MedPath

Combination Chemotherapy With or Without Lestaurtinib in Treating Younger Patients With Newly Diagnosed Acute Lymphoblastic Leukemia

Phase 3
Completed
Conditions
Acute Undifferentiated Leukemia
Acute Lymphoblastic Leukemia
Childhood T Acute Lymphoblastic Leukemia
Interventions
Procedure: Biospecimen Collection
Procedure: Bone Marrow Biopsy
Procedure: Echocardiography
Biological: Filgrastim
Other: Laboratory Biomarker Analysis
Procedure: Multigated Acquisition Scan
Other: Pharmacological Study
Registration Number
NCT00557193
Lead Sponsor
Children's Oncology Group
Brief Summary

This phase III trial studies combination chemotherapy with or without lestaurtinib with to see how well they work in treating younger patients with newly diagnosed acute lymphoblastic leukemia. Drugs used in chemotherapy work in different ways to stop the growth of stop cancer cells, either by killing the cells, by stopping them from dividing, or by stopping them from spreading. Lestaurtinib may stop the growth of cancer cells by blocking some of the enzymes needed for cell growth. It is not yet known whether combination chemotherapy is more effective with or without lestaurtinib in treating acute lymphoblastic leukemia.

Detailed Description

PRIMARY OBJECTIVES:

I. To estimate the 3-year event-free survival (EFS) of infants with mixed lineage leukemia-rearranged (MLL-R) acute lymphoblastic leukemia (ALL) treated with chemotherapy plus the fms-related tyrosine kinase 3 (FLT3) inhibitor lestaurtinib.

SECONDARY OBJECTIVES:

I. To compare the 3-year EFS of infants with MLL-R ALL treated with chemotherapy plus the FLT3 inhibitor lestaurtinib to MLL-R patients treated with chemotherapy alone.

II. To determine a safe, tolerable and biologically active dose of lestaurtinib given in sequential combination with chemotherapy in MLL-R infants.

III. To characterize the pharmacokinetics and pharmacodynamics of lestaurtinib in infants when given at the proposed dose in sequential combination with chemotherapy.

IV. To identify molecular mechanisms of resistance to lestaurtinib in leukemic blasts.

V. To describe levels of minimal residual disease in infants with ALL within the context of the proposed therapy, and correlate with outcome.

VI. To identify gene expression patterns in diagnostic infant leukemia samples that correlate with outcome within the context of the proposed therapy.

VII. To describe the outcome of infants with MLL-G ALL treated with a modified P9407 chemotherapy backbone that includes an extended continuation phase.

OUTLINE:

INDUCTION THERAPY (WEEKS 1-5): All patients receive induction therapy comprising vincristine sulfate intravenously (IV) over 1 minute on days 8, 15, 22, and 29; daunorubicin hydrochloride IV over 30 minutes on days 8 and 9; cyclophosphamide IV over 30 minutes every 12 hours on days 3 and 4 (closed as of 05/19/09); pegaspargase or asparaginase intramuscularly (IM) on days 15, 18, 22, 25, 29, and 33; prednisone orally (PO) thrice daily (TID) or methylprednisolone IV on days 1-7; dexamethasone IV or PO TID on days 8-28; cytarabine IV over 30 minutes on days 8-21; methotrexate intrathecally (IT) on days 1 and 29; cytarabine IT on day 15; hydrocortisone IT on days 15 and 29; and filgrastim IV or subcutaneously (SC) beginning on day 5 and continuing until blood counts recover. Standard-risk patients are non-randomly assigned to receive a less intensive chemotherapy regimen without lestaurtinib (post-induction therapy A). Patients undergo echocardiography (ECHO) or multigated acquisition scan (MUGA), blood sample collection and bone marrow biopsy on day 1 week 1.

POST-INDUCTION THERAPY A: (for standard-risk patients MLL-germline \[G\])

INDUCTION INTENSIFICATION (WEEKS 6-9): Patients receive high-dose methotrexate IV continuously over 24 hours on days 1 and 8; triple IT chemotherapy comprising methotrexate, cytarabine, and hydrocortisone on days 1 and 8; leucovorin calcium IV or PO every 6 hours beginning 42 hours after start of high-dose methotrexate and continuing until methotrexate level is \< 0.1 uM; cyclophosphamide IV over 30 minutes on days 15-19; etoposide IV over 2 hours on days 15-19; and filgrastim IV or SC beginning on day 20 and continuing until blood counts recover. Patients in morphologic remission proceed to re-induction therapy. Patients may undergo bone marrow biopsy on day 1 week 6.

RE-INDUCTION (WEEKS 10-12): Patients receive vincristine sulfate IV over 1 minute on days 1, 8, and 15; daunorubicin hydrochloride IV over 30 minutes on days 1 and 2; cyclophosphamide IV over 30 minutes every 12 hours on days 3 and 4; pegaspargase or asparaginase IM on day 4; dexamethasone IV or PO twice daily (BID) on days 1-7 and 15-21; triple IT chemotherapy comprising methotrexate, cytarabine, and hydrocortisone on days 1 and 15; and filgrastim IV or SC beginning on day 5 and continuing until blood counts recover. Patients undergo ECHO or MUGA, blood sample collection and bone marrow biopsy on day 1 week 10.

CONSOLIDATION (WEEKS 13-19): Patients receive high-dose methotrexate IV continuously over 24 hours on days 1 and 8; leucovorin calcium IV every 6 hours beginning 42 hours after start of high-dose methotrexate and continuing until methotrexate level is \< 0.1 uM; triple IT chemotherapy comprising methotrexate, cytarabine, and hydrocortisone on day 1; etoposide IV over 2 hours on days 15-19; cyclophosphamide IV over 30 minutes on days 15-19; high-dose cytarabine IV over 3 hours every 12 hours on days 29 and 30; pegaspargase or asparaginase IM on day 30; and filgrastim IV or SC beginning on day 20 and day 31 and continuing until blood counts recover.

CONTINUATION I (WEEKS 20-41): Patients receive vincristine sulfate IV on day 1 in weeks 20 and 24; dexamethasone IV or PO BID on days 1-5 in weeks 20, and 24; triple IT chemotherapy comprising methotrexate, cytarabine, and hydrocortisone on day 1 in weeks 20 and 24; methotrexate IV on day 1 in weeks 21-24 and 25-27; etoposide IV over 2 hours on day 1-5 in week 28; cyclophosphamide IV over 30 minutes on days 1-5 in week 28; mercaptopurine PO on days 1-7 in weeks 21-23 and 25-27; and filgrastim SC or IV beginning on day 6 in week 28 and continuing until blood counts recover. Patients may undergo bone marrow biopsy on day 1 week 20.

CONTINUATION II (WEEKS 42-104): Patients receive vincristine sulfate IV on days 1, 29, and 57; dexamethasone IV or PO BID on days 1-5, 29-33, and 57-61; methotrexate IT on day 1; methotrexate PO on days 8, 15, 22, 36, 43, 50, 64, 71, and 78; and mercaptopurine PO on days 8-28, 36-56, and 64-84. Treatment repeats every 12 weeks for 2 years from diagnosis.

A safety/activity phase is conducted separately for the intermediate-risk (IR) and high-risk (HR) patients to identify a safe, tolerable, and biologically active dose of lestaurtinib combined with chemotherapy backbone. Once a tolerable/active dose of lestaurtinib has been identified for IR patients, subsequent IR patients are eligible to proceed to an efficacy phase, where they are randomized (or non-randomly assigned as of 7/16/2014) to chemotherapy with or without lestaurtinib. HR patients separately proceed to the randomized efficacy phase if a tolerable/active dose is identified for the HR stratum. IR and HR patients are randomized (or non-randomly assigned as of 7/16/2014) to 1 of 2 post-induction therapy regimens (post-induction therapy B or C).

POST-INDUCTION THERAPY B: (chemotherapy only for IR/HR patients classified as MLL-R; age \>= 90 days at diagnosis):

INDUCTION INTENSIFICATION (WEEKS 6-9): Patients receive high-dose methotrexate, leucovorin calcium, cyclophosphamide, etoposide, and filgrastim as in post-induction therapy A induction intensification. Patients in morphologic remission proceed to re-induction Patients undergo ECHO or MUGA, blood sample collection and bone marrow biopsy on day 1 week 6. (Retired as of 7/16/2014)

RE-INDUCTION (WEEKS 10-12): Patients receive vincristine sulfate, daunorubicin hydrochloride, cyclophosphamide, pegaspargase or asparaginase, dexamethasone, triple IT chemotherapy, and filgrastim as in post-induction therapy A re-induction. Patients undergo ECHO or MUGA, blood sample collection and bone marrow biopsy on day 1 week 10. (Retired as of 7/16/2014)

CONSOLIDATION (WEEKS 13-19): Patients receive high-dose methotrexate, leucovorin calcium, triple IT chemotherapy, etoposide, cyclophosphamide, high-dose cytarabine, pegaspargase or asparaginase, and filgrastim as in post-induction therapy A consolidation. (Retired as of 7/16/2014)

CONTINUATION I (WEEKS 20-49): Patients receive vincristine sulfate IV over 1 minute on day 1 in weeks 20, 24, 33, 37, and 46; dexamethasone PO or IV BID on days 1-5 in weeks 20, 24, 33, 37, and 46; triple IT chemotherapy on day 1 in weeks 20, 24, 33, 37, and 46; methotrexate IV on day 1 in weeks 21-23, 25-26 and 37-45; mercaptopurine PO on days 1-7 in weeks 21-23, 25-26 and 37-45; etoposide IV over 2 hours on days 1-5 in week 27; cyclophosphamide IV over 2 hours on days 1-5 in week 27: high-dose cytarabine IV over 3 hours every 12 hours on days 1 and 2 in week 30; pegaspargase or asparaginase IM on day 2 in week 30: and filgrastim SC or IV beginning on day 3 in weeks 30 and continuing until blood counts recover. Patients may undergo bone marrow biopsy on day 1 of weeks 20, 33 and 46. (Retired as of 7/16/2014)

CONTINUATION II (WEEKS 50-104): Patients receive vincristine sulfate, dexamethasone, IT methotrexate, methotrexate PO, and mercaptopurine PO as in post-induction therapy A continuation II. Treatment repeats every 12 weeks for 2 years from diagnosis. (Retired as of 7/16/2014)

POST-INDUCTION THERAPY C: (chemotherapy and lestaurtinib for IR/HR patients classified as MLL-R; age \< 90 days at diagnosis)

INDUCTION INTENSIFICATION THERAPY (WEEKS 6-9): Patients receive high-dose methotrexate, leucovorin calcium, cyclophosphamide, etoposide, and filgrastim as in post-induction therapy B induction intensification. Patients also receive lestaurtinib PO BID on days 20-27. Patients in morphologic remission proceed to re-induction.Patients undergo ECHO or MUGA, blood sample collection and bone marrow biopsy on day 1 week 6.

RE-INDUCTION (WEEKS 10-12): Patients receive vincristine sulfate, daunorubicin hydrochloride, cyclophosphamide, pegaspargase or asparaginase, dexamethasone, triple IT chemotherapy, and filgrastim as in post-induction therapy B re-induction. Patients also receive lestaurtinib PO on days 5-20. Patients undergo ECHO or MUGA, blood sample collection and bone marrow biopsy on day 1 week 10.

CONSOLIDATION (WEEKS 13-19) Patients receive high-dose methotrexate, leucovorin calcium, triple IT chemotherapy, etoposide, cyclophosphamide, high-dose cytarabine, pegaspargase or asparaginase, and filgrastim as in post-induction therapy B consolidation. Patients also receive lestaurtinib PO on days 20-27 and 31-42.

CONTINUATION I (WEEKS 20-49): Patients receive vincristine sulfate, dexamethasone, triple IT chemotherapy, methotrexate, mercaptopurine, etoposide, high-dose cytarabine, pegaspargase or asparaginase, and filgrastim as in post-induction therapy B continuation I. Patients also receive lestaurtinib PO on days 2-6 in weeks 20 and 24; days 27-41 in weeks 27-29; days 45-56 in weeks 30-32. Patients may undergo bone marrow biopsy on day 1 of weeks 20, 33 and 46.

CONTINUATION II (WEEKS 50-104): Patients receive vincristine sulfate, dexamethasone, IT methotrexate, methotrexate PO, and mercaptopurine PO as in post-induction therapy B continuation II. Treatment repeats every 12 weeks for 2 years from diagnosis.

After completion of study treatment, all patients are followed up every 1-6 months for 4 years and then annually thereafter.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
218
Inclusion Criteria
  • Patients must be enrolled on a Children's Oncology Group (COG) ALL Classification Study (AALL08B1) prior to enrollment on AALL0631
  • Patients must be < 366 days of age at the time of diagnosis; for neonates in the first month of life, patients must be > 36 weeks gestational age at the time of diagnosis
  • Patients must be newly diagnosed with acute lymphoblastic leukemia (ALL) or acute undifferentiated leukemia (AUL); patients with T-cell ALL are eligible; patients with bilineage or biphenotypic acute leukemia are eligible, provided the morphology and immunophenotype are predominately lymphoid
  • Patients must be previously untreated with the exception of steroids and intrathecal chemotherapy; no other systemic chemotherapy may have been administered; patients receiving prior steroid therapy are eligible for study; any amount of steroid pretreatment will not affect initial induction assignment as long as the patient meets all other eligibility criteria; IT chemotherapy per protocol is allowed for patient convenience at the time of the diagnostic bone marrow or venous line placement to avoid second lumbar puncture; (note: the central nervous system [CNS] status must be determined based on a sample obtained prior to administration of any systemic or intrathecal chemotherapy, except for steroid pretreatment); systemic chemotherapy must begin within 72 hours of this IT therapy
  • All patients and/or their parents or legal guardians must sign a written informed consent
  • All institutional, Food and Drug Administration (FDA), and National Cancer Institute (NCI) requirements for human studies must be met
  • Patients with mature B-cell ALL or acute myelogenous leukemia (AML) are NOT eligible
  • Patients with Down syndrome are NOT eligible
Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Arm B (IR/HR MLL-R chemotherapy)Daunorubicin HydrochloridePopulation Description: Eligible patients with MLL-R (rearranged). Considered Intermediate Risk (IR) if age \>= 90 days at diagnosis and High Risk (HR) if age \< 90 days at diagnosis.
Arm A (standard risk MLL-G)Vincristine SulfatePopulation Description: Eligible patients with MLL-G (germline, or non-rearranged)
Arm A (standard risk MLL-G)Therapeutic HydrocortisonePopulation Description: Eligible patients with MLL-G (germline, or non-rearranged)
Arm A (standard risk MLL-G)Biospecimen CollectionPopulation Description: Eligible patients with MLL-G (germline, or non-rearranged)
Arm A (standard risk MLL-G)Bone Marrow BiopsyPopulation Description: Eligible patients with MLL-G (germline, or non-rearranged)
Arm A (standard risk MLL-G)Laboratory Biomarker AnalysisPopulation Description: Eligible patients with MLL-G (germline, or non-rearranged)
Arm C (IR/HR MLL-R chemotherapy and lestaurtinib)Vincristine SulfatePopulation Description: Eligible patients with MLL-R (rearranged). Considered Intermediate Risk (IR) if age \>= 90 days at diagnosis and High Risk (HR) if age \< 90 days at diagnosis.
Arm A (standard risk MLL-G)Daunorubicin HydrochloridePopulation Description: Eligible patients with MLL-G (germline, or non-rearranged)
Arm A (standard risk MLL-G)FilgrastimPopulation Description: Eligible patients with MLL-G (germline, or non-rearranged)
Arm A (standard risk MLL-G)Leucovorin CalciumPopulation Description: Eligible patients with MLL-G (germline, or non-rearranged)
Arm A (standard risk MLL-G)EchocardiographyPopulation Description: Eligible patients with MLL-G (germline, or non-rearranged)
Arm A (standard risk MLL-G)Pharmacological StudyPopulation Description: Eligible patients with MLL-G (germline, or non-rearranged)
Arm B (IR/HR MLL-R chemotherapy)Biospecimen CollectionPopulation Description: Eligible patients with MLL-R (rearranged). Considered Intermediate Risk (IR) if age \>= 90 days at diagnosis and High Risk (HR) if age \< 90 days at diagnosis.
Arm B (IR/HR MLL-R chemotherapy)Bone Marrow BiopsyPopulation Description: Eligible patients with MLL-R (rearranged). Considered Intermediate Risk (IR) if age \>= 90 days at diagnosis and High Risk (HR) if age \< 90 days at diagnosis.
Arm C (IR/HR MLL-R chemotherapy and lestaurtinib)Biospecimen CollectionPopulation Description: Eligible patients with MLL-R (rearranged). Considered Intermediate Risk (IR) if age \>= 90 days at diagnosis and High Risk (HR) if age \< 90 days at diagnosis.
Arm A (standard risk MLL-G)Multigated Acquisition ScanPopulation Description: Eligible patients with MLL-G (germline, or non-rearranged)
Arm B (IR/HR MLL-R chemotherapy)FilgrastimPopulation Description: Eligible patients with MLL-R (rearranged). Considered Intermediate Risk (IR) if age \>= 90 days at diagnosis and High Risk (HR) if age \< 90 days at diagnosis.
Arm B (IR/HR MLL-R chemotherapy)Vincristine SulfatePopulation Description: Eligible patients with MLL-R (rearranged). Considered Intermediate Risk (IR) if age \>= 90 days at diagnosis and High Risk (HR) if age \< 90 days at diagnosis.
Arm B (IR/HR MLL-R chemotherapy)Laboratory Biomarker AnalysisPopulation Description: Eligible patients with MLL-R (rearranged). Considered Intermediate Risk (IR) if age \>= 90 days at diagnosis and High Risk (HR) if age \< 90 days at diagnosis.
Arm B (IR/HR MLL-R chemotherapy)EchocardiographyPopulation Description: Eligible patients with MLL-R (rearranged). Considered Intermediate Risk (IR) if age \>= 90 days at diagnosis and High Risk (HR) if age \< 90 days at diagnosis.
Arm B (IR/HR MLL-R chemotherapy)Leucovorin CalciumPopulation Description: Eligible patients with MLL-R (rearranged). Considered Intermediate Risk (IR) if age \>= 90 days at diagnosis and High Risk (HR) if age \< 90 days at diagnosis.
Arm B (IR/HR MLL-R chemotherapy)Multigated Acquisition ScanPopulation Description: Eligible patients with MLL-R (rearranged). Considered Intermediate Risk (IR) if age \>= 90 days at diagnosis and High Risk (HR) if age \< 90 days at diagnosis.
Arm B (IR/HR MLL-R chemotherapy)Pharmacological StudyPopulation Description: Eligible patients with MLL-R (rearranged). Considered Intermediate Risk (IR) if age \>= 90 days at diagnosis and High Risk (HR) if age \< 90 days at diagnosis.
Arm C (IR/HR MLL-R chemotherapy and lestaurtinib)FilgrastimPopulation Description: Eligible patients with MLL-R (rearranged). Considered Intermediate Risk (IR) if age \>= 90 days at diagnosis and High Risk (HR) if age \< 90 days at diagnosis.
Arm B (IR/HR MLL-R chemotherapy)Therapeutic HydrocortisonePopulation Description: Eligible patients with MLL-R (rearranged). Considered Intermediate Risk (IR) if age \>= 90 days at diagnosis and High Risk (HR) if age \< 90 days at diagnosis.
Arm C (IR/HR MLL-R chemotherapy and lestaurtinib)Leucovorin CalciumPopulation Description: Eligible patients with MLL-R (rearranged). Considered Intermediate Risk (IR) if age \>= 90 days at diagnosis and High Risk (HR) if age \< 90 days at diagnosis.
Arm C (IR/HR MLL-R chemotherapy and lestaurtinib)Pharmacological StudyPopulation Description: Eligible patients with MLL-R (rearranged). Considered Intermediate Risk (IR) if age \>= 90 days at diagnosis and High Risk (HR) if age \< 90 days at diagnosis.
Arm C (IR/HR MLL-R chemotherapy and lestaurtinib)Therapeutic HydrocortisonePopulation Description: Eligible patients with MLL-R (rearranged). Considered Intermediate Risk (IR) if age \>= 90 days at diagnosis and High Risk (HR) if age \< 90 days at diagnosis.
Arm C (IR/HR MLL-R chemotherapy and lestaurtinib)Bone Marrow BiopsyPopulation Description: Eligible patients with MLL-R (rearranged). Considered Intermediate Risk (IR) if age \>= 90 days at diagnosis and High Risk (HR) if age \< 90 days at diagnosis.
Arm C (IR/HR MLL-R chemotherapy and lestaurtinib)EchocardiographyPopulation Description: Eligible patients with MLL-R (rearranged). Considered Intermediate Risk (IR) if age \>= 90 days at diagnosis and High Risk (HR) if age \< 90 days at diagnosis.
Arm C (IR/HR MLL-R chemotherapy and lestaurtinib)Multigated Acquisition ScanPopulation Description: Eligible patients with MLL-R (rearranged). Considered Intermediate Risk (IR) if age \>= 90 days at diagnosis and High Risk (HR) if age \< 90 days at diagnosis.
Arm C (IR/HR MLL-R chemotherapy and lestaurtinib)Laboratory Biomarker AnalysisPopulation Description: Eligible patients with MLL-R (rearranged). Considered Intermediate Risk (IR) if age \>= 90 days at diagnosis and High Risk (HR) if age \< 90 days at diagnosis.
Arm C (IR/HR MLL-R chemotherapy and lestaurtinib)Daunorubicin HydrochloridePopulation Description: Eligible patients with MLL-R (rearranged). Considered Intermediate Risk (IR) if age \>= 90 days at diagnosis and High Risk (HR) if age \< 90 days at diagnosis.
Arm A (standard risk MLL-G)AsparaginasePopulation Description: Eligible patients with MLL-G (germline, or non-rearranged)
Arm A (standard risk MLL-G)CyclophosphamidePopulation Description: Eligible patients with MLL-G (germline, or non-rearranged)
Arm A (standard risk MLL-G)CytarabinePopulation Description: Eligible patients with MLL-G (germline, or non-rearranged)
Arm A (standard risk MLL-G)MercaptopurinePopulation Description: Eligible patients with MLL-G (germline, or non-rearranged)
Arm A (standard risk MLL-G)DexamethasonePopulation Description: Eligible patients with MLL-G (germline, or non-rearranged)
Arm A (standard risk MLL-G)EtoposidePopulation Description: Eligible patients with MLL-G (germline, or non-rearranged)
Arm A (standard risk MLL-G)MethotrexatePopulation Description: Eligible patients with MLL-G (germline, or non-rearranged)
Arm A (standard risk MLL-G)PegaspargasePopulation Description: Eligible patients with MLL-G (germline, or non-rearranged)
Arm A (standard risk MLL-G)PrednisonePopulation Description: Eligible patients with MLL-G (germline, or non-rearranged)
Arm B (IR/HR MLL-R chemotherapy)AsparaginasePopulation Description: Eligible patients with MLL-R (rearranged). Considered Intermediate Risk (IR) if age \>= 90 days at diagnosis and High Risk (HR) if age \< 90 days at diagnosis.
Arm B (IR/HR MLL-R chemotherapy)CyclophosphamidePopulation Description: Eligible patients with MLL-R (rearranged). Considered Intermediate Risk (IR) if age \>= 90 days at diagnosis and High Risk (HR) if age \< 90 days at diagnosis.
Arm B (IR/HR MLL-R chemotherapy)CytarabinePopulation Description: Eligible patients with MLL-R (rearranged). Considered Intermediate Risk (IR) if age \>= 90 days at diagnosis and High Risk (HR) if age \< 90 days at diagnosis.
Arm B (IR/HR MLL-R chemotherapy)DexamethasonePopulation Description: Eligible patients with MLL-R (rearranged). Considered Intermediate Risk (IR) if age \>= 90 days at diagnosis and High Risk (HR) if age \< 90 days at diagnosis.
Arm B (IR/HR MLL-R chemotherapy)EtoposidePopulation Description: Eligible patients with MLL-R (rearranged). Considered Intermediate Risk (IR) if age \>= 90 days at diagnosis and High Risk (HR) if age \< 90 days at diagnosis.
Arm B (IR/HR MLL-R chemotherapy)MercaptopurinePopulation Description: Eligible patients with MLL-R (rearranged). Considered Intermediate Risk (IR) if age \>= 90 days at diagnosis and High Risk (HR) if age \< 90 days at diagnosis.
Arm B (IR/HR MLL-R chemotherapy)MethotrexatePopulation Description: Eligible patients with MLL-R (rearranged). Considered Intermediate Risk (IR) if age \>= 90 days at diagnosis and High Risk (HR) if age \< 90 days at diagnosis.
Arm B (IR/HR MLL-R chemotherapy)PegaspargasePopulation Description: Eligible patients with MLL-R (rearranged). Considered Intermediate Risk (IR) if age \>= 90 days at diagnosis and High Risk (HR) if age \< 90 days at diagnosis.
Arm B (IR/HR MLL-R chemotherapy)PrednisonePopulation Description: Eligible patients with MLL-R (rearranged). Considered Intermediate Risk (IR) if age \>= 90 days at diagnosis and High Risk (HR) if age \< 90 days at diagnosis.
Arm C (IR/HR MLL-R chemotherapy and lestaurtinib)AsparaginasePopulation Description: Eligible patients with MLL-R (rearranged). Considered Intermediate Risk (IR) if age \>= 90 days at diagnosis and High Risk (HR) if age \< 90 days at diagnosis.
Arm C (IR/HR MLL-R chemotherapy and lestaurtinib)CytarabinePopulation Description: Eligible patients with MLL-R (rearranged). Considered Intermediate Risk (IR) if age \>= 90 days at diagnosis and High Risk (HR) if age \< 90 days at diagnosis.
Arm C (IR/HR MLL-R chemotherapy and lestaurtinib)DexamethasonePopulation Description: Eligible patients with MLL-R (rearranged). Considered Intermediate Risk (IR) if age \>= 90 days at diagnosis and High Risk (HR) if age \< 90 days at diagnosis.
Arm C (IR/HR MLL-R chemotherapy and lestaurtinib)CyclophosphamidePopulation Description: Eligible patients with MLL-R (rearranged). Considered Intermediate Risk (IR) if age \>= 90 days at diagnosis and High Risk (HR) if age \< 90 days at diagnosis.
Arm C (IR/HR MLL-R chemotherapy and lestaurtinib)EtoposidePopulation Description: Eligible patients with MLL-R (rearranged). Considered Intermediate Risk (IR) if age \>= 90 days at diagnosis and High Risk (HR) if age \< 90 days at diagnosis.
Arm C (IR/HR MLL-R chemotherapy and lestaurtinib)LestaurtinibPopulation Description: Eligible patients with MLL-R (rearranged). Considered Intermediate Risk (IR) if age \>= 90 days at diagnosis and High Risk (HR) if age \< 90 days at diagnosis.
Arm C (IR/HR MLL-R chemotherapy and lestaurtinib)MethotrexatePopulation Description: Eligible patients with MLL-R (rearranged). Considered Intermediate Risk (IR) if age \>= 90 days at diagnosis and High Risk (HR) if age \< 90 days at diagnosis.
Arm C (IR/HR MLL-R chemotherapy and lestaurtinib)MercaptopurinePopulation Description: Eligible patients with MLL-R (rearranged). Considered Intermediate Risk (IR) if age \>= 90 days at diagnosis and High Risk (HR) if age \< 90 days at diagnosis.
Arm C (IR/HR MLL-R chemotherapy and lestaurtinib)PegaspargasePopulation Description: Eligible patients with MLL-R (rearranged). Considered Intermediate Risk (IR) if age \>= 90 days at diagnosis and High Risk (HR) if age \< 90 days at diagnosis.
Arm C (IR/HR MLL-R chemotherapy and lestaurtinib)PrednisonePopulation Description: Eligible patients with MLL-R (rearranged). Considered Intermediate Risk (IR) if age \>= 90 days at diagnosis and High Risk (HR) if age \< 90 days at diagnosis.
Arm A (standard risk MLL-G)MethylprednisolonePopulation Description: Eligible patients with MLL-G (germline, or non-rearranged)
Arm B (IR/HR MLL-R chemotherapy)MethylprednisolonePopulation Description: Eligible patients with MLL-R (rearranged). Considered Intermediate Risk (IR) if age \>= 90 days at diagnosis and High Risk (HR) if age \< 90 days at diagnosis.
Arm C (IR/HR MLL-R chemotherapy and lestaurtinib)MethylprednisolonePopulation Description: Eligible patients with MLL-R (rearranged). Considered Intermediate Risk (IR) if age \>= 90 days at diagnosis and High Risk (HR) if age \< 90 days at diagnosis.
Primary Outcome Measures
NameTimeMethod
Percent Probability for Event-free Survival (EFS) for Patients on Arm C at Dose Level 2 (DL2)From start of post-induction therapy for up to 10 years

EFS time is defined as time from randomization to first event (relapse, second malignant neoplasm, death) or date of last contact for patients who are event-free. EFS is constructed using the Kaplan-Meier life table method with confidence interval based on standard errors computed using the method of Peto and Peto.

Secondary Outcome Measures
NameTimeMethod
Identification of Gene Expression Patterns in Diagnostic Infant Leukemia Samples That Correlate With PIA ValuesAt 3 years

Means and standard deviations of Plasma Inhibitory Activity (PIA) will be given by genotype

Percent Probability for Event-free Survival (EFS) of MLL-R Infants Treated With Combination Chemotherapy With or Without Lestaurtinib at DL2From start of post-induction therapy for up to 10 years.

Event Free Probability where EFS time is defined as time from randomization to first event (relapse, second malignant neoplasm, death) or date of last contact for patients who are event-free. EFS is constructed using the Kaplan-Meier life table method with confidence interval based on standard errors computed using the method of Peto and Peto. EFS will be compared between patients on treatment Arm C at DL2 to those on Arm B.

Number of Patients Who Experienced Lestaurtinib-related Dose Limiting Toxicity (DLT)Up to 12 weeks from start of induction

Lestaurtinib-related dose-limiting toxicity proportions, as measured by NCI Common Terminology Criteria for Adverse Events (CTCAE) version 4.0, will by summarized by dose level for Safety phase patients.

Describe FLT3 Protein Expression as a Molecular Mechanism of Acquired Resistance to Lestaurtinib in Leukemic BlastsAt relapse (up to 3 years)

Described via means and standard deviations in available Arm C relapse samples

Describe in Vitro Sensitivity as a Molecular Mechanism of Acquired Resistance to Lestaurtinib in Leukemic BlastsAt relapse (up to 3 years)

Described via means and standard deviations in samples which have acquired resistance to lestaurtinib

Identification of Gene Expression Patterns in Diagnostic Infant Leukemia Samples That Correlate With Survival OutcomesAt 3 years

EFS outcomes will be reported by genotype.

Pharmacokinetic AGP Levels in Infants Given Lestaurtinib at DL2 in Combination With ChemotherapyUp to 12 weeks

Pharmacokinetic AGP levels in infants given lestaurtinib at DL2 in combination with chemotherapy will be described with mean and standard deviation for those with available data.

Describe FLT3 Protein Expression as a Molecular Mechanism of Primary Resistance to Lestaurtinib in Leukemic BlastsSampled at the start of induction

Described via mean and standard deviation by group.

Describe in Vitro Sensitivity as a Molecular Mechanism of Primary Resistance to Lestaurtinib in Leukemic BlastsSampled at the start of induction

Described via means and standard deviations in samples which have primary resistance to lestaurtinib

Percent Probability of Event Free Survival (EFS) by MRD Status and Treatment Arm3 Years from end of Induction)

Three-year EFS estimates and 90% CI will be reported by treatment arm and end-induction MRD status.

Percent Probability for Event-free Survival (EFS) for Patients on Arm AFrom start of post-induction therapy for up to 10 years

EFS time is defined as time from treatment assignment to first event (relapse, second malignant neoplasm, death) or date of last contact for patients who are event-free. EFS is constructed using the Kaplan-Meier life table method with confidence interval based on standard errors computed using the method of Peto and Peto.

Pharmacokinetic Albumin in Infants Given Lestaurtinib at DL2 in Combination With ChemotherapyUp to 12 weeks

Pharmacokinetic albumin in infants given lestaurtinib at DL2 in combination with chemotherapy will be described with mean and standard deviation for those with available data.

Pharmacodynamics PIA Levels in Infants Given Lestaurtinib at DL2 in Combination With ChemotherapySampled between weeks 6-12 from start of induction

Summarized with mean and standard deviation for those with available data in Arm C

Trial Locations

Locations (170)

Children's Hospital of Pittsburgh of UPMC

🇺🇸

Pittsburgh, Pennsylvania, United States

Connecticut Children's Medical Center

🇺🇸

Hartford, Connecticut, United States

MedStar Georgetown University Hospital

🇺🇸

Washington, District of Columbia, United States

Kaiser Permanente-Oakland

🇺🇸

Oakland, California, United States

Lucile Packard Children's Hospital Stanford University

🇺🇸

Palo Alto, California, United States

Advocate Children's Hospital-Park Ridge

🇺🇸

Park Ridge, Illinois, United States

Johns Hopkins All Children's Hospital

🇺🇸

Saint Petersburg, Florida, United States

Augusta University Medical Center

🇺🇸

Augusta, Georgia, United States

Loyola University Medical Center

🇺🇸

Maywood, Illinois, United States

Alfred I duPont Hospital for Children

🇺🇸

Wilmington, Delaware, United States

Golisano Children's Hospital of Southwest Florida

🇺🇸

Fort Myers, Florida, United States

Memorial Health University Medical Center

🇺🇸

Savannah, Georgia, United States

Saint Luke's Cancer Institute - Boise

🇺🇸

Boise, Idaho, United States

Eastern Maine Medical Center

🇺🇸

Bangor, Maine, United States

Lee Memorial Health System

🇺🇸

Fort Myers, Florida, United States

Mercy Children's Hospital

🇺🇸

Toledo, Ohio, United States

Hackensack University Medical Center

🇺🇸

Hackensack, New Jersey, United States

Novant Health Presbyterian Medical Center

🇺🇸

Charlotte, North Carolina, United States

ProMedica Toledo Hospital/Russell J Ebeid Children's Hospital

🇺🇸

Toledo, Ohio, United States

Overlook Hospital

🇺🇸

Summit, New Jersey, United States

Laura and Isaac Perlmutter Cancer Center at NYU Langone

🇺🇸

New York, New York, United States

Morristown Medical Center

🇺🇸

Morristown, New Jersey, United States

University of Mississippi Medical Center

🇺🇸

Jackson, Mississippi, United States

BI-LO Charities Children's Cancer Center

🇺🇸

Greenville, South Carolina, United States

Starship Children's Hospital

🇳🇿

Grafton, Auckland, New Zealand

The Steven and Alexandra Cohen Children's Medical Center of New York

🇺🇸

New Hyde Park, New York, United States

Covenant Children's Hospital

🇺🇸

Lubbock, Texas, United States

Sanford Broadway Medical Center

🇺🇸

Fargo, North Dakota, United States

Advocate Children's Hospital-Oak Lawn

🇺🇸

Oak Lawn, Illinois, United States

University of Vermont and State Agricultural College

🇺🇸

Burlington, Vermont, United States

Saint Peter's University Hospital

🇺🇸

New Brunswick, New Jersey, United States

Columbia Regional

🇺🇸

Columbia, Missouri, United States

University of New Mexico Cancer Center

🇺🇸

Albuquerque, New Mexico, United States

Roswell Park Cancer Institute

🇺🇸

Buffalo, New York, United States

Saint Christopher's Hospital for Children

🇺🇸

Philadelphia, Pennsylvania, United States

Nationwide Children's Hospital

🇺🇸

Columbus, Ohio, United States

Rutgers Cancer Institute of New Jersey-Robert Wood Johnson University Hospital

🇺🇸

New Brunswick, New Jersey, United States

Geisinger Medical Center

🇺🇸

Danville, Pennsylvania, United States

Carolinas Medical Center/Levine Cancer Institute

🇺🇸

Charlotte, North Carolina, United States

British Columbia Children's Hospital

🇨🇦

Vancouver, British Columbia, Canada

Greenville Cancer Treatment Center

🇺🇸

Greenville, South Carolina, United States

East Tennessee Childrens Hospital

🇺🇸

Knoxville, Tennessee, United States

Dartmouth Hitchcock Medical Center/Dartmouth Cancer Center

🇺🇸

Lebanon, New Hampshire, United States

Penn State Children's Hospital

🇺🇸

Hershey, Pennsylvania, United States

Albany Medical Center

🇺🇸

Albany, New York, United States

Children's Hospital of Philadelphia

🇺🇸

Philadelphia, Pennsylvania, United States

Scott and White Memorial Hospital

🇺🇸

Temple, Texas, United States

NYU Langone Hospital - Long Island

🇺🇸

Mineola, New York, United States

Saint Joseph's Regional Medical Center

🇺🇸

Paterson, New Jersey, United States

Marshfield Medical Center-Marshfield

🇺🇸

Marshfield, Wisconsin, United States

Children's Hospital Medical Center of Akron

🇺🇸

Akron, Ohio, United States

Newark Beth Israel Medical Center

🇺🇸

Newark, New Jersey, United States

West Virginia University Charleston Division

🇺🇸

Charleston, West Virginia, United States

Sanford USD Medical Center - Sioux Falls

🇺🇸

Sioux Falls, South Dakota, United States

CancerCare Manitoba

🇨🇦

Winnipeg, Manitoba, Canada

Mary Bridge Children's Hospital and Health Center

🇺🇸

Tacoma, Washington, United States

IWK Health Centre

🇨🇦

Halifax, Nova Scotia, Canada

Texas Tech University Health Sciences Center-Amarillo

🇺🇸

Amarillo, Texas, United States

Prisma Health Richland Hospital

🇺🇸

Columbia, South Carolina, United States

Children's Hospital of Eastern Ontario

🇨🇦

Ottawa, Ontario, Canada

Inova Fairfax Hospital

🇺🇸

Falls Church, Virginia, United States

Alberta Children's Hospital

🇨🇦

Calgary, Alberta, Canada

University of Alberta Hospital

🇨🇦

Edmonton, Alberta, Canada

Medical City Dallas Hospital

🇺🇸

Dallas, Texas, United States

Madigan Army Medical Center

🇺🇸

Tacoma, Washington, United States

Saint Vincent Hospital Cancer Center Green Bay

🇺🇸

Green Bay, Wisconsin, United States

Cook Children's Medical Center

🇺🇸

Fort Worth, Texas, United States

Driscoll Children's Hospital

🇺🇸

Corpus Christi, Texas, United States

UT Southwestern/Simmons Cancer Center-Dallas

🇺🇸

Dallas, Texas, United States

Valley Children's Hospital

🇺🇸

Madera, California, United States

Children's Healthcare of Atlanta - Egleston

🇺🇸

Atlanta, Georgia, United States

Lurie Children's Hospital-Chicago

🇺🇸

Chicago, Illinois, United States

University of Illinois

🇺🇸

Chicago, Illinois, United States

University of Chicago Comprehensive Cancer Center

🇺🇸

Chicago, Illinois, United States

Rainbow Babies and Childrens Hospital

🇺🇸

Cleveland, Ohio, United States

Cleveland Clinic Foundation

🇺🇸

Cleveland, Ohio, United States

University of Arkansas for Medical Sciences

🇺🇸

Little Rock, Arkansas, United States

Kaiser Permanente Downey Medical Center

🇺🇸

Downey, California, United States

Loma Linda University Medical Center

🇺🇸

Loma Linda, California, United States

Miller Children's and Women's Hospital Long Beach

🇺🇸

Long Beach, California, United States

Nemours Children's Clinic-Jacksonville

🇺🇸

Jacksonville, Florida, United States

Advocate Lutheran General Hospital

🇺🇸

Park Ridge, Illinois, United States

University of Maryland/Greenebaum Cancer Center

🇺🇸

Baltimore, Maryland, United States

Sinai Hospital of Baltimore

🇺🇸

Baltimore, Maryland, United States

Johns Hopkins University/Sidney Kimmel Cancer Center

🇺🇸

Baltimore, Maryland, United States

Tufts Children's Hospital

🇺🇸

Boston, Massachusetts, United States

Michigan State University Clinical Center

🇺🇸

East Lansing, Michigan, United States

Hurley Medical Center

🇺🇸

Flint, Michigan, United States

Bronson Methodist Hospital

🇺🇸

Kalamazoo, Michigan, United States

Corewell Health Grand Rapids Hospitals - Helen DeVos Children's Hospital

🇺🇸

Grand Rapids, Michigan, United States

Kalamazoo Center for Medical Studies

🇺🇸

Kalamazoo, Michigan, United States

Dayton Children's Hospital

🇺🇸

Dayton, Ohio, United States

Providence Sacred Heart Medical Center and Children's Hospital

🇺🇸

Spokane, Washington, United States

Janeway Child Health Centre

🇨🇦

Saint John's, Newfoundland and Labrador, Canada

Children's Hospital

🇨🇦

London, Ontario, Canada

Saskatoon Cancer Centre

🇨🇦

Saskatoon, Saskatchewan, Canada

Baylor College of Medicine/Dan L Duncan Comprehensive Cancer Center

🇺🇸

Houston, Texas, United States

University of Miami Miller School of Medicine-Sylvester Cancer Center

🇺🇸

Miami, Florida, United States

Ascension Saint Vincent Indianapolis Hospital

🇺🇸

Indianapolis, Indiana, United States

Miami Cancer Institute

🇺🇸

Miami, Florida, United States

Riley Hospital for Children

🇺🇸

Indianapolis, Indiana, United States

Alliance for Childhood Diseases/Cure 4 the Kids Foundation

🇺🇸

Las Vegas, Nevada, United States

Summerlin Hospital Medical Center

🇺🇸

Las Vegas, Nevada, United States

Nevada Cancer Research Foundation NCORP

🇺🇸

Las Vegas, Nevada, United States

Cincinnati Children's Hospital Medical Center

🇺🇸

Cincinnati, Ohio, United States

Rady Children's Hospital - San Diego

🇺🇸

San Diego, California, United States

Children's Hospitals and Clinics of Minnesota - Minneapolis

🇺🇸

Minneapolis, Minnesota, United States

University of Minnesota/Masonic Cancer Center

🇺🇸

Minneapolis, Minnesota, United States

Duke University Medical Center

🇺🇸

Durham, North Carolina, United States

Methodist Children's Hospital of South Texas

🇺🇸

San Antonio, Texas, United States

University of Texas Health Science Center at San Antonio

🇺🇸

San Antonio, Texas, United States

UCSF Medical Center-Parnassus

🇺🇸

San Francisco, California, United States

UCSF Medical Center-Mission Bay

🇺🇸

San Francisco, California, United States

Vanderbilt University/Ingram Cancer Center

🇺🇸

Nashville, Tennessee, United States

Primary Children's Hospital

🇺🇸

Salt Lake City, Utah, United States

Children's Hospital of Orange County

🇺🇸

Orange, California, United States

University of Rochester

🇺🇸

Rochester, New York, United States

Princess Margaret Hospital for Children

🇦🇺

Perth, Western Australia, Australia

Children's Hospital of Alabama

🇺🇸

Birmingham, Alabama, United States

Phoenix Childrens Hospital

🇺🇸

Phoenix, Arizona, United States

University of Alabama at Birmingham Cancer Center

🇺🇸

Birmingham, Alabama, United States

Wayne State University/Karmanos Cancer Institute

🇺🇸

Detroit, Michigan, United States

University of Oklahoma Health Sciences Center

🇺🇸

Oklahoma City, Oklahoma, United States

Rocky Mountain Hospital for Children-Presbyterian Saint Luke's Medical Center

🇺🇸

Denver, Colorado, United States

Legacy Emanuel Children's Hospital

🇺🇸

Portland, Oregon, United States

Legacy Emanuel Hospital and Health Center

🇺🇸

Portland, Oregon, United States

Hospital for Sick Children

🇨🇦

Toronto, Ontario, Canada

The Montreal Children's Hospital of the MUHC

🇨🇦

Montreal, Quebec, Canada

Children's Hospital Colorado

🇺🇸

Aurora, Colorado, United States

Saint Joseph's Hospital/Children's Hospital-Tampa

🇺🇸

Tampa, Florida, United States

Children's Hospital and Medical Center of Omaha

🇺🇸

Omaha, Nebraska, United States

Children's Hospital of Wisconsin

🇺🇸

Milwaukee, Wisconsin, United States

State University of New York Upstate Medical University

🇺🇸

Syracuse, New York, United States

Mayo Clinic in Rochester

🇺🇸

Rochester, Minnesota, United States

Children's National Medical Center

🇺🇸

Washington, District of Columbia, United States

Nemours Children's Clinic - Pensacola

🇺🇸

Pensacola, Florida, United States

East Carolina University

🇺🇸

Greenville, North Carolina, United States

Saint Mary's Hospital

🇺🇸

West Palm Beach, Florida, United States

Mercy Hospital Saint Louis

🇺🇸

Saint Louis, Missouri, United States

Mission Hospital

🇺🇸

Asheville, North Carolina, United States

University of California Davis Comprehensive Cancer Center

🇺🇸

Sacramento, California, United States

C S Mott Children's Hospital

🇺🇸

Ann Arbor, Michigan, United States

Wake Forest University Health Sciences

🇺🇸

Winston-Salem, North Carolina, United States

Orlando Health Cancer Institute

🇺🇸

Orlando, Florida, United States

Nemours Children's Hospital

🇺🇸

Orlando, Florida, United States

AdventHealth Orlando

🇺🇸

Orlando, Florida, United States

Arnold Palmer Hospital for Children

🇺🇸

Orlando, Florida, United States

Norton Children's Hospital

🇺🇸

Louisville, Kentucky, United States

Nemours Children's Clinic - Orlando

🇺🇸

Orlando, Florida, United States

New York Medical College

🇺🇸

Valhalla, New York, United States

Yale University

🇺🇸

New Haven, Connecticut, United States

UCSF Benioff Children's Hospital Oakland

🇺🇸

Oakland, California, United States

Cedars Sinai Medical Center

🇺🇸

Los Angeles, California, United States

Saint Barnabas Medical Center

🇺🇸

Livingston, New Jersey, United States

Children's Mercy Hospitals and Clinics

🇺🇸

Kansas City, Missouri, United States

UNC Lineberger Comprehensive Cancer Center

🇺🇸

Chapel Hill, North Carolina, United States

Tulane University School of Medicine

🇺🇸

New Orleans, Louisiana, United States

University of Florida Health Science Center - Gainesville

🇺🇸

Gainesville, Florida, United States

University of Hawaii Cancer Center

🇺🇸

Honolulu, Hawaii, United States

Kapiolani Medical Center for Women and Children

🇺🇸

Honolulu, Hawaii, United States

Tripler Army Medical Center

🇺🇸

Honolulu, Hawaii, United States

Children's Hospital New Orleans

🇺🇸

New Orleans, Louisiana, United States

Dell Children's Medical Center of Central Texas

🇺🇸

Austin, Texas, United States

Blank Children's Hospital

🇺🇸

Des Moines, Iowa, United States

University of Kentucky/Markey Cancer Center

🇺🇸

Lexington, Kentucky, United States

Montefiore Medical Center - Moses Campus

🇺🇸

Bronx, New York, United States

University of Wisconsin Carbone Cancer Center - University Hospital

🇺🇸

Madison, Wisconsin, United States

Arkansas Children's Hospital

🇺🇸

Little Rock, Arkansas, United States

Children's Hospital of The King's Daughters

🇺🇸

Norfolk, Virginia, United States

Rhode Island Hospital

🇺🇸

Providence, Rhode Island, United States

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