MedPath

Testing the Role of FDG-PET/CT to Predict Response to Therapy Prior to Surgery for HER2-positive Breast Cancer, The DIRECT Trial

Phase 2
Recruiting
Conditions
Anatomic Stage II Breast Cancer AJCC v8
Anatomic Stage III Breast Cancer AJCC v8
Invasive Breast Carcinoma
HER2-Positive Breast Carcinoma
Interventions
Drug: Chemotherapy
Procedure: Computed Tomography
Other: Fludeoxyglucose F-18
Procedure: Positron Emission Tomography
Procedure: Surgical Procedure
Registration Number
NCT05710328
Lead Sponsor
ECOG-ACRIN Cancer Research Group
Brief Summary

This phase II trial tests how well an imaging procedure called fludeoxyglucose F-18 (FDG) positron emission tomography/computed tomography (PET/CT) works in predicting response to standard of care chemotherapy prior to surgery in patients with HER2-positive stage IIa-IIIc breast cancer. FDG is a radioactive tracer that is given in a vein before PET/CT imaging and helps to identify areas of active cancer. PET and CT are imaging techniques that make detailed, computerized pictures of areas inside the body. The use of FDG-PET/CT may help doctors better decide if a patient needs more or less treatment before surgery in order to get the best response. This study evaluates whether FDG-PET/CT is useful in predicting a patient's response to standard of care chemotherapy.

Detailed Description

PRIMARY OBJECTIVE:

I. To estimate the negative predictive value (NPV) of neoadjuvant interim (ni)FDG-PET/CT for pathologic complete response (pCR), using delta maximum standardized uptake value corrected for lean body mass day 15 (deltaSULmaxD15), completed through central review, of the primary breast cancer at a threshold of 40%, in patients treated with neoadjuvant HER2-directed therapy.

SECONDARY OBJECTIVES:

I. To estimate the sensitivity, specificity, and positive predictive value (PPV) of niFDG-PET/CT for pCR, using deltaSULmaxD15 of the primary breast cancer at a threshold of 40%, in patients treated with neoadjuvant HER2-directed therapy.

II. To evaluate the performance of niFDG-PET/CT, using deltaSULmaxD15 of the primary breast cancer at a threshold of 40%, as a predictor of 3-year event-free survival (EFS) from time of study registration.

EXPLORATORY OBJECTIVES:

I. To estimate the NPV of niFDG-PET/CT for pCR, using deltaSULmaxD15 of the primary breast cancer at a grid of alternative thresholds ranging from 30% to 60%, in patients treated with neoadjuvant HER2-directed therapy.

II. To compare deltaSULmaxD15 using automated image analysis of FDG-PET/CT by AutoPERCIST (trademark) to standard PET analysis software.

OUTLINE:

Patients receive FDG intravenously (IV), undergo PET/CT, receive standard of care chemotherapy, and undergo standard of care surgery on study.

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
235
Inclusion Criteria
  • Patients (all genders) must be >= 18 years of age.

  • Patient must have the ability to understand and the willingness to sign a written informed consent document. Patients with impaired decision-making capacity (IDMC) who have a legally authorized representative (LAR) or caregiver and/or family member available will also be considered eligible.

  • Patient must have an Eastern Cooperative Oncology Group (ECOG) performance status of 0-2.

  • Patient must have histologically confirmed HER2-positive primary invasive breast carcinoma by American Society of Clinical Oncology (ASCO)/College of American Pathologists (CAP) guidelines that has been determined by local testing.

  • Patient must have known (either positive or negative) hormone receptor (estrogen receptor [ER] or progesterone receptor [PR]) status by local testing, per ASCO/CAP guidelines. Patients with either hormone receptor-positive or hormone receptor- negative HER2-positive breast cancer are eligible.

  • Patient must have American Joint Committee on Cancer (AJCC) 8th Edition stage IIa-IIIc according to anatomic staging table at diagnosis and below criteria.

    • Patients without nodal involvement (cN0) are eligible if T size > 2.0 cm (T2-4)
    • Patients with nodal involvement (cN1-3) are eligible if T2-4
    • Patients with clinical T4d are not eligible
  • Patients with bilateral invasive breast cancers are eligible if both cancers are HER2-positive and at least one meets all protocol eligibility criteria and neither cancer renders the patient ineligible.

  • Patients with multiple ipsilateral invasive tumors are eligible as long as all tumors are HER2-positive and at least one tumor focus meets all eligibility criteria. Multiple lesions that appear part of the same index tumor do not require additional biopsy/HER2 testing.

  • Patient must plan to start a standard neoadjuvant pertuzumab (or other biosimilars) based regimen.

  • Patients with a prior or concurrent malignancy whose natural history or treatment does not have the potential to interfere with the safety or efficacy assessment of this imaging intervention are eligible for this trial.

  • Patients with human immunodeficiency virus (HIV) on effective anti-retroviral therapy with undetectable viral load within 6 months of registration are eligible for this trial.

  • Patient must be participating in the trial at an institution which has agreed to perform the imaging research studies, completed the Eastern Cooperative Oncology Group-American College of Radiology Imaging Network Cancer Center Group (ECOG-ACRIN) defined PET/CT scanner qualification procedures and received ECOG-ACRIN PET/CT scanner approval.

    • For patients who completed the baseline (T0) FDG-PET/CT PRIOR to registration, neoadjuvant pertuzumab-based regimen must start after study registration and within 21 days after the T0 scan.

      • Patients must not have used colony stimulating growth factors within 14 days prior to completing a T0 scan done prior to registration.
Exclusion Criteria
  • Patient must not have any prior treatment for the current breast cancer, including surgery, chemotherapy, hormonal therapy, radiation or experimental therapy.

  • Patient must not be pregnant or breast-feeding due to the potential harm to an unborn fetus and possible risk for adverse events in nursing infants with the teratogenic effects of FDG in addition to the radiation exposure during PET/CT. All patients of childbearing potential must have a blood test or urine study within 7 days prior to registration to rule out pregnancy.

    • NOTE: A pregnancy test within 7 days prior to the T0 scan is also required but will only need to be done if a) the T0 scan is completed after study registration and b) if the pregnancy test done prior to registration is completed outside of the 7-day window.

A patient of childbearing potential is defined as anyone, regardless of sexual orientation or whether they have undergone tubal ligation, who meets the following criteria: 1) has achieved menarche at some point, 2) has not undergone a hysterectomy or bilateral oophorectomy; or 3) has not been naturally postmenopausal (amenorrhea following cancer therapy does not rule out childbearing potential) for at least 24 consecutive months (i.e., has had menses at any time in the preceding 24 consecutive months).

  • Patient must not have any contraindication to FDG-PET/CT imaging which includes routine glucose values > 200 mg/dL and severe claustrophobia.

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
Diagnostic (FDG-PET/CT scan)ChemotherapyPatients receive FDG IV, undergo PET/CT, receive standard of care chemotherapy, and undergo standard of care surgery on study.
Diagnostic (FDG-PET/CT scan)Computed TomographyPatients receive FDG IV, undergo PET/CT, receive standard of care chemotherapy, and undergo standard of care surgery on study.
Diagnostic (FDG-PET/CT scan)Fludeoxyglucose F-18Patients receive FDG IV, undergo PET/CT, receive standard of care chemotherapy, and undergo standard of care surgery on study.
Diagnostic (FDG-PET/CT scan)Positron Emission TomographyPatients receive FDG IV, undergo PET/CT, receive standard of care chemotherapy, and undergo standard of care surgery on study.
Diagnostic (FDG-PET/CT scan)Surgical ProcedurePatients receive FDG IV, undergo PET/CT, receive standard of care chemotherapy, and undergo standard of care surgery on study.
Primary Outcome Measures
NameTimeMethod
Negative predictive value of neoadjuvant interim (ni) fludeoxyglucose F-18 (FDG) positron emission tomography/computed tomography (PET/CT) for pathologic complete response (pCR)Up to 5 years

The analysis set for this objective will comprise all patients who enrolled in the study and had a FDG-PET/CT scan at T0 and T1 timepoint. The negative predictive value is defined as the probability that pCR will not be achieved by study participants who experience a using delta maximum standardized uptake value corrected for lean body mass day 15 (deltaSULmaxD15) below 40% and will be estimated via an exact, two-sided 95% confidence interval.

Secondary Outcome Measures
NameTimeMethod
Performance of niFDG-PET/CT as predictor of 3-year event-free survivalUp to 5 years

Using deltaSULmaxD15 of the primary breast cancer at a threshold of 40%. The analysis set for this objective will be the same as for the primary objective. The analysis will compare estimates of 3-year event-free survival between participants with deltaSULmaxD15 above and below the 40% threshold using a log-rank test.

Specificity of niFDG-PET/CT for pCRUp to 5 years

The analysis set for this objective will be the same as for the primary objective. The estimation approach will also be similar.

Sensitivity of niFDG-PET/CT for pCRUp to 5 years

The analysis set for this objective will be the same as for the primary objective. The estimation approach will also be similar.

Positive predictive value of niFDG-PET/CT for pCRUp to 5 years

The analysis set for this objective will be the same as for the primary objective. The estimation approach will also be similar.

Trial Locations

Locations (102)

Johns Hopkins University/Sidney Kimmel Cancer Center

🇺🇸

Baltimore, Maryland, United States

Centro Comprensivo de Cancer de UPR

🇵🇷

San Juan, Puerto Rico

Los Angeles General Medical Center

🇺🇸

Los Angeles, California, United States

Sibley Memorial Hospital

🇺🇸

Washington, District of Columbia, United States

Northwestern University

🇺🇸

Chicago, Illinois, United States

Mayo Clinic in Florida

🇺🇸

Jacksonville, Florida, United States

Carle Physician Group-Effingham

🇺🇸

Effingham, Illinois, United States

Northwestern Medicine Lake Forest Hospital

🇺🇸

Lake Forest, Illinois, United States

USC / Norris Comprehensive Cancer Center

🇺🇸

Los Angeles, California, United States

Carle Physician Group-Mattoon/Charleston

🇺🇸

Mattoon, Illinois, United States

Hawaii Cancer Care - Westridge

🇺🇸

'Aiea, Hawaii, United States

Saint John's Cancer Institute

🇺🇸

Santa Monica, California, United States

Wilcox Memorial Hospital and Kauai Medical Clinic

🇺🇸

Lihue, Hawaii, United States

Saint Luke's Cancer Institute - Twin Falls

🇺🇸

Twin Falls, Idaho, United States

Northwestern Medicine Cancer Center Delnor

🇺🇸

Geneva, Illinois, United States

Carle at The Riverfront

🇺🇸

Danville, Illinois, United States

Bryn Mawr Health Center

🇺🇸

Newtown Square, Pennsylvania, United States

Inspira Medical Center Vineland

🇺🇸

Vineland, New Jersey, United States

MetroHealth Medical Center

🇺🇸

Cleveland, Ohio, United States

Bryn Mawr Hospital

🇺🇸

Bryn Mawr, Pennsylvania, United States

Mercy Hospital

🇺🇸

Coon Rapids, Minnesota, United States

MD Anderson Cancer Center at Cooper-Voorhees

🇺🇸

Voorhees, New Jersey, United States

Geisinger Wyoming Valley/Henry Cancer Center

🇺🇸

Wilkes-Barre, Pennsylvania, United States

Cooper Hospital University Medical Center

🇺🇸

Camden, New Jersey, United States

Saint Joseph's Regional Medical Center

🇺🇸

Paterson, New Jersey, United States

Ohio State University Comprehensive Cancer Center

🇺🇸

Columbus, Ohio, United States

Morristown Medical Center

🇺🇸

Morristown, New Jersey, United States

Community Medical Center

🇺🇸

Scranton, Pennsylvania, United States

Nebraska Medicine-Bellevue

🇺🇸

Bellevue, Nebraska, United States

University of Washington Medical Center - Montlake

🇺🇸

Seattle, Washington, United States

Baptist Memorial Hospital and Cancer Center-Memphis

🇺🇸

Memphis, Tennessee, United States

Marshfield Medical Center-EC Cancer Center

🇺🇸

Eau Claire, Wisconsin, United States

Aurora Cancer Care-Southern Lakes VLCC

🇺🇸

Burlington, Wisconsin, United States

San Juan Community Oncology Group

🇵🇷

San Juan, Puerto Rico

Saint Vincent Hospital Cancer Center Green Bay

🇺🇸

Green Bay, Wisconsin, United States

Guthrie Medical Group PC-Robert Packer Hospital

🇺🇸

Sayre, Pennsylvania, United States

Marshfield Medical Center-Marshfield

🇺🇸

Marshfield, Wisconsin, United States

Marshfield Medical Center-River Region at Stevens Point

🇺🇸

Stevens Point, Wisconsin, United States

FHCC South Lake Union

🇺🇸

Seattle, Washington, United States

Doctors Cancer Center

🇵🇷

Manati, Puerto Rico

Lankenau Medical Center

🇺🇸

Wynnewood, Pennsylvania, United States

Marshfield Clinic - Wisconsin Rapids Center

🇺🇸

Wisconsin Rapids, Wisconsin, United States

Fred Hutchinson Cancer Center

🇺🇸

Seattle, Washington, United States

Marshfield Clinic-Minocqua Center

🇺🇸

Minocqua, Wisconsin, United States

Aurora Health Care Germantown Health Center

🇺🇸

Germantown, Wisconsin, United States

Marshfield Medical Center - Ladysmith

🇺🇸

Ladysmith, Wisconsin, United States

San Juan City Hospital

🇵🇷

San Juan, Puerto Rico

Cancer Center at Saint Joseph's

🇺🇸

Phoenix, Arizona, United States

Wayne State University/Karmanos Cancer Institute

🇺🇸

Detroit, Michigan, United States

Abbott-Northwestern Hospital

🇺🇸

Minneapolis, Minnesota, United States

University of Oklahoma Health Sciences Center

🇺🇸

Oklahoma City, Oklahoma, United States

Huntsman Cancer Institute/University of Utah

🇺🇸

Salt Lake City, Utah, United States

Mercy Hospital South

🇺🇸

Saint Louis, Missouri, United States

CoxHealth South Hospital

🇺🇸

Springfield, Missouri, United States

University of Alabama at Birmingham Cancer Center

🇺🇸

Birmingham, Alabama, United States

Mayo Clinic in Rochester

🇺🇸

Rochester, Minnesota, United States

Nebraska Medicine-Village Pointe

🇺🇸

Omaha, Nebraska, United States

University of Nebraska Medical Center

🇺🇸

Omaha, Nebraska, United States

Aurora Saint Luke's Medical Center

🇺🇸

Milwaukee, Wisconsin, United States

United Hospital

🇺🇸

Saint Paul, Minnesota, United States

Castle Medical Center

🇺🇸

Kailua, Hawaii, United States

Northwestern Medicine Cancer Center Kishwaukee

🇺🇸

DeKalb, Illinois, United States

Minnesota Oncology Hematology PA-Woodbury

🇺🇸

Woodbury, Minnesota, United States

Northwestern Medicine Cancer Center Warrenville

🇺🇸

Warrenville, Illinois, United States

Dana-Farber Cancer Institute

🇺🇸

Boston, Massachusetts, United States

Minnesota Oncology - Burnsville

🇺🇸

Burnsville, Minnesota, United States

Carle Cancer Center

🇺🇸

Urbana, Illinois, United States

Baptist Memorial Hospital and Cancer Center-Desoto

🇺🇸

Southhaven, Mississippi, United States

Aurora Sinai Medical Center

🇺🇸

Milwaukee, Wisconsin, United States

Indu and Raj Soin Medical Center

🇺🇸

Beavercreek, Ohio, United States

Saint Vincent Hospital Cancer Center at Saint Mary's

🇺🇸

Green Bay, Wisconsin, United States

Baptist Memorial Hospital and Cancer Center-Collierville

🇺🇸

Collierville, Tennessee, United States

Geisinger Medical Center

🇺🇸

Danville, Pennsylvania, United States

Paoli Memorial Hospital

🇺🇸

Paoli, Pennsylvania, United States

Marshfield Medical Center-Rice Lake

🇺🇸

Rice Lake, Wisconsin, United States

Aurora West Allis Medical Center

🇺🇸

West Allis, Wisconsin, United States

Marshfield Medical Center - Weston

🇺🇸

Weston, Wisconsin, United States

Inspira Medical Center Mullica Hill

🇺🇸

Mullica Hill, New Jersey, United States

Kettering Medical Center

🇺🇸

Kettering, Ohio, United States

Minnesota Oncology Hematology PA-Maplewood

🇺🇸

Maplewood, Minnesota, United States

Baptist Memorial Hospital and Cancer Center-Oxford

🇺🇸

Oxford, Mississippi, United States

Park Nicollet Clinic - Saint Louis Park

🇺🇸

Saint Louis Park, Minnesota, United States

Roswell Park Cancer Institute

🇺🇸

Buffalo, New York, United States

Marshfield Medical Center - Neillsville

🇺🇸

Neillsville, Wisconsin, United States

Cancer Center-Metro Medical Center Bayamon

🇵🇷

Bayamon, Puerto Rico

Hawaii Cancer Care Inc - Waterfront Plaza

🇺🇸

Honolulu, Hawaii, United States

Queen's Cancer Cenrer - POB I

🇺🇸

Honolulu, Hawaii, United States

Queen's Medical Center

🇺🇸

Honolulu, Hawaii, United States

University of Hawaii Cancer Center

🇺🇸

Honolulu, Hawaii, United States

Queen's Cancer Center - Kuakini

🇺🇸

Honolulu, Hawaii, United States

Virginia Commonwealth University/Massey Cancer Center

🇺🇸

Richmond, Virginia, United States

Kapiolani Medical Center for Women and Children

🇺🇸

Honolulu, Hawaii, United States

The James Graham Brown Cancer Center at University of Louisville

🇺🇸

Louisville, Kentucky, United States

Louisiana State University Health Science Center

🇺🇸

New Orleans, Louisiana, United States

University Medical Center New Orleans

🇺🇸

New Orleans, Louisiana, United States

Dell Seton Medical Center at The University of Texas

🇺🇸

Austin, Texas, United States

Montefiore Medical Center-Einstein Campus

🇺🇸

Bronx, New York, United States

University of Texas at Austin

🇺🇸

Austin, Texas, United States

UNC Lineberger Comprehensive Cancer Center

🇺🇸

Chapel Hill, North Carolina, United States

University of Wisconsin Carbone Cancer Center - University Hospital

🇺🇸

Madison, Wisconsin, United States

Riddle Memorial Hospital

🇺🇸

Media, Pennsylvania, United States

Chester County Hospital

🇺🇸

West Chester, Pennsylvania, United States

© Copyright 2025. All Rights Reserved by MedPath