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Pivotal Study in HER2 Negative, Locally Recurrent or Metastatic Breast Cancer

Phase 3
Terminated
Conditions
Metastatic Breast Cancer
Locally Recurrent Breast Cancer
Interventions
Registration Number
NCT03786094
Lead Sponsor
Spexis AG
Brief Summary

This is a phase 3, multicenter, open-label, randomized active-controlled, parallel group to investigate the efficacy, safety and tolerability of intravenous balixafortide given with eribulin versus eribulin alone in the treatment of HER2 negative, Locally Recurrent or Metastatic Breast Cancer.

Detailed Description

Not available

Recruitment & Eligibility

Status
TERMINATED
Sex
All
Target Recruitment
432
Inclusion Criteria
  • Histologically confirmed Breast cancer
  • Metastatic Breast Cancer currently of stage IV disease or unresectable locoregionally recurrent breast cancer
  • refractory to the most recent chemotherapy, documented by progression on or within six (6) months of therapy
  • At least 14 days from the completion of any previous cancer therapy
  • Adequate organ function
  • Life expectancy of 3 months or more
  • Willing and able to comply with the protocol and able to understand and willing to sign an informed consent

Key

Exclusion Criteria
  • Previously treated with eribulin
  • Peripheral neuropathy Grade ≥3
  • Receipt of prior CXCR4 therapy
  • Receipt of colony stimulating factors (CSFs) filgrastim, pegfilgrastim, or sargramostim, or radiation therapy within 14 days prior to study Day 1
  • History of allergic reactions attributed to compounds of similar chemical or biologic composition to balixafortide or eribulin or other agents used in the study
  • Breast feeding or pregnant
  • Patients with congestive heart failure, electrolyte abnormalities, bradyarrhythmias, known congenital long QT syndrome, QT interval corrected with Fridericia's formula (QTcF) ≥470 msec at baseline in the absence of bundle branch block, or currently taking drugs at known risk of prolonging the QT interval or causing torsades de pointes

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
EribulinEribulin-
Balixafortide + EribulinEribulin-
Balixafortide + EribulinBalixafortide-
Primary Outcome Measures
NameTimeMethod
Progression Free Survival (2nd Line+ Population)Patients received treatment until PD by RECIST v1.1 criteria was met or until one of the treatment discontinuation or study withdrawal criteria was met.

To evaluate the efficacy of balixafortide + eribulin versus eribulin monotherapy on the primary endpoint of progression free survival (PFS). PFS, as assessed by the Independent Review Committee, defined as the time from the date of randomization to the earliest evidence of documented progressive disease or death from any cause. Patients who were alive without postbaseline assessments or without documented progressive disease, lost to follow-up, withdrew consent, started an anticancer therapy prior to observing a progressive disease or with an event documented after 2 or more missing tumor assessments were censored.

PFS was evaluated according to RECIST v1.1 guidelines for complete response (CR), partial response (PR), stable disease (SD), or progressive disease (PD).

Progression Free Survival (3rd Line+ Population)Patients received treatment until PD by RECIST v1.1 criteria was met or until one of the treatment discontinuation or study withdrawal criteria was met.

To evaluate the efficacy of balixafortide + eribulin versus eribulin monotherapy on the primary endpoint of progression free survival (PFS). PFS, as assessed by the Independent Review Committee, defined as the time from the date of randomization to the earliest evidence of documented progressive disease or death from any cause. Patients who were alive without postbaseline assessments or without documented progressive disease, lost to follow-up, withdrew consent, started an anticancer therapy prior to observing a progressive disease or with an event documented after 2 or more missing tumor assessments were censored.

PFS was evaluated according to RECIST v1.1 guidelines for complete response (CR), partial response (PR), stable disease (SD), or progressive disease (PD).

Secondary Outcome Measures
NameTimeMethod
Overall Survival (3rd Line+ Population)The Investigator monitored the patient for OS status every 6 months (or more frequently) until: death, the patient withdrew consent to follow-up for survival, or until the patient was lost to follow-up (whichever occurred first).

To compare the overall survival (OS) between patients in the balixafortide + eribulin treatment arm versus eribulin monotherapy treatment arm. OS is defined as the time from date of randomization to date of death due to any cause. Patients who are lost to follow-up or are not known to have died at the time of data-cut-off for analysis or who do not have any follow up since randomization were censored.

Trial Locations

Locations (88)

California Cancer Associates for Research and Excellence

🇺🇸

Fresno, California, United States

Tallahassee Memorial HealthCare

🇺🇸

Tallahassee, Florida, United States

West Virginia University Hospital

🇺🇸

Morgantown, West Virginia, United States

Comprehensive Cancer Centers of Nevada

🇺🇸

Las Vegas, Nevada, United States

Grand Hopital de Charleroi asbl

🇧🇪

Charleroi, Hainaut, Belgium

UZ Gent

🇧🇪

Gent, Belgium

Volgograd Regional Clinical Oncology Dispensary

🇷🇺

Volgograd, Russian Federation

LLC Evimed

🇷🇺

Chelyabinsk, Russian Federation

Taipei Veterans General Hospital

🇨🇳

Taipei, Taiwan

UCSF Mount Zion Cancer Center

🇺🇸

San Francisco, California, United States

Virginia Piper Cancer Institute

🇺🇸

Minneapolis, Minnesota, United States

Sarah Cannon Research Institute

🇺🇸

Nashville, Tennessee, United States

Florida Cancer Specialists SOUTH - SCRI - PPDS

🇺🇸

Fort Myers, Florida, United States

CHI Health St. Francis

🇺🇸

Grand Island, Nebraska, United States

Florida Cancer Specialists NORTH - SCRI - PPDS

🇺🇸

Saint Petersburg, Florida, United States

Orchard Healthcare Research Inc

🇺🇸

Skokie, Illinois, United States

Herbert-Herman Cancer Center, Sparrow Hospital

🇺🇸

Lansing, Michigan, United States

Mercy Research Oncology

🇺🇸

Saint Louis, Missouri, United States

Centro Polivalente de Asistencia e Investigación Clínica - CER San Juan

🇦🇷

San Juan, Buenos Aires, Argentina

Sanatorio Parque de Rosario

🇦🇷

Rosario, Santa Fe, Argentina

UZ Antwerpen

🇧🇪

Antwerpen, Belgium

CHIREC Centre Hospitalier Interregional Edith Cavell

🇧🇪

Brussels, Belgium

CHU de Liège

🇧🇪

Liège, Belgium

Centro de Oncologia Da Bahia

🇧🇷

Bahia, Brazil

Azienda Ospedaliero Universitaria Di Bologna - Policlinico S Orsola Malpighi

🇮🇹

Bologna, Italy

Fakultni nemocnice v Motole

🇨🇿

Prague, Czechia

Hospital de Base Da Faculdade de Medicina de São José Do Rio Preto

🇧🇷

São José Do Rio Preto, Brazil

Centre Léon Bérard Centre Régional de Lutte Contre Le Cancer Rhône Alpes

🇫🇷

Lyon, France

Institut de Cancérologie de l'Ouest

🇫🇷

Saint-Herblain, France

Ospedale San Raffaele S.r.l. - PPDS

🇮🇹

Milano, Lombardia, Italy

Asan Medical Center

🇰🇷

Seoul, Korea, Republic of

Hospital Universitario Virgen Macarena

🇪🇸

Sevilla, Andalucia, Spain

Krasnoyarsk Regional Oncology Center n.a. A.I. Kryzhanovskiy

🇷🇺

Krasnoyarsk, Russian Federation

Medical Center Tonus

🇷🇺

Nizhny Novgorod, Russian Federation

Budgetary Healthcare Institution of the Omsk region "Clinical Oncology Dispensary"

🇷🇺

Omsk, Russian Federation

Evromedservis LCC

🇷🇺

Pushkin, Russian Federation

Mordovia State University

🇷🇺

Saransk, Russian Federation

Hospital Quironsalud Barcelona

🇪🇸

Barcelona, Cataluña, Spain

Hospital Universitari Arnau de Vilanova

🇪🇸

Lleida, Cataluña, Spain

Hospital Universitario A Coruña

🇪🇸

A Coruña, Spain

Hospital Universitario de Badajoz

🇪🇸

Badajoz, Spain

Hospital General Universitario Gregorio Marañon

🇪🇸

Madrid, Spain

Chi Mei Medical Center, Liouying

🇨🇳

Tainan City, Taiwan

LLC Medical Center Family Medicine Clinic

🇺🇦

Dnipro, Ukraine

Leicester Royal Infirmary

🇬🇧

Leicester, United Kingdom

Municipal Institution City Clinical Hospital #4 of Dnipro City Council - PPDS

🇺🇦

Dnipro, Ukraine

Municipal Institution SubCarpathian Clinical Oncological Centre

🇺🇦

Ivano-Frankivs'k, Ukraine

Koo Foundation Sun Yat-Sen Cancer Center

🇨🇳

Taipei, Taiwan

Azienda Ospedaliera Universitaria - Università degli studi della Campania "Luigi Vanvitelli"

🇮🇹

Napoli, Italy

Universidade de Caxias do Sul (IPCEM-UCS)

🇧🇷

Caxias Do Sul, Brazil

Hospital Ruber Internacional

🇪🇸

Madrid, Spain

Hospital Clinico San Carlos

🇪🇸

Madrid, Spain

Florida Cancer Specialists EAST - SCRI - PPDS

🇺🇸

West Palm Beach, Florida, United States

Cedars-Sinai Medical Center

🇺🇸

Los Angeles, California, United States

Norwalk Hospital

🇺🇸

Norwalk, Connecticut, United States

Florida Cancer Specialists PAN - SCRI - PPDS

🇺🇸

Tallahassee, Florida, United States

University Cancer and Blood Center, LLC

🇺🇸

Athens, Georgia, United States

Magee Women's Hospital

🇺🇸

Pittsburgh, Pennsylvania, United States

Queens Hospital Cancer Center

🇺🇸

New York, New York, United States

Vanderbilt University Medical Center

🇺🇸

Tennessee, Tennessee, United States

Centro de Investigación Clínica - Clínica Viedma

🇦🇷

Viedma, Río Negro, Argentina

CAIPO Centro para la atención integral del paciente oncológico

🇦🇷

San Miguel De Tucumán, Argentina

Liga Paranaense de Combate Ao Cancer - Hospital Erasto Gaertner

🇧🇷

Curitiba, Brazil

Hospital Sao Lucas Da Pontificia Universidade Catolica Do Rio Grande Do Sul (PUCRS)

🇧🇷

Porto Alegre, Brazil

Clinica de Pesquisas e Centro de Estudos Oncologia Ginecologica e Mamaria Ltda

🇧🇷

São Paulo, Brazil

INCA Instituto Nacional De Cancer

🇧🇷

Rio De Janeiro, Brazil

Fakultni nemocnice Hradec Kralove

🇨🇿

Hradec Králové, Czechia

Multiscan s.r.o - Onkologická ambulance

🇨🇿

Hořovice, Czechia

EDOG - Institut Claudius Regaud - PPDS

🇫🇷

Toulouse, France

ASST di Monza - Azienda Ospedaliera San Gerardo

🇮🇹

Monza, Milano, Italy

Azienda Ospedaliero Universitaria Policlinico Vittorio Emanuele

🇮🇹

Catania, Italy

National Cancer Center

🇰🇷

Goyang-si, Korea, Republic of

Ulsan University Hospital

🇰🇷

Ulsan, Korea, Republic of

Samsung Medical Center

🇰🇷

Seul, Korea, Republic of

Hospital Universitario Germans Trias i Pujol

🇪🇸

Badalona, Barcelona, Spain

Research Oncology Institute of Tomsk Scientific Center

🇷🇺

Tomsk, Russian Federation

ICO l'Hospitalet - Hospital Duran i Reynals

🇪🇸

L'Hospitalet De Llobregat, Barcelona, Spain

Hospital Universitario Vall D'Hebrón

🇪🇸

Barcelona, Spain

Hospital Clinico Universitario de Valencia

🇪🇸

Valencia, Spain

CNCE of Lviv Regional Council Lviv Oncological Regional Therapeutical and Diagnostic Centre

🇺🇦

Lviv, Ukraine

University of Vermont Medical Center

🇺🇸

Burlington, Vermont, United States

Stanford Cancer Center South Bay

🇺🇸

San Jose, California, United States

Piedmont Cancer Institute PC

🇺🇸

Atlanta, Georgia, United States

Orlando Health

🇺🇸

Orlando, Florida, United States

Saint Luke's Cancer Institute 150 Entrance

🇺🇸

Kansas City, Missouri, United States

HCA Midwest Health - SCRI - PPDS

🇺🇸

Kansas City, Missouri, United States

OHSU Knight Cancer Institute Hematology Oncology

🇺🇸

Portland, Oregon, United States

Barts Cancer Institute

🇬🇧

London, United Kingdom

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