MedPath

Shingles Prevention Study

Phase 3
Completed
Conditions
Herpes Zoster
Postherpetic Neuralgia
Interventions
Biological: Varicella-zoster vaccine
Biological: Placebo
Registration Number
NCT00007501
Lead Sponsor
US Department of Veterans Affairs
Brief Summary

The incidence and severity of HZ (or shingles), as well as the frequency and severity of its complications, increases markedly with increasing age. More than half of all cases occur in persons over the age of 60. Even without complications, HZ can interfere with an elderly patient's ability to perform essential activities of daily living, resulting in a loss of independence that is emotionally devastating and frequently irreversible. The most common complication of HZ in elderly persons is postherpetic neuralgia (PHN), which frequently results in disordered sleep, chronic fatigue, anxiety and severe depression. Antiviral therapy has a modest impact on the acute phase of HZ. However, it does not appear to prevent the development of PHN.

This study is a 5.5 year randomized, double-blind, placebo-controlled, efficacy trial to determine whether vaccination with live-attenuated Oka/Merck varicella-zoster decreases the incidence and/or severity of herpes zoster (HZ) and its complications in adults 60 years of age and older.

Detailed Description

Primary Hypothesis:

Immunization with live, attenuated (Oka/Merck) varicella-zoster vaccine will significantly reduce the burden of illness associated with herpes zoster (HZ).

Secondary Hypotheses:

Immunization with live, attenuated (Oka/Merck) varicella-zoster vaccine will reduce the incidence of postherpetic neuralgia (PHN).

Primary Outcomes:

The primary outcome is the burden of illness due to HZ defined by the area under the worst pain versus time curve measured during the 6 month period following HZ rash onset in subjects who develop of HZ. The burden of illness outcome is sensitive to the incidence, severity, and duration of HZ-associated pain. The secondary outcome is the incidence of PHN, where PHN is defined as HZ-associated pain rated as greater than or equal to 3 (on a 0 to 10 scale) persisting or appearing more than 30 days after the onset of the HZ rash.

Interventions:

Immunization with 0.5 ml, live, attenuated (Oka/Merck) varicella-zoster vaccine versus vaccine placebo.

Study Abstract:

The incidence and severity of HZ (or shingles), as well as the frequency and severity of its complications, increases markedly with increasing age. More than half of all cases occur in persons over the age of 60. Even without complications, HZ can interfere with an elderly patient's ability to perform essential activities of daily living, resulting in a loss of independence that is emotionally devastating and frequently irreversible. The most common complication of HZ in elderly persons is postherpetic neuralgia (PHN), which frequently results in disordered sleep, chronic fatigue, anxiety and severe depression. Antiviral therapy has a modest impact on the acute phase of HZ. However, it does not appear to prevent the development of PHN.

This study was a 5.5 year randomized, double-blind, placebo-controlled, efficacy trial to determine whether vaccination with live-attenuated Oka/Merck varicella-zoster decreases the incidence and/or severity of herpes zoster (HZ) and its complications in adults 60 years of age and older; 37,200 subjects over 60 years of age will be randomized at 22 sites to receive either vaccine or placebo. At least one third of the subjects were to be 70 years of age or older. Subjects were followed actively for HZ until at least 750 cases of HZ and at least 62 cases of PHN occurred. Subjects who developed HZ were evaluated for severity and duration of associated pain, extent and duration of rash, and for changes in quality of life associated with the disease for six months after the onset of HZ rash. All adverse events (serious and non-serious) occurring within 42 days after vaccination were recorded. Thereafter, serious adverse events were recorded if assessed as possibly related to the vaccination. An adverse event substudy was to enroll 6000 subjects for recording all adverse events on a vaccination Report Card. Substudy participants were also followed for any hospital admissions during the study.

The study was initiated in December 1998. Patient recruitment began in November 1998 at one site, at 20 sites between February 1999 and July 1999, and at one site that was added in January 2000. On September 26, 2001, enrollment in the study was completed with 38,456 randomized subjects. The time point for the study definition of PHN was changed by protocol amendment from 30 days to 90 days after HZ rash onset. A formal sample size re-estimation was performed in June 2003. The Executive Committee and DSMB reviewed these results and approved the increase in event size from 400 to 750 evaluable cases of HZ for the primary endpoint. It was projected that the number of evaluable cases of HZ for the primary endpoint and the number of evaluable cases of PHN for the secondary (co-primary) endpoint would be observed by the end of September 2003. Therefore, the Study initiated its closeout plan beginning in October 2004. Follow-up of the last suspected case of HZ was completed in March 2004 and closeout interviews for the more than 37,000 surviving subjects were completed as of April 28, 2004.

The results of the main efficacy and safety analyses were unblinded on December 1, 2004, and presented to the DSMB, Executive Committee, and representatives for Merck \& Co., Inc. Letters were sent to the study subjects informing them of the overall results and the treatment they received. The main manuscript was published in the New England Journal of Medicine (June 2005; 352:2271-84). The vaccine was approved for the prevention of shingles by the FDA on May 25, 2006. The main efficacy study is closed. Additionally, three substudies have been conducted:

A substudy (CSP#403B) was initiated in November 2005 to offer investigational zoster vaccine to the placebo recipients of CSP#403. Vaccination was completed in March 2007 with 13,681 (75%) of the placebo recipients vaccinated. This substudy is closed. The safety results from the substudy were published in the Journal of Infectious Diseases (J Infect Dis. 2013 May 31 epub).

A short-term persistence substudy (CSP#403A) was initiated in September 2004 to extend the follow-up vaccine and placebo recipients to assess the longer term effectiveness of the vaccine. This substudy bridged the period between the end of the efficacy study and the vaccination of placebo recipients and the initiation of a long-term persistence study. The study enrolled 14,270 subjects and completed follow-up in May 2007. This substudy is closed and is in ongoing analysis. The primary results for this study were published in Clinical Infectious Diseases (Clin Infect Dis. 2012 Nov 15;55(10):1320-1328)

CSP#403C, the Long-Term Persistence Substudy, was initiated in March 2006 and enrolled 6867 vaccine recipients from the main efficacy study. Enrollment was restricted to vaccine recipients from the main efficacy study with no history of herpes zoster. This study was initiated to complete an additional five-years of follow-up post-vaccination. The objective of this study was to estimate the longer-term durability of zoster vaccine efficacy by following a cohort of vaccine recipients from the primary efficacy study for three study outcomes: 1) the incidence of herpes zoster, 2) the incidence of postherpetic neuralgia (PHN), and 3) the burden of illness (BOI) due to herpes zoster. The study completed surveillance for new cases of herpes zoster as of December 2010 and completed the follow-up of the last case of herpes zoster in February 2011. All study sites have been closed out. This substudy has been completed and is in the final analysis phase.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
38456
Inclusion Criteria
  • Adults 60 years of age and older.
  • History of Chickenpox.
  • Have given written informed consent prior to enrollment.
  • History of varicella or long-term (greater than or equal to 30 years) residence in the continental USA.
Exclusion Criteria
  • No history of shingles, no current history of immune suppression (e.g. malignancy or neoplastic disease, corticosteroid therapy).
  • No immunosuppression resulting from disease (e.g., malignancy; HIV infection), corticosteroids (except intermittent topical or inhaled corticosteroid [greater than 800 mcg/day beclomethasone dipropionate or equivalent]), or other immunosuppressive/cytotoxic therapy (cancer chemotherapy or organ transplantation).
  • No active neoplastic disease (except local skin cancer or other malignancies [e.g., prostate cancer] that are stable in the absence of immunosuppressive/cytotoxic therapy).
  • No prior Herpes Zoster.
  • No prior receipt of varicella vaccine.
  • No allergic sensitivity to neomycin.
  • No history of anaphylactoid reaction to gelatin.
  • No significant underlying illness that would be expected to prevent completion of the study (e.g., life-threatening disease likely to limit survival to less than 5 years).
  • Not ambulatory (must not be bed-ridden or homebound).
  • No receipt of immune globulin or any other blood product within 3 months before or planned during the 3-5 year study period.
  • No receipt of any other immunizations within one month before study vaccination (2 weeks in the case of inactivated influenza vaccines or other non-replicating immunization products [e.g., dT, pneumococcal vaccine, hepatitis A vaccine, hepatitis B vaccine]), or scheduled within 6 weeks after study vaccination.
  • Not currently receiving antiviral therapy.
  • No other condition (e.g., extensive psoriasis, chronic pain syndrome, cognitive impairment, severe hearing loss) that, in the opinion of the investigator, might interfere with the evaluations required by the study.
  • No intercurrent illness (e.g., urinary tract infection, influenza) that might interfere with the interpretation of the study.
  • No females who are pre-menopausal.
  • No subjects unlikely to adhere to protocol follow-up.
  • No subjects involved in a conflicting (vaccine or investigational drug) clinical trial.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Arm 1Varicella-zoster vaccinevaricella-zoster vaccine
Arm 2Placebovaccine placebo
Primary Outcome Measures
NameTimeMethod
Reduce burden of illness due to herpes zoster (HZ)Incidence of postherpetic neuralgia (PHN), where PHN is defined as HZ-associated pain greater than or equal to 3 persisting or appearing more than 30 days after the onset of the HZ rash
Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (22)

VA Maryland Health Care System, Baltimore

🇺🇸

Baltimore, Maryland, United States

VA Medical Center, Birmingham

🇺🇸

Birmingham, Alabama, United States

University of Texas at San Antonio

🇺🇸

San Antonio, Texas, United States

Vanderbilt University

🇺🇸

Nashville, Tennessee, United States

VA Palo Alto Health Care System

🇺🇸

Palo Alto, California, United States

VA San Diego Healthcare System, San Diego

🇺🇸

San Diego, California, United States

University of Colorado

🇺🇸

Denver, Colorado, United States

James A. Haley Veterans Hospital, Tampa

🇺🇸

Tampa, Florida, United States

Edward Hines, Jr. VA Hospital

🇺🇸

Hines, Illinois, United States

VA Medical Center, Lexington

🇺🇸

Lexington, Kentucky, United States

VA Medical Center, Jamaica Plain Campus

🇺🇸

Boston, Massachusetts, United States

VA Ann Arbor Healthcare System

🇺🇸

Ann Arbor, Michigan, United States

VA Medical Center, Minneapolis

🇺🇸

Minneapolis, Minnesota, United States

New York Harbor HCS

🇺🇸

New York, New York, United States

New Mexico VA Health Care System, Albuquerque

🇺🇸

Albuquerque, New Mexico, United States

VA Medical Center, St Louis

🇺🇸

St Louis, Missouri, United States

VA Medical Center, Northport

🇺🇸

Northport, New York, United States

Rochester, NY (NIH)

🇺🇸

Rochester, New York, United States

Baylor University

🇺🇸

Houston, Texas, United States

VA Medical Center, Durham

🇺🇸

Durham, North Carolina, United States

VA Puget Sound Health Care System, Seattle

🇺🇸

Seattle, Washington, United States

NIH-NIAID (Bethesda, MD)

🇺🇸

Bethesda, Maryland, United States

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