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First-in-human Study With Ascending Single Intra-articular Doses of GZ389988 in Patients With Painful Osteoarthritis of the Knee

Phase 1
Completed
Conditions
Osteoarthritis
Interventions
Drug: placebo
Registration Number
NCT02424942
Lead Sponsor
Genzyme, a Sanofi Company
Brief Summary

Primary Objective:

To assess the safety and tolerability of ascending single intraarticular doses of GZ389988 in patients with painful osteoarthritis (OA) of the knee.

Secondary Objectives:

To assess the pharmacokinetic (PK) parameters of ascending single intraarticular doses of GZ389988 in patients with painful OA of the knee.

To obtain preliminary pharmacodynamic evaluation of ascending single intraarticular doses of GZ389988 in patients with painful OA of the knee.

Detailed Description

Screening will be performed within 28 days of dosing. Following the single dose of study medication, the study period for each patient will be 84 ± 7 days up to the end-of-study visit.

Total duration for one patient will be up to 17 weeks (up to the end-of-study visit), not including the long term observational safety follow-up by phone call for 12 additional weeks.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
28
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
PlaceboplaceboSingle intraarticular injection of placebo for GZ389988 in the knee joint
GZ389988GZ389988Single intraarticular injection of GZ389988 in the knee joint
Primary Outcome Measures
NameTimeMethod
Proportion of patients with adverse eventsUp to Day 84 after single intraarticular dose of GZ389988
Proportion of patients with serious adverse events12 additional weeks after day 84 (by phone calls)
Secondary Outcome Measures
NameTimeMethod
Apparent volume of distribution (Vz/F) of single dose GZ389988 IA24 timepoints up to Day 84
Maximum plasma concentration (Cmax) of GZ389988 single dose intraarticular (IA)24 timepoints up to Day 84
Area under the curve from time zero to last quantifiable concentration (AUClast) of single dose GZ389988 IA24 timepoints up to Day 84
Area under the curve (AUC) of single dose GZ389988 IA24 timepoints up to Day 84
Plasma elimination half-life (t1/2z) of single dose GZ389988 IA24 timepoints up to Day 84
Time to peak plasma concentration (tmax) of single dose GZ389988 IA24 timepoints up to Day 84
Time curve from administration to last measurement (tlast) of single dose GZ389988 IA24 timepoints up to Day 84
Apparent total body clearance(CL/F) of single dose GZ389998 IA24 timepoints up to Day 84
Synovial fluid concentrations (if possible) of single dose GZ389988 IA3 timepoints up to Day 84
Change from baseline in WOMAC index (total score)Over 1, 2, 3, 4, 6, 8, 10, and 12 weeks following the single intraarticular injection
Change from baseline in WOMAC pain (including WOMAC A1 pain subscores)Over 1, 2, 3, 4, 6, 8, 10, and 12 weeks following the single intraarticular injection
Change from baseline in WOMAC stiffness subscoreOver 1, 2, 3, 4, 6, 8, 10, and 12 weeks following the single intraarticular injection
Change from baseline in WOMAC physical function subscoreOver 1, 2, 3, 4, 6, 8, 10, and 12 weeks following the single intraarticular injection

Trial Locations

Locations (1)

Investigational Site Number 276001

🇩🇪

Berlin, Germany

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