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Azacitidine in Treating Patients With Chronic Myelomonocytic Leukemia

Phase 2
Completed
Conditions
Leukemia
Registration Number
NCT01235117
Lead Sponsor
University of Leeds
Brief Summary

RATIONALE: Drugs used in chemotherapy, such as azacitidine, work in different ways to stop the growth of cancer cells, either by killing the cells or by stopping them from dividing.

PURPOSE: This phase II trial is studying the side effects of azacitidine and to see how well it works in treating patients with chronic myelomonocytic leukemia.

Detailed Description

OBJECTIVES:

Primary

* To assess the safety and tolerability of azacitidine in patients with chronic myelomonocytic leukemia (CMML).

* To assess the overall response rate in these patients.

Secondary

* To assess the incidence of clinical remission/complete remission or partial response in these patients.

* To assess hematological improvement in patients treated with this drug.

* To assess the overall survival of patients treated with this drug.

* To assess progression-free survival of patients treated with this drug.

* To assess the time to acute myeloid leukemia (AML) transformation of CMML.

* To assess the time to death or AML transformation of CMML.

* To assess the biological correlates.

OUTLINE: This is a multicenter study.

Patients receive azacitidine subcutaneously on days 1-5 and 8-9. Treatment repeats every 4 weeks for at least 6 courses in the absence of loss of response/disease progression or unacceptable toxicity. Patients undergo response evaluation after 6 courses or the last course of treatment. Responders may continue azacitidine until loss of response/disease progression or unacceptable toxicity.

Some patients undergo blood, bone marrow, and buccal swab sample collection periodically for correlative studies.

After completion of study treatment, patients are followed up for 1 month.

Peer Reviewed and Funded or Endorsed by Cancer Research UK

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
30
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Safety and tolerability
Overall response rate
Secondary Outcome Measures
NameTimeMethod
Incidence of clinical remission/complete remission or partial response according to International Working Group (IWG) criteria
Hematological improvement according to IWG criteria
Overall survival
Progression-free survival
Time to acute myeloid leukemia (AML) transformation of CMML
Time to death or AML transformation of CMML
Biological correlates

Trial Locations

Locations (2)

Leeds Cancer Centre at St. James's University Hospital

🇬🇧

Leeds, England, United Kingdom

Beatson West of Scotland Cancer Centre

🇬🇧

Glasgow, Scotland, United Kingdom

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