia, Missouri, United States

UMDNJ

🇺🇸

Newark, New Jersey, United States

Jules Stein Eye Institute

🇺🇸

Los Angeles, California, United States

Loma Linda University

🇺🇸

Loma Linda, California, United States

Manhattan Eye, Ear and Throat Hospital

🇺🇸

New York, New York, United States

Retina Group of Florida

🇺🇸

Ft. Lauderdale, Florida, United States

Georgia Retina, PC

🇺🇸

Decatur, Georgia, United States

University of Iowa

🇺🇸

Iowa City, Iowa, United States

Eldorado Retina Associates, PC

🇺🇸

Louisville, Colorado, United States

Emory University Eye Center

🇺🇸

Atlanta, Georgia, United States

The University of Illinois

🇺🇸

Chicago, Illinois, United States

Retina Consultants, PLLC

🇺🇸

Slingerlands, New York, United States

Northwestern University

🇺🇸

Chicago, Illinois, United States

NorthShore University HealthSystems

🇺🇸

Glenview, Illinois, United States

The Retina Institute

🇺🇸

St Louis, Missouri, United States

Ingalls Memorial Hospital

🇺🇸

Harvey, Illinois, United States

Ophthalmic Consultants of Long Island

🇺🇸

Lynbrook, New York, United States

The Research Foundation of SUNY/Stony Brook

🇺🇸

Stony Brook, New York, United States

Texas Retina Associates

🇺🇸

Lubbock, Texas, United States

Retina Center Northwest

🇺🇸

Silverdale, Washington, United States

University of Pittsburgh Medical Center

🇺🇸

Pittsburgh, Pennsylvania, United States

UT Southwestern Medical Center

🇺🇸

Dallas, Texas, United States

Baylor College of Medicine

🇺🇸

Houston, Texas, United States

Retina Consultants of Houston

🇺🇸

Houston, Texas, United States

Bascom Palmer Eye Institute

🇺🇸

Miami, Florida, United States

Duke University

🇺🇸

Durham, North Carolina, United States

West Coast Retina Medical Group, Inc

🇺🇸

San Francisco, California, United States

Pacific Eye Associates

🇺🇸

San Francisco, California, United States

Vanderbilt Eye Institute

🇺🇸

Nashville, Tennessee, United States

John Moran Eye Center

🇺🇸

Salt Lake City, Utah, United States

Mayo Clinic

🇺🇸

Rochester, Minnesota, United States

Colorado Retina Associates

🇺🇸

Denver, Colorado, United States

Kresge Eye Institute

🇺🇸

Detroit, Michigan, United States

Dean McGee Eye Institute

🇺🇸

Oklahoma City, Oklahoma, United States

University of Alabama at Birmingham

🇺🇸

Birmingham, Alabama, United States

Henry Ford Health System - Eye Care Services

🇺🇸

Detroit, Michigan, United States

Devers Eye Institute

🇺🇸

Portland, Oregon, United States

Retina Northwest, PC

🇺🇸

Portland, Oregon, United States

The Medical College of Wisconsin

🇺🇸

Milwaukee, Wisconsin, United States

National Eye Institute

🇺🇸

Bethesda, Maryland, United States

Paducah Retinal Center

🇺🇸

Paducah, Kentucky, United States

Retina Associates of Kentucky

🇺🇸

Lexington, Kentucky, United States

The Retina Group of Washington

🇺🇸

Fairfax, Virginia, United States

Western Carolina Retinal Associates

🇺🇸

Asheville, North Carolina, United States

Pennsylvania Retina Specialists, PC

🇺🇸

Camp Hill, Pennsylvania, United States

Scheie Eye Institute

🇺🇸

Philadelphia, Pennsylvania, United States

Penn State M.S. Hershey Medical Center

🇺🇸

Hershey, Pennsylvania, United States

Palmetto Retina Center

🇺🇸

Columbia, South Carolina, United States

Retina Vitreous Consultants

🇺🇸

Pittsburgh, Pennsylvania, United States

Sarasota Retina Institute

🇺🇸

Sarasota, Florida, United States

University of Florida

🇺🇸

Jacksonville, Florida, United States

Vision Research Foundation

🇺🇸

Traverse City, Michigan, United States

Washington University School of Medicine

🇺🇸

St. Louis, Missouri, United States

New York Eye and Ear Infirmary

🇺🇸

New York, New York, United States

Ohio State University

🇺🇸

Columbus, Ohio, United States

Shiley Eye Center - UCSD

🇺🇸

La Jolla, California, United States

Doheny Eye Institute

🇺🇸

Los Angeles, California, United States

Charlotte Eye Ear Nose and Throat Associates

🇺🇸

Charlotte, North Carolina, United States

Scott and White Memorial Hospital

🇺🇸

Temple, Texas, United States

Wills Eye Hospital/Mid Atlantic Retina

🇺🇸

Philadelphia, Pennsylvania, United States

Fletcher Allen Health Care

🇺🇸

Burlington, Vermont, United States

University of Wisconsin

🇺🇸

Madison, Wisconsin, United States

Wake Forest University Eye Center

🇺🇸

Winston-Salem, North Carolina, United States

Eye Foundation of Kansas City

🇺🇸

Kansas City, Missouri, United States

UNC Department of Ophthalmology

🇺🇸

Chapel Hill, North Carolina, United States

Mid-America Retina Consultants, PA

🇺🇸

Kansas City, Missouri, United States

Yale University Eye Center

🇺🇸

New Haven, Connecticut, United States

University of California, Davis

🇺🇸

Sacramento, California, United States

Jones Eye Institute - UAMS

🇺🇸

Little Rock, Arkansas, United States

Elman Retina Group

🇺🇸

Baltimore, Maryland, United States

Wilmer Eye Institute, Johns Hopkins Hospital

🇺🇸

Baltimore, Maryland, United States

Delaware Valley Retina Associates

🇺🇸

Lawrenceville, New Jersey, United States

Carolina Retina Center

🇺🇸

Columbia, South Carolina, United States

Southeastern Retina Associates, PC

🇺🇸

Knoxville, Tennessee, United States

University of Tennessee

🇺🇸

Memphis, Tennessee, United States

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