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The Effect of Gaucher Disease on Bone Cells

Completed
Conditions
10005330
10005959
Gaucher disease
Registration Number
NL-OMON34135
Lead Sponsor
Vrije Universiteit Medisch Centrum
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
Completed
Sex
Not specified
Target Recruitment
24
Inclusion Criteria

Patients
1. Men and women between the age of 18 and 65 years
2. Informed consent
3. Patient with a proven diagnosis of Gaucher disease
4. Stable (< 5% change) body weight for at least 6 months and a BMI between 18-30;healthy controls
1. Men and women between the age of 18 and 65 years
2. Informed consent
3. Stable (< 5% change) body weight for at least 6 months and a BMI between 18-30

Exclusion Criteria

Patients and healthy controls:
1. Documented inflammatory or malignant bowel disease
2. Previous bowel surgery, both small intestine and/or colon, with the exception of appendicular surgery.
3. Cholestatic disease defined by elevated values of AP or gammaGT > 2 x upper reference limit
4. Fever of unknown cause during the past 4 weeks prior to study
5. Co-morbidity influencing bone metabolism:
Renal insufficiency (creatinin clearance < 40 ml/min)
untreated hypo- / hyperthyroidism (stabily treated hypothyroidism may be included)
Paget*s disease or other metabolic bone diseases, Cushing*s disease or hyperprolactinemia
6. Patients who have received calcitonin, bisphosphonates and strontium within 1 year
7. Use of corticosteroids current use and in the last 3 months in case of longterm use or in the last 6 weeks in case of induction therapy
8. Patients who have been treated with anti-TNF in the last 6 months
9. Use of antitrombotic agents
10. Patients who are pregnant or breast-feeding

Study & Design

Study Type
Observational invasive
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
<p>osteoblast proliferation, osteoblast differentiation, osteoclastogenesis,<br /><br>osteoclast function</p><br>
Secondary Outcome Measures
NameTimeMethod
<p>na</p><br>
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