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THERAPEUTIC EFFECTIIVENESS OF N-ACETYL-CYSTEINE AND ASCORBIC ACID IN PATIENTS WITH ALKAPTONURIA-OCHRONOSIS - Acetilcisteina-Ocronosi-SI/2009

Conditions
patient affected by alkaptonuria-ocronosis
Registration Number
EUCTR2009-012707-26-IT
Lead Sponsor
AZIENDA OSPEDALIERA SENESE
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
ot Recruiting
Sex
All
Target Recruitment
50
Inclusion Criteria

Inclusion Criteria:
- informed consent
- Established diagnosis of alkaptonuria
- Age:18-75
Are the trial subjects under 18? no
Number of subjects for this age range:
F.1.2 Adults (18-64 years) yes
F.1.2.1 Number of subjects for this age range
F.1.3 Elderly (>=65 years) yes
F.1.3.1 Number of subjects for this age range

Exclusion Criteria

Exclusion criteria
- NAC intolerance
- History of malignacy or neoplastic disease
- pregnant or lactanting females
- chronic or acute renal disease
- values of aspartate aminotrasferase (AST), alanine aminotrasferase (ALT) or bilirubin > 2 x upper limit of normal (ULN)
-history of excessive alcohol consuption or chronic alcohol induced disease
-patients who were treated with ascorbic acid or other antioxidant agents in the previous 30 days
- disorders that may interfere with the interpretation of the outcome data

Study & Design

Study Type
Interventional clinical trial of medicinal product
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Main Objective: Evaluation of NAC effectiveness to inhibit HGA oxidation and its polymerization within connective tissue in patients affected by Ochronosis;Secondary Objective: Evaluation of NAC treatment on 1)plasmatic and urinary parameters of oxidative stress 2) radiologic assessment of joint damage;Primary end point(s): Evaluation of NAC effect on plasmatic and urinary levels of homogentisic acid in <br>patients with homogentisic acid oxidase (HGO) deficiency.
Secondary Outcome Measures
NameTimeMethod
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