Outcome of treatment with Triheptanoin in pediatric patients with long chain fatty acid oxidation disorders (LCFAODs)

• Conditions: longchain fatty acid oxidation disorders (LCFAODs); long; chain fatty acid oxidation disorders (LCFAODs), outcome, treatment

• Registration Number: TCTR20210604002
• Lead Sponsor: /A

Brief Summary

Not available

Detailed Description

Not available

Study Timeline

• Study Start: 2021-06-04
• Study Completion: 2022-07-31
• Last Update Posted: 19 August 2024

Recruitment & Eligibility

• Status: Pending (Not yet recruiting)
• Sex: All
• Target Recruitment: 2

Inclusion Criteria

Patient with diagnosis of long
chain fatty acid oxidation disorders (LCFAODs)

Exclusion Criteria

can not continue treatment until the end of research

Study & Design

• Study Type: Observational
• Study Design: Not specified

Primary Outcome Measures

Name	Time	Method
frequency of hospitalization with rhabdomyolysis 2 years number

Secondary Outcome Measures

Name	Time	Method
abnormality of the cardiac muscles 2 years echo