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Determination of Correct hydroxyurea dose in Dickle Cell Anemia Patients

Phase 3
Conditions
Health Condition 1: D578- Other sickle-cell disorders
Registration Number
CTRI/2020/08/027022
Lead Sponsor
ICMR New Delhi
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
ot Yet Recruiting
Sex
Not specified
Target Recruitment
0
Inclusion Criteria

a) Newly diagnosed patients of less than 18 years of age with sickle cell disease as characterized by three or more painful crisis over the period of 12 months and the requirement of 2 or more blood transfusions over the same period. Painful crisis is defined as a presence of pain for 4 or more hours requiring the intervention with any injectable analgesics.

b) Patients should be homozygous for sickle cell disease (HbSS).

c) Patients willing to provide informed consent and assent.

Exclusion Criteria

a) Patients with other forms of sickle cell syndromes.

b) Patients on any immunosuppressant drugs.

c) Patients with abnormal liver function tests.

d) Patients allergic to any drug provided during the study period.

e) Patients on drugs interfering with the metabolism of hydroxyurea.

Study & Design

Study Type
Interventional
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Efficacy and Safety of Low dose hydroxyurea might be as equally efficacious as normal dose hydroxyurea. <br/ ><br>Timepoint: 1. (-2 weeks): Screening for eligibility <br/ ><br>2. (0 week): Randomization and drug therapy initiation <br/ ><br>3. (2-4 weeks): Follow-up and Pharmacokinetic analysis <br/ ><br>4. (12 weeks): Follow-up, efficacy and safety evaluation <br/ ><br>5. (24 weeks): Follow-up, efficacy and safety evaluation <br/ ><br>6. (36 weeks): Follow-up, efficacy and safety evaluation <br/ ><br>7. (48-52 weeks) Final follow-up, efficacy and safety evaluation and Study Closure
Secondary Outcome Measures
NameTimeMethod
Pharmacogenetic analysisTimepoint: Between 2-4 weeks of drug therapy: <br/ ><br>The cellular component of the blood samples collected during pharmacokinetic analysis will be utilized for pharmacogenetic analysis;Pharmacokinetic parametersTimepoint: Between 2-4 weeks of drug therapy (one time)
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