MedPath

High-Dose Melphalan Plus Peripheral Stem Cell Transplantation in Treating Patients With Primary Systemic Amyloidosis

Phase 2
Completed
Conditions
Multiple Myeloma and Plasma Cell Neoplasm
Registration Number
NCT00003353
Lead Sponsor
Eastern Cooperative Oncology Group
Brief Summary

RATIONALE: High-dose chemotherapy may destroy the amyloid-producing cells in bone marrow. Peripheral stem cell transplantation

PURPOSE: Phase II trial to study the effectiveness of high dose melphalan plus peripheral stem cell transplantation in treating patients who have primary systemic amyloidosis.

Detailed Description

OBJECTIVES: I. Assess the response rate and overall survival of patients with biopsy proven primary amyloidosis following treatment with myeloablative chemotherapy and hematopoietic stem cell reconstitution. II. Evaluate the toxicity of high dose melphalan in this patient population.

OUTLINE: Patients receive filgrastim (G-CSF) subcutaneously daily beginning on day 1 of the peripheral blood stem cell (PBSC) collection period and continuing until PBSC collection is completed. PBSC are collected beginning on day 5 of the collection period and continuing until the final target cell count is reached or for up to a maximum of 7 collections. If sufficient PBSCs are not harvested within a maximum of 7 collections, the patient is removed from the study. Within 30 days of PBSC collection, patients receive melphalan IV on day -1 of the infusion period and PBSC infusion on day 0. The infusion period continues until day 30. Patients receive G-CSF subcutaneously daily starting on day 1 and continuing until blood counts recover. Patients are followed every 3 months for 2 years, every 3 months for 3 additional years, and yearly thereafter.

PROJECTED ACCRUAL: A maximum of 33 patients will be accrued for this study over 2 years.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
Not specified
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (17)

CCOP - Illinois Oncology Research Association

🇺🇸

Peoria, Illinois, United States

CCOP - Scottsdale Oncology Program

🇺🇸

Scottsdale, Arizona, United States

University of Rochester Cancer Center

🇺🇸

Rochester, New York, United States

CCOP - Evanston

🇺🇸

Evanston, Illinois, United States

CCOP - Metro-Minnesota

🇺🇸

Saint Louis Park, Minnesota, United States

Ireland Cancer Center

🇺🇸

Cleveland, Ohio, United States

CCOP - Marshfield Medical Research and Education Foundation

🇺🇸

Marshfield, Wisconsin, United States

New England Medical Center Hospital

🇺🇸

Boston, Massachusetts, United States

Sylvester Cancer Center, University of Miami

🇺🇸

Miami, Florida, United States

Indiana University Cancer Center

🇺🇸

Indianapolis, Indiana, United States

Veterans Affairs Medical Center - Indianapolis (Roudebush)

🇺🇸

Indianapolis, Indiana, United States

Veterans Affairs Medical Center - Nashville

🇺🇸

Nashville, Tennessee, United States

Vanderbilt Cancer Center

🇺🇸

Nashville, Tennessee, United States

Mayo Clinic Cancer Center

🇺🇸

Rochester, Minnesota, United States

H. Lee Moffitt Cancer Center and Research Institute

🇺🇸

Tampa, Florida, United States

Medical College of Wisconsin

🇺🇸

Milwaukee, Wisconsin, United States

Veterans Affairs Medical Center - Milwaukee (Zablocki)

🇺🇸

Milwaukee, Wisconsin, United States

© Copyright 2025. All Rights Reserved by MedPath