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Study Evaluating the Efficacy and Safety of Idelalisib in Combination With Bendamustine and Rituximab for Previously Treated Chronic Lymphocytic Leukemia (CLL) (Tugela )

Phase 3
Completed
Conditions
Chronic Lymphocytic Leukemia
Interventions
Registration Number
NCT01569295
Lead Sponsor
Gilead Sciences
Brief Summary

The primary objective of this study is to evaluate the effect of the addition of idelalisib (formerly GS-1101) to bendamustine + rituximab (BR) on progression-free survival (PFS) in participants with previously treated chronic lymphocytic leukemia (CLL)

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
416
Inclusion Criteria
  • Previously treated recurrent CLL
  • Measurable lymphadenopathy
  • Requires therapy for CLL
  • Has experienced CLL progression < 36 months since the completion of the last prior therapy

Key

Exclusion Criteria
  • Recent history of a major non-CLL malignancy
  • Evidence of an ongoing infection
  • CLL refractory to bendamustine
  • Concurrent participation in another therapeutic clinical trial

NOTE: Other protocol defined Inclusion/ Exclusion criteria may apply.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Idelalisib+bendamustine+rituximabRituximabParticipants will receive idelalisib plus bendamustine and rituximab
Idelalisib+bendamustine+rituximabIdelalisibParticipants will receive idelalisib plus bendamustine and rituximab
Idelalisib+bendamustine+rituximabBendamustineParticipants will receive idelalisib plus bendamustine and rituximab
Placebo to match idelalisib+bendamustine+rituximabRituximabParticipants will receive placebo to match idelalisib plus bendamustine and rituximab
Placebo to match idelalisib+bendamustine+rituximabBendamustineParticipants will receive placebo to match idelalisib plus bendamustine and rituximab
Placebo to match idelalisib+bendamustine+rituximabPlacebo to match idelalisibParticipants will receive placebo to match idelalisib plus bendamustine and rituximab
Primary Outcome Measures
NameTimeMethod
Progression-Free Survival (PFS)Up to 84 months

PFS was defined as the interval from randomization to the earlier of the first documentation of definitive disease progression or death from any cause. PFS (months) = (minimum (date of disease progression, date of death) - date of randomization + 1)/30.4375.

Secondary Outcome Measures
NameTimeMethod
Overall Response Rate (ORR)Up to 84 months

ORR was the percentage of participants who achieved a complete response (CR), CR with incomplete marrow recovery (CRi,) or partial response (PR) and maintained the response for at least 12 weeks. CR was defined as no lymphadenopathy, hepatomegaly, splenomegaly; normal complete blood count; confirmed by bone marrow aspirate \& biopsy.

PR was defined as \>1 of the following criteria: a 50% decrease in peripheral blood lymphocytes, lymphadenopathy, liver size, spleen size; plus ≥ 1 of the following: ≥ 1500/μL absolute neutrophil count, \> 100000/μL platelets, \> 11.0 g/dL hemoglobin or 50% improvement for either of these parameters without transfusions or growth factors. CRi was defined as all criteria for CR met but with persistent anemia, thrombocytopenia, neutropenia or a hypocellular bone marrow.

Lymph Node Response RateUp to 84 months

Lymph node response rate was defined as the percentage of participants who achieved a ≥ 50% decrease from baseline in the sum of the products of the greatest perpendicular diameters (SPD) of index lesions.

Overall SurvivalUp to 84 months

Overall survival (OS) was defined as the interval from randomization to death from any cause. Overall survival (months) = (date of death - date of randomization + 1)/30.4375.

Complete Response RateUp to 84 months

Complete response (CR) rate was defined as the percentage of participants who achieved a CR.

Trial Locations

Locations (104)

University of Florida

🇺🇸

Gainesville, Florida, United States

University College London

🇬🇧

London, United Kingdom

G. Genimatas Hospital

🇬🇷

Athens, Greece

Centre Hospitalier Lyon Sud

🇫🇷

Pierre Bénite, France

Cancer Care Northwest, US Oncology

🇺🇸

Spokane, Washington, United States

Texas Oncology

🇺🇸

Fort Worth, Texas, United States

Fakultní nemocnice Hradec Králové

🇨🇿

Hradec Králové, Czechia

Centre Jean Bernard - Clinique Victor Hugo

🇫🇷

Le Mans cedex, France

Wojewodzki Szpital Specjalistyczny im. M. Kopernika w Lodzi

🇵🇱

Lodz, Poland

Klinichki Bolnicki Centar-Zagreb

🇭🇷

Zagreb, Croatia

UZ Leuven

🇧🇪

Leuven, Belgium

Sir Charles Gairdner Hospital

🇦🇺

Nedlands, Western Australia, Australia

Medical College of Wisconsin

🇺🇸

Milwaukee, Wisconsin, United States

Tallian Gyula utca 20-32

🇭🇺

Kaposvár, Hungary

University Hospital Merkur

🇭🇷

Zagreb, Croatia

Ziekenhuisnetwerk Antwerpen - AZ Stuivenberg

🇧🇪

Antwerpen, Belgium

UZ Gent

🇧🇪

Gent, Belgium

University General Hospital of Patras

🇬🇷

Patras, Greece

Charleston Hematology Oncology

🇺🇸

Charleston, South Carolina, United States

Hôpitaux de Brabois

🇫🇷

Vandoeuvre-lés-Nancy, France

Stanford Cancer Center

🇺🇸

Palo Alto, California, United States

Summit Medical Group, P.A.

🇺🇸

Morristown, New Jersey, United States

Saratov State Medical University

🇷🇺

Saratov, Russian Federation

Ryazan Regional Clinical Hospital

🇷🇺

Ryazan, Russian Federation

State Budgetary Healthcare Institution Volgograd Regional Clinical Oncology Dispensary #1

🇷🇺

Volgograd, Russian Federation

Hospital de la Santa Creu i Sant Pau

🇪🇸

Barcelona, Cataluña, Spain

King's College Hospital

🇬🇧

London, United Kingdom

Russian Oncology Research Center (N.N. Blokhin)

🇷🇺

Moscow, Russian Federation

Novosibirsk State Regional Clinical Hospital

🇷🇺

Novosibirsk, Russian Federation

Hospital Clinic de Barcelona

🇪🇸

Barcelona, Cataluña, Spain

St. James University Hospital

🇬🇧

Leeds, United Kingdom

Ondokuz Mayis University Faculty of Medicine

🇹🇷

Samsun, Turkey

St Bartholomews Hospital

🇬🇧

London, United Kingdom

Christie Hospital

🇬🇧

Manchester, United Kingdom

University Hospital of Wales

🇬🇧

Cardiff, United Kingdom

Hospital 12 de Octubre

🇪🇸

Madrid, Madrid, Communidad De, Spain

New Cross Hospital

🇬🇧

Wolverhampton, United Kingdom

Gazi University Medical Faculty Gazi Hospital

🇹🇷

Ankara, Turkey

Kent and Canterbury Hospital

🇬🇧

Canterbury, United Kingdom

Dorset County Hospital

🇬🇧

Dorchester, United Kingdom

Winship Cancer Institute at Emory University

🇺🇸

Atlanta, Georgia, United States

UCLA Medical Center

🇺🇸

Los Angeles, California, United States

North Shore University Hospital

🇺🇸

Manhasset, New York, United States

Texas Oncology PA

🇺🇸

Dallas, Texas, United States

University of Texas MD Anderson Cancer Center

🇺🇸

Houston, Texas, United States

Seattle Cancer Care Alliance

🇺🇸

Seattle, Washington, United States

IRCCS Ospedale San Raffaele

🇮🇹

Milano, Italy

Ankara University Medical Faculty

🇹🇷

Ankara, Turkey

Hammersmith Hospital

🇬🇧

London, United Kingdom

Nottingham University Hospitals NHS Trust

🇬🇧

Nottingham, United Kingdom

Royal Cornwall Hospital

🇬🇧

Truro, United Kingdom

CHRU Lille-Hôpital Claude Huriez

🇫🇷

Lille, France

Centre Hospitalier de Mulhouse

🇫🇷

Mulhouse, France

Clearview Cancer Institute

🇺🇸

Huntsville, Alabama, United States

Rocky Mountain Cancer Center

🇺🇸

Denver, Colorado, United States

University of Nebraska Medical Center

🇺🇸

Omaha, Nebraska, United States

Dana Farber Cancer Institute

🇺🇸

Boston, Massachusetts, United States

Memorial Sloan Kettering Cancer Center

🇺🇸

New York, New York, United States

Long Island Jewish Medical Center

🇺🇸

New Hyde Park, New York, United States

Columbia University Medical Center

🇺🇸

New York, New York, United States

Országos Onkológiai Intézet

🇭🇺

Budapest, Hungary

Mater Misericordiae Hospital

🇮🇪

Dublin, Ireland

Debreceni Egyetem Orvos- és Egészségtudományi Centrum

🇭🇺

Debrecen, Hungary

Spedali Civili di Brescia

🇮🇹

Brescia, Italy

Ospedale Oncologico Regionale A. Businco

🇮🇹

Cagliari, Italy

Azienda Ospedaliera Universitaria San Giovanni Battista-Molinette

🇮🇹

Torino, Italy

Malopolskie Centrum Medyczne

🇵🇱

Krakow, Poland

Szpital Specjalistyczny w Brzozowie

🇵🇱

Brzozow, Poland

Wojewodzki Szpital w Opolu

🇵🇱

Opole, Poland

"Colentina" Clinical Hospital

🇷🇴

Bucharest, Romania

Hospital Santa Maria

🇵🇹

Lisboa, Portugal

Research Institute of Hematology and Blood Transfusion

🇷🇺

St. Petersburg, Russian Federation

"Fundeni" Clinical Institute

🇷🇴

Bucharest, Romania

Nizhegorodskaya Regional Clinical Hospital n.a. N.A. Semashko

🇷🇺

Nizhniy Novgorod, Russian Federation

Hospital Universitario Germans Trias i Pujol

🇪🇸

Badalona, Cataluña, Spain

Hospital Universitario Puerta de Hierro

🇪🇸

Majadahonda, Madrid, Communidad De, Spain

Istanbul University Istanbul Medical Faculty

🇹🇷

Istanbul, Turkey

Hospital Universitario de La Princesa

🇪🇸

Madrid, Spain

Birmingham Heartlands Hospital

🇬🇧

Birmingham, United Kingdom

Willamette Valley Cancer Center

🇺🇸

Eugene, Oregon, United States

St Vincent's Hospital - Sydney

🇦🇺

Darlinghurst, New South Wales, Australia

Royal Adelaide Hospital

🇦🇺

Adelaide, South Australia, Australia

Fakultni nemocnice Brno

🇨🇿

Brno, Czechia

Cancer Care Manitoba

🇨🇦

Winnipeg, Manitoba, Canada

Princess Alexandra Hospital

🇦🇺

Woolloongabba, Australia

Virginia Cancer Specialists, PC

🇺🇸

Vancouver, Washington, United States

Gosford Hospital

🇦🇺

Gosford, New South Wales, Australia

Centre Léon Bérard - Centre régional de lutte contre le cancer Rhône-Alpes

🇫🇷

Lyon, France

Fakultni nemocnice Ostrava

🇨🇿

Ostrava, Czechia

Hopital Henri Mondor

🇫🇷

Créteil, France

CHU Hôtel-Dieu-Service Hématologie

🇫🇷

Nantes, France

Churchill Hospital

🇬🇧

Oxford, United Kingdom

Hopital Purpan

🇫🇷

Toulouse, France

Emergency County Clinical Hospital Brasov

🇷🇴

Brasov, Romania

Samodzielny Publiczny Szpital Kliniczny Nr 1

🇵🇱

Lublin, Poland

Centrum Onkologii Instytut im. Marii Sklodowskiej-Curie

🇵🇱

Warszawa, Poland

"Instituto Portugues de Oncologia do Porto Francisco Gentil (IPOPFG, EPE)

🇵🇹

Porto, Portugal

Szegedi Tudományegyetem Szent-Györgyi Albert Klinikai Központ

🇭🇺

Szeged, Hungary

Centralny Szpital Kliniczny MSW w Warszawie

🇵🇱

Warszawa, Poland

Regional Oncology Institute Iasi

🇷🇴

Iasi, Romania

Clinical Hospital "Dubrava"

🇭🇷

Zagreb, Croatia

Monash Medical Centre - Clayton Campus

🇦🇺

Clayton, Victoria, Australia

Semmelweis Egyetem

🇭🇺

Budapest, Hungary

Royal Liverpool University Hospital

🇬🇧

Liverpool, United Kingdom

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