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Clinical Trials/NCT05099874
NCT05099874
Recruiting
N/A

Feasibility and Efficacy of Attentional-Control Training in Sickle Cell Disease

Children's National Research Institute1 site in 1 country20 target enrollmentDecember 20, 2022

Overview

Phase
N/A
Intervention
Not specified
Conditions
Sickle Cell Disease
Sponsor
Children's National Research Institute
Enrollment
20
Locations
1
Primary Endpoint
EndeavorRx feasibility assessed by patient/family interest
Status
Recruiting
Last Updated
last year

Overview

Brief Summary

Children with sickle cell disease (SCD) exhibit significantly reduced cognitive functioning (often difficulties with attention) compared to peers and siblings without SCD. EndeavorRx (Akili Interactive Labs: Boston, MA) is an FDA-approved home-based, electronic attentional-control training program designed to treat attention problems in youth. Users access EndeavorRx on a tablet device for 25-30 minutes each day, 5 days per week, for 4 weeks. The program involves training in a game-like environment that repeatedly challenges attentional-control abilities and adapts to user performance, becoming more difficult over time as performance improves. This pilot study is examining the feasibility, acceptability, and preliminary efficacy of EndeavorRx in a sample of 20 children with SCD ages 8-16 who are being treated with chronic blood transfusion therapy.

Detailed Description

Children with sickle cell disease (SCD) exhibit significantly reduced cognitive functioning compared to peers and siblings without SCD. Cognitive deficits are greatest among those with severe SCD genotypes, persistent anemia, and strokes and these deficits worsen over time. These deficits often manifest as difficulties with executive functioning and attention due to the predominance of cerebral infarcts (\>90%) that occur in the frontal cortex. Reduced capacity to engage such cognitive skills has significant real-world implications, leading to disruption to academic achievement and attainment, vocational outcomes, and quality of life. EndeavorRx (Akili Interactive Labs: Boston, MA) is an FDA-approved home-based, electronic attentional-control training program designed to treat attention problems in youth. Users access EndeavorRx on a tablet device for 25-30 minutes each day, 5 days per week, for 4 weeks. The program involves training in a game-like environment that repeatedly challenges attentional-control abilities and adapts to user performance, becoming more difficult over time as performance improves. Data support effects of EndeavorRx on performance-based and parent-reported measures of attention in youth with Attention-Deficit/Hyperactivity Disorder (ADHD). Given the similarities in attentional functioning among youth with ADHD and those with SCD, EndeavorRx holds promise as an intervention for patients experiencing SCD-related cognitive deficits. This pilot study is examining the feasibility, acceptability, and preliminary efficacy of EndeavorRx in a sample of 20 children with SCD ages 8-16 who are being treated with chronic blood transfusion therapy due to an identified high risk of stroke or as a preventive measure to protect against additional stroke events.

Registry
clinicaltrials.gov
Start Date
December 20, 2022
End Date
December 2025
Last Updated
last year
Study Type
Interventional
Study Design
Single Group
Sex
All

Investigators

Sponsor
Children's National Research Institute
Responsible Party
Principal Investigator
Principal Investigator

Steven J. Hardy

Associate Professor of Psychiatry and Behavioral Sciences

Children's National Research Institute

Eligibility Criteria

Inclusion Criteria

  • diagnosis of SCD
  • ages 8-16 years
  • maintained on monthly blood transfusions consistently for at least 3 months.
  • patients will be proceed to the intervention phase only if they have a T-score \> 75th percentile for Omission Errors on the Conners' Continuous Performance Test, 3rd Edition (CPT-3) or a T-score \> 75th percentile for the Inattention subscale of the ADHD Rating Scale, Fifth Edition (ADHD-RS-V).

Exclusion Criteria

  • estimated Intelligence Quotient \< 70
  • motor, visual, or auditory impairment that prevents computer use
  • known diagnosis of a mental health condition that precludes, or takes treatment precedence over, participation in cognitive training
  • history of photosensitive seizures
  • insufficient English fluency.

Outcomes

Primary Outcomes

EndeavorRx feasibility assessed by patient/family interest

Time Frame: Approximately 10 months

Feasibility will be determined by examining the proportion of eligible patients/families approached about the study who enroll.

EndeavorRx feasibility assessed by reports of technical ease-of-use and satisfaction

Time Frame: Approximately 4 weeks from start of intervention

Feasibility will be determined by examining parent and child reports of technical ease-of-use and satisfaction.

EndeavorRx feasibility assessed by program completion rates

Time Frame: Approximately 4 weeks per participant

Feasibility will be evaluated by examining the proportion of the sample that completes at least 60 EndeavorRx missions (50%).

Secondary Outcomes

  • Inattention assessed by change in Omission Errors on the Conners' Continuous Performance Test, 3rd Edition (CPT-3)(Approximately 4 weeks from start of intervention)
  • Inattention assessed by change in the Inattention subscale of the ADHD Rating Scale, Fifth Edition (ADHD-RS-V)(Approximately 4 weeks from start of intervention)

Study Sites (1)

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