MedPath

Long-term, Open-label, Flexible-dose, Extension Study of Vortioxetine in Child and Adolescent Participants With Major Depressive Disorder (MDD) From 7 to 18 Years of Age

Phase 3
Terminated
Conditions
Depressive Disorder, Major
Interventions
Registration Number
NCT02871297
Lead Sponsor
H. Lundbeck A/S
Brief Summary

Evaluation of the long-term safety and tolerability of vortioxetine in child and adolescent participants with a Diagnostic and Statistical Manual of Mental Disorders, 5th edition (DSM-5™) diagnosis of MDD.

Detailed Description

Not available

Recruitment & Eligibility

Status
TERMINATED
Sex
All
Target Recruitment
662
Inclusion Criteria
  • The participant is a male or female child aged ≥7 and <12 years or adolescent aged ≥12 and ≤18 years in the lead-in study (12709A and 12710A).
  • The participant must have completed Study 12709A or 12710A (Visit 12, Completion Visit) immediately prior to enrolment into this extension study.
  • The participant had a primary diagnosis of MDD at entry in study 12709A or 12710A, diagnosed according to DSM-5™.
  • The participant is indicated for long-term treatment with vortioxetine according to the clinical opinion of the Investigator.
  • For participants aged ≥7 and ≤17 years at the Baseline visit; the participant is able to understand the Informed Assent Form, and parent(s)/legal representative(s) are able to read and understand the Informed Consent Form.
  • For participants who turned 18 years during the lead-in study 12710A; the participant has signed the Informed Consent Form.
Exclusion Criteria
  • The participant has been diagnosed with another psychiatric disorder (for example mania, bipolar disorder, schizophrenia or any psychotic disorder) during study 12709A or 12710A.
  • The participant has an attention-deficit/hyperactivity disorder (ADHD) that requires a pharmacological treatment other than a stimulant medication.

Other protocol-defined inclusion and exclusion criteria may apply

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
VortioxetineVortioxetineVortioxetine tablets for 26 weeks. Single dose of vortioxetine oral drops (only a subset of participants).
Primary Outcome Measures
NameTimeMethod
Number of Participants With Treatment-Emergent Adverse Events (TEAEs)Baseline up to Week 30

An adverse event (AE) was defined as any untoward medical occurrence that develops or worsens in severity during the conduct of a clinical study and does not necessarily have a causal relationship to the study drug. SAEs included death, a life-threatening adverse event, inpatient hospitalization or prolongation of existing hospitalization, persistent or significant disability or incapacity, a congenital anomaly or birth defect, or an important medical event that jeopardized the participant and required medical intervention to prevent 1 of the outcomes listed in this definition. TEAE was defined as an AE that started or increased in intensity on or after the date of first dose of study drug in this study 12712A. A summary of serious and non-serious AEs regardless of causality is located in 'Reported Adverse Events module'.

Secondary Outcome Measures
NameTimeMethod
Change From Baseline in Children Depression Rating Scale - Revised (CDRS-R) Total Score at Week 26Baseline, Week 26

CDRS-R consisted of 17 items out of which 3 items rated nonverbal observations (listless speech, hypoactivity, and depressed affect). Fourteen items were rated on a 7-point scale from 1 to 7, and 3 items (sleep disturbance, appetite disturbance, and listless speech) were scored on a 5-point scale from 1 to 5. A rating of 1 indicated normal functioning and a higher number indicated a greater degree of depression. Total score ranged from 17 (normal) to 113 (severe depression). Least square (LS) mean was calculated using a restricted maximum likelihood-based mixed model for repeated measurements (MMRM) approach.

Adolescents (12-18 Years): Change From Baseline in BRIEF-SR Using the MI Score at Week 26Baseline, Week 26

BRIEF form is an 86-item measure that assesses impairment in executive function with symptoms rated on a 3-point likert scale of 1 "never", 2 "sometimes" or 3 "often". These items cover 8 non-overlapping clinical scales. Clinical scales combined to form 2 indexes, the BRI and the MI. For BRIEF-SR, MI is comprised of Working Memory (12), Plan/Organize (13), Organization of Materials (7), and Task Completion (10) scales. The MI scores are calculated as the sum of the total 42 items ranging from 42 to 126 with lower scores reflecting better functioning. Raw scores converted to T-scores as detailed in T-score conversion tables for BRIEF-SR. The conversion was based on gender and the age group. T-scores ranged between 31 to 100, with a lower score indicating better functioning.

Number of Participants With Response to the Palatability Questionnaireassessed at Baseline up to Week 26, Week 26 reported

The palatability of vortioxetine oral drops was assessed after intake of a single dose (5 to 20 mg) corresponding to the participant's current vortioxetine dose (replacing the vortioxetine tablet on that day). The palatability assessment included 4 questions on the overall appreciation of a medicinal product in relation to its taste (What do you think of the taste), mouthfeel (How does medicine feel in your mouth), aftertaste (What do you think of the after taste), and smell (What do you think of the smell). The items were rated on a 5-point hedonic scale; really bad, bad, neither good or bad, good, or very good. The oral drops were considered acceptable if the mean hedonic scores were ≤3 for each aspect of palatability (taste, aftertaste, smell, and mouthfeel).

Time to First RelapseBaseline up to Week 26

Relapse was defined as a total score ≥40 on the CDRS-R. CDRS-R consisted of 17 items out of which 3 items rated nonverbal observations (listless speech, hypoactivity, and depressed affect). Fourteen items were rated on a 7-point scale from 1 to 7, and 3 items (sleep disturbance, appetite disturbance, and listless speech) were scored on a 5-point scale from 1 to 5. A rating of 1 indicated normal functioning and a higher number indicated a greater degree of depression. Total score ranged from 17 (normal) to 113 (severe depression).

Change From Baseline in Children's Global Assessment Scale (CGAS) Score at Week 26Baseline, Week 26

The CGAS is a clinician-rated global scale to measure the lowest level of functioning for a child (4 to 16 years) during a specified time period. The CGAS contains behaviourally-oriented descriptors at each anchor point that depict behaviours and life situations applicable to a child. The score ranges from 1 (most functionally impaired child) to 100 (the healthiest). A score greater than 70 indicates normal function.

Change From Baseline in Pediatric Quality of Life Inventory Present Functioning Visual Analogue Scale (PedsQL VAS) Total Score at Week 26Baseline, Week 26

The PedsQL™ VAS is designed to measure at-that-moment functioning in children and adolescents. The PedsQL™ VAS consists of 6 domains: anxiety, sadness, anger, worry, fatigue, and pain using VAS. The functionality for each domain is measured on a 10 cm line with a happy face at one end and a sad face at the other (0-10 points). The participants are asked to mark on the line how they feel. The total score is the average of all 6 items ranging from 0 to 10, where a lower value represents a better outcome.

Time to First Loss of RemissionBaseline up to Week 26

Remission was defined as a total score ≤28 on the CDRS-R. CDRS-R consisted of 17 items out of which 3 items rated nonverbal observations (listless speech, hypoactivity, and depressed affect). Fourteen items were rated on a 7-point scale from 1 to 7, and 3 items (sleep disturbance, appetite disturbance, and listless speech) were scored on a 5-point scale from 1 to 5. A rating of 1 indicated normal functioning and a higher number indicated a greater degree of depression. Total score ranged from 17 (normal) to 113 (severe depression).

Change From Baseline in Clinical Global Impression - Severity of Illness (CGI-S) Score at Week 26Baseline, Week 26

The CGI-S provides the clinician's impression of the participant's current state of mental illness. The clinician uses his or her clinical experience of this participant population to rate the severity of the participant's current mental illness on a 7-point scale ranging from 1 (normal - not at all ill) to 7 (among the most extremely ill participants). LS mean was calculated using a restricted maximum likelihood-based MMRM approach.

Children (7-11 Years): Change From Baseline in Behaviour Rating Inventory of Executive Function - Preschool (BRIEF-P) Using the Global Executive Composite (GEC) Score at Week 26Baseline, Week 26

BRIEF form is an 86-item measure with symptoms rated on a 3-point likert scale of 1 "never", 2 "sometimes" or 3 "often". These items cover 8 non-overlapping clinical scales. For BRIEF-P form, only the first 72 items (Inhibit \[10\], Shift \[8\], Emotional Control \[10\], Initiate \[8\], Working Memory \[10\], Plan/Organize \[12\], Organization of Materials \[6\], Monitor \[8\]) were included in clinical scales. Clinical scales combined to form 2 indexes, Behavioural Regulation Index (BRI) and Metacognition Index (MI), and 1 composite summary score, the GEC, that incorporates all 8 clinical scales. GEC score was calculated as the sum of index scores ranging from 72-216; higher scores indicating greater impairment in executive functions. Raw scores converted to T-scores as detailed in T-score conversion tables for BRIEF-P. Conversion was based on gender and age group. T-scores ranged between 30 to 101, with a lower score indicating better functioning.

Clinical Global Impression - Global Improvement (CGI-I) ScoreWeek 26

The CGI-I provides the clinician's impression of the participant's improvement (or worsening). The clinician assesses the participant's condition relative to a baseline on a 7-point scale ranging from 1 (very much improved) to 7 (very much worse). LS mean was calculated using a restricted maximum likelihood-based MMRM approach.

Adolescents (12-18 Years): Change From Baseline in Behaviour Rating Inventory of Executive Function - Self-report (BRIEF-SR) Using the GEC Score at Week 26Baseline, Week 26

BRIEF form is an 86-item measure that assesses impairment in executive function with symptoms rated on a 3-point likert scale of 1 "never", 2 "sometimes" or 3 "often". These items cover 8 non-overlapping clinical scales. For BRIEF-SR form, only 80 items (Inhibit \[13\], Shift \[10\], Emotional Control \[10\], Initiate \[5\], Working Memory \[12\], Plan/Organize \[13\], Organization of Materials \[7\], Monitor \[10\]) were included in clinical scales. Clinical scales combined to form 2 indexes, the BRI and the MI, and 1 composite summary score, the GEC, that incorporates all 8 clinical scales. GEC score was calculated as the sum of index scores and ranges from 80-240 with higher scores indicating greater impairment in functions. Raw scores converted to T-scores as detailed in T-score conversion tables for BRIEF-SR. The conversion was based on gender and the age group. T-scores ranged between 29 to 104, with a lower score indicating better functioning.

Children (7-11 Years): Change From Baseline in BRIEF-P Using the MI Score at Week 26Baseline, Week 26

BRIEF form is an 86-item measure that assesses impairment in executive function with symptoms rated on a 3-point likert scale of 1 "never", 2 "sometimes" or 3 "often". These items cover 8 non-overlapping clinical scales. Clinical scales combined to form 2 indexes, the BRI and the MI. For BRIEF-P, MI is comprised of Initiate (8), Working Memory (10), Plan/Organize (12), Organization of Materials (6), and Monitor (8) scales. The MI scores are calculated as the sum of the total 44 items ranging from 44 to 132 with lower scores reflecting better functioning. Raw scores converted to T-scores as detailed in T-score conversion tables for BRIEF-P. The conversion was based on gender and the age group. T-scores ranged between 30 to 98, with a lower score indicating better functioning.

Number of Participants With Response to the Acceptability Questionnaireassessed at Baseline up to Week 26, Week 26 reported

The acceptability of vortioxetine oral drops was assessed after intake of a single dose (5 to 20 mg) corresponding to the participant's current vortioxetine dose (replacing the vortioxetine tablet on that day). The acceptability assessment was based on 3 items; acceptability of the taste, whether the drops were perceived as easy to take, willingness to take the drops every day (provided it was the only available formulation). For each item the response options were no, not sure, and yes. The oral drops were considered acceptable if \<60% of participants responded "no" to each of the 3 questions regarding acceptability.

Trial Locations

Locations (78)

Cape Trial Centre

🇿🇦

Bellville, Cape Town, South Africa

NHS Greater Glasgow and Clyde Glasgow Clinical Research Facility-Queen Elizabeth University Hospi...

🇬🇧

Glasgow, United Kingdom

Hospital General Universitario Gregorio Maranon

🇪🇸

Madrid, Spain

Unidad de Salud Mental Infanto-Juvenil (USMI-J) Edificio de Consultas Externas. Hospital MarAtimo

🇪🇸

Torremolinos, Malaga, Spain

Child and Adolescent Neurology and Psychiatry Clinic

🇷🇸

Belgrade, Serbia

Alder Hey Hospital

🇬🇧

Liverpool, United Kingdom

Daily Hospital for Children and Adolescents

🇷🇸

Pantelej-Nis, Serbia

Hospital Universitario Fundacion Alcorcon

🇪🇸

Alcorcon, Madrid, Spain

University Hospital Cleveland Medical Center Division of Child and Adolescent Psychiatry

🇺🇸

Cleveland, Ohio, United States

Paediatric Sleep Research Inc.

🇨🇦

Toronto, Ontario, Canada

The University of Arizona Sarver Heart Center (SHC)

🇺🇸

Tucson, Arizona, United States

University of Cincinnati Medical Center

🇺🇸

Cincinnati, Ohio, United States

MHAT Targovishte AD

🇧🇬

Targovishte, Bulgaria

Diagnostic Consultative Center Mladost-M Varna OOD

🇧🇬

Varna, Bulgaria

E.S.E. Hospital Mental de Antioquia HOMO

🇨🇴

Bello, Antioquia, Colombia

Centro de Investigaciones y Proyectos en Neurociencias CIPNA LTDA IPS.

🇨🇴

Barranquilla, Atlantico, Colombia

Centro de investigaciones del Sistema Nervioso SAS Grupo CISNE SAS

🇨🇴

Bogota, DC, Colombia

Psynapsis Salud Mental S.A.

🇨🇴

Pereira, Risaralda, Colombia

Marienthali Kliinik

🇪🇪

Tallinn, Estonia

Cabinet Psyche

🇫🇷

Douai, Nord, France

Centre Medical Ambroise Pare

🇫🇷

Elancourt, France

Klinik fur Kinderneurologie und Sozialpadiatrie Kinderzentrum Maulbronn gGmbH

🇩🇪

Maulbronn, Germany

CHU de Nantes - Hopital Hotel Dieu

🇫🇷

Nantes Cedex 1, France

Rheinhessen-Fachklinik Mainz, Kinder und Jugendpsychiatri

🇩🇪

Mainz, Germany

Univ. Freiburg

🇩🇪

Freiburg, Baden-Wurttemberg, Germany

University Hospital Tuebingen -

🇩🇪

Tuebingen, Germany

Vadaskert Child Psychiatric Hospital and Outpatient

🇭🇺

Budapest, Hungary

Bekes Megyei Kozponti Korhaz Pandy Kalman Tagkorhaza

🇭🇺

Gyula, Hungary

Ramat Chen - Mental Health Clinic

🇮🇱

Tel Aviv, Israel

Scientific Institute Fondazione Stella Maris

🇮🇹

Calambrone, Pisa, Italy

U.O.C. Neuropsichiatria Infantile - IRCCS Istituto Giannina Gaslini

🇮🇹

Genova, Italy

Soon Chun Hyang University Hospital Cheonan

🇰🇷

Cheonan-si, Chungcheongnam-do, Korea, Republic of

Asan Medical Center

🇰🇷

Seoul, Korea, Republic of

Hospital Gintermuiza

🇱🇻

Jelgava, Latvia

Linda Keruze's Psychiatric Center, LLC

🇱🇻

Liepaja, Latvia

Children Hospilal -Gailezers

🇱🇻

Riga, Latvia

Sigulda Hospital Outpatient Clinic

🇱🇻

Sigulda, Latvia

Instituto Nacional de Pediatria (INP) (National Institute of Pediatrics)

🇲🇽

Ciudad de Mexico, Distrito Federal, Mexico

Clinica Cemelli

🇲🇽

Guadalajara, Jalisco, Mexico

Roberto Zepeda Sanchez

🇲🇽

Guadalajara, Jalisco, Mexico

CRI Centro Regiomontano de Investigacion SC

🇲🇽

Monterrey, Nuevo Leon, Mexico

B & B Investigaciones Medicas, SC

🇲🇽

Mazatlan, Sinaloa, Mexico

BIND Investigaciones S.C

🇲🇽

San Luis Potosi, Mexico

Centrum Badan Klinicznych PI-House Sp. z o.o.

🇵🇱

Gdansk, Poland

Spectrum Centrum Psychiatrii Specjalistyczny Gabinet Psychiatryczny

🇵🇱

Lublin, Poland

Przychodnia Syntonia Poradnia Zdrowia Psychicznego

🇵🇱

Kielce, Poland

Filip Rybakowski Specjalistyczna Praktyka Lekarska

🇵🇱

Poznan, Poland

Specjalistyczny Szpital im. dra A. Sokolowskiego w Walbrzychu

🇵🇱

Walbrzych, Poland

Centrum Neuropsychiatrii Neuromed

🇵🇱

Wroclaw, Poland

Medicorehabilitation Research Center Phoenix

🇷🇺

Rostov-On-Don, Rostov State, Russian Federation

Stavropol Region Psychiatric Hospital No.2

🇷🇺

Stavropol, Stavropol Region, Russian Federation

Arkhangelsk Regional Clinical Mental Hospital

🇷🇺

Arkhangelsk, Russian Federation

State Budgetary Healthcare Institution of Sverdlovsk Region ¿Sverdlovsk Regional Clinical Psychi...

🇷🇺

Ekaterinburg, Russian Federation

GUZ Engels Psychiatric Hospital

🇷🇺

Engels, Russian Federation

Lipetsk Regional Psychoneurological Hospital

🇷🇺

Lipetsk, Russian Federation

State Budgetary Healthcare Institution (SBHI) Specialized Clinical Psychiatric Hospital 1 of the ...

🇷🇺

Krasnodar, Russian Federation

Nizhny Novgorod Region State Institution Of Healthcare Clinical Psychiatric Hospital 1 Of Nizhny ...

🇷🇺

Nizhny Novgorod, Russian Federation

LLC City Neurological Center Sibneuromed

🇷🇺

Novosibirsk, Russian Federation

Saratov State Medical University

🇷🇺

Saratov, Russian Federation

Rostov State Medical University of the Minzdravsotsrazvitiya of Russia

🇷🇺

Rostov-on-Don, Russian Federation

City Psychiatric Hospital No.3 named after I.I. Skvortsov-Stepanov

🇷🇺

St-Petersburg, Russian Federation

Guz Saratov Regional Psychiatric Hospital St. Sofii

🇷🇺

Saratov, Russian Federation

Yaroslavl Regional Clinical Psychiatry Hospital

🇷🇺

Yaroslavl, Russian Federation

Nebbiolo LLC

🇷🇺

Tomsk, Russian Federation

Kansas University School of Medicine-Wichita

🇺🇸

Wichita, Kansas, United States

Centro para el Desarrollo de la Medicina y de Asistencia Medica Especializada S.C

🇲🇽

Culiacan De Rosales, Sinaloa, Mexico

Sciaf Ulss 16 Padova

🇮🇹

Padova, Regione Veneto, Italy

Hospital Trust-University of Cagliari

🇮🇹

Cagliari, Italy

Dip.Sc.Biomediche, Odont. e Imm.Funz.li, AOU Policlinico G. Martino

🇮🇹

Messina, Italy

University Federico II Of Naples

🇮🇹

Napoli, Italy

Prywatne Gabinety Lekarskie Promedicus

🇵🇱

Bialystok, Podlaskie, Poland

University Clinical Center Kragujevac

🇷🇸

Kragujevac, Serbia

Ukrainian Research Institute Of Social, Forensic Psychiatry And Drug Abuse, Kiev City Psychoneuro...

🇺🇦

Kyiv, Ukraine

Odessa Regional Medical Centre of Mental Health

🇺🇦

Odessa, Ukraine

Ternopil Regional Clinical Municipal Psycho-Neurological Hospital, Ternopil State Medical Univers...

🇺🇦

Ternopil, Ukraine

Institute of Mental Health

🇷🇸

Belgrade, Serbia

Maltsev Poltava Regional Clinical Psychiatric Hospital, Higher State Educational Institution Of U...

🇺🇦

Poltava, Ukraine

Clinical Center of Vojvodina - Clinic of Psychiatry

🇷🇸

Novi Sad, Serbia

© Copyright 2025. All Rights Reserved by MedPath