MedPath

A Study to Evaluate the Safety, Tolerability, Pharmacokinetics, and Efficacy of RO7446603 Administered Alone or in Combination With Aflibercept or Faricimab in Participants With Diabetic Macular Edema

Phase 1
Recruiting
Conditions
Diabetic Macular Edema
Interventions
Registration Number
NCT06850922
Lead Sponsor
Genentech, Inc.
Brief Summary

This study aims to evaluate the ocular and systemic safety, tolerability and efficacy of RO7446603 in participants with diabetic macular edema (DME). The study consists of 2 segments: Phase I (Parts 1-4) and Phase II (Part 5). Phase I investigated the safety of RO7446603 following a single and multiple intravitreal (IVT) doses as monotherapy or co-administered with IVT aflibercept or IVT faricimab (in separate injections). Phase II will investigate the safety, tolerability, pharmacokinetics (PK) and efficacy of two dose levels of RO7446603 in combination with faricimab, with the two drugs co-mixed and administered as a single IVT injection, compared to faricimab alone. The first participant was enrolled in the Phase I segment on June 22, 2022. Phase I has been completed.

Detailed Description

Not available

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
546
Inclusion Criteria
  • Documented diagnosis of diabetes mellitus (DM) (Type 1 or Type 2) with glycated hemoglobin (HbA1c) < 12%
  • Macular thickening secondary to DME involving the center of the fovea > 325 microns
  • Decreased VA attributable primarily to DME between 25 and 73 ETDRS letters
Exclusion Criteria
  • Currently untreated DM or previously untreated participants who initiated oral anti-diabetic medication or insulin within 90 days prior to Day 1
  • Uncontrolled blood pressure (BP)
  • Pregnancy or breastfeeding, or intention to become pregnant during the study
  • For Parts 1-4: IVT anti-VEGF treatment within 90 days prior to Day 1; For Part 5: IVT anti-VEGF treatment within 120 days prior to Day 1 or IVT anti-VEGF treatment prior to Day 1 for treatment naïve participants
  • Treatment with SUSVIMOTM (ranibizumab injection) prior to Day 1
  • Any IVT or periocular (sub-tenons) corticosteroid treatment within 6 months prior to Day 1
  • Any current or history of ocular disease other than DME that may confound assessment of the macula or affect central vision
  • Proliferative diabetic retinopathy (PDR) in the study eye
  • Active or history of uveitis, vitritis (grade trace or above), and/or scleritis in either eye Other protocol-specified inclusion/exclusion criteria may apply

Study & Design

Study Type
INTERVENTIONAL
Study Design
SEQUENTIAL
Arm && Interventions
GroupInterventionDescription
Part 1: Single Ascending Dose (SAD) StageRO7446603Participants received a single dose of RO7446603 at five different dose levels as IVT injection on Day 1.
Part 2: Multiple Dose (MD) Monotherapy StageRO7446603Participants received four different dose levels of RO7446603 (two doses at each planned dose level) as IVT injection, every 8 weeks (Q8W).
Part 3: MD Co-administration With Aflibercept StageRO7446603Participants received two different dose levels (two doses at each planned dose level) of RO7446603 as IVT injection, Q8W along with four doses of aflibercept IVT injections, every 4 weeks (Q4W).
Part 3: MD Co-administration With Aflibercept StageAfliberceptParticipants received two different dose levels (two doses at each planned dose level) of RO7446603 as IVT injection, Q8W along with four doses of aflibercept IVT injections, every 4 weeks (Q4W).
Part 4: MD Co-administration With Faricimab StageFaricimabParticipants received a single dose of faricimab followed by a 4-week enrichment screening period. Eligible participants received two different dose levels (two doses at each planned dose level) of RO7446603 as IVT injection, Q8W, along with three doses of faricimab (co-administered with RO7446603 or alone) as IVT injection, Q4W.
Part 5: MD Co-mixed With Faricimab StageFaricimabParticipants will receive two different dose levels of RO7446603 (co-mixed with faricimab or faricimab alone) as IVT injection, Q4W for the first six doses followed by Q8W for four doses.
Part 4: MD Co-administration With Faricimab StageRO7446603Participants received a single dose of faricimab followed by a 4-week enrichment screening period. Eligible participants received two different dose levels (two doses at each planned dose level) of RO7446603 as IVT injection, Q8W, along with three doses of faricimab (co-administered with RO7446603 or alone) as IVT injection, Q4W.
Part 5: MD Co-mixed With Faricimab StageRO7446603Participants will receive two different dose levels of RO7446603 (co-mixed with faricimab or faricimab alone) as IVT injection, Q4W for the first six doses followed by Q8W for four doses.
Primary Outcome Measures
NameTimeMethod
Parts 1-5: Percentage of Participants With Adverse Events (AEs)From study start through end of study (Up to approximately 58 months)
Parts 1-5: Percentage of Participants With Ocular AEsFrom study start through end of study (Up to approximately 58 months)
Part 1: Change in Best Corrected Visual Acuity (BCVA) Over TimeFrom Baseline up to Week 16

BCVA will be measured via Early Treatment Diabetic Retinopathy Study (ETDRS) chart at a starting distance of 4 meters using a set of three precision VisionTM or lighthouse distance acuity charts (modified ETDRS Charts 1, 2, and R) prior to dilating eyes by a trained and certified visual acuity (VA) examiner. The range of EDTRS is 0 to 100 letters. Higher scores indicate improvement in VA.

Parts 2-4: Change in BCVA Over TimeFrom Baseline up to Week 28

BCVA will be measured via ETDRS chart at a starting distance of 4 meters using a set of three precision VisionTM or lighthouse distance acuity charts (modified ETDRS Charts 1, 2, and R) prior to dilating eyes by a trained and certified VA examiner. The range of EDTRS is 0 to 100 letters. Higher scores indicate improvement in VA.

Part 5: Change From Baseline in BCVA Averaged Over Weeks 52 and 56From Baseline up to Week 56

BCVA will be measured via ETDRS chart at a starting distance of 4 meters using a set of three precision VisionTM or lighthouse distance acuity charts (modified ETDRS Charts 1, 2, and R) prior to dilating eyes by a trained and certified VA examiner. The range of EDTRS is 0 to 100 letters. Higher scores indicate improvement in VA.

Secondary Outcome Measures
NameTimeMethod
Part 5: Proportion of Participants Gaining ≥ 15 Letters in BCVA From Baseline Averaged Over Weeks 52 and 56From Baseline up to Week 56

BCVA will be measured via ETDRS chart at a starting distance of 4 meters using a set of three precision VisionTM or lighthouse distance acuity charts (modified ETDRS Charts 1, 2, and R) prior to dilating eyes by a trained and certified VA examiner. The range of EDTRS is 0 to 100 letters. Higher scores indicate improvement in VA.

Part 5: Percentage of Participants Gaining ≥ 15, ≥ 10, ≥ 5, or ≥ 0 Letters in BCVA From Baseline Over TimeFrom Baseline up to Week 56

BCVA will be measured via ETDRS chart at a starting distance of 4 meters using a set of three precision VisionTM or lighthouse distance acuity charts (modified ETDRS Charts 1, 2, and R) prior to dilating eyes by a trained and certified VA examiner. The range of EDTRS is 0 to 100 letters. Higher scores indicate improvement in VA.

Part 5: Percentage of Participants Avoiding a Loss of ≥ 15, ≥ 10, ≥ 5, or ≥ 0 Letters in BCVA From Baseline Over TimeFrom Baseline up to Week 56

BCVA will be measured via ETDRS chart at a starting distance of 4 meters using a set of three precision VisionTM or lighthouse distance acuity charts (modified ETDRS Charts 1, 2, and R) prior to dilating eyes by a trained and certified VA examiner. The range of EDTRS is 0 to 100 letters. Higher scores indicate improvement in VA.

Parts 1-4: Serum Concentration of RO7446603 Total FabPart 1: From Baseline up to Week 16; Parts 2-4: From Baseline up to Week 28
Parts 1-5: Aqueous Humor Concentration of RO7446603 Measured as Total FabFrom study start through end of study (Up to approximately 58 months)
Part 5: Change From Baseline in BCVA Score Over TimeFrom Baseline up to Week 56

BCVA will be measured via ETDRS chart at a starting distance of 4 meters using a set of three precision VisionTM or lighthouse distance acuity charts (modified ETDRS Charts 1, 2, and R) prior to dilating eyes by a trained and certified VA examiner. The range of EDTRS is 0 to 100 letters. Higher scores indicate improvement in VA.

Parts 1-5: Number of Participants With Serum Treatment-emergent Anti-drug Antibody (ADA) Formation to RO7446603From study start through end of study (Up to approximately 58 months)

Trial Locations

Locations (53)

Barnet Dulaney Perkins Eye Center

🇺🇸

Phoenix, Arizona, United States

Arizona Retina and Vitreous Consultants

🇺🇸

Phoenix, Arizona, United States

Associated Retinal Consultants PC

🇺🇸

Phoenix, Arizona, United States

Retinal Consultants of Arizona

🇺🇸

Phoenix, Arizona, United States

The Retina Partners

🇺🇸

Encino, California, United States

Retina Consultants of Orange County

🇺🇸

Fullerton, California, United States

Retinal Consultants Medical Group

🇺🇸

Sacramento, California, United States

Northern California Retina-Vitreous Associates

🇺🇸

Mountain View, California, United States

Macula Retina Vitreous Research Institute

🇺🇸

Torrance, California, United States

Retina Specialists of Colorado

🇺🇸

Aurora, Colorado, United States

Retina Consultants of Southern Colorado PC

🇺🇸

Colorado Springs, Colorado, United States

Advanced Vision Research Institute

🇺🇸

Longmont, Colorado, United States

Retina Group of New England

🇺🇸

Waterford, Connecticut, United States

Blue Ocean Clinical Research

🇺🇸

Clearwater, Florida, United States

National Ophthalmic Research Institute

🇺🇸

Fort Myers, Florida, United States

Retina Associates of Florida;Retina Associates of Florida

🇺🇸

Tampa, Florida, United States

Georgia Retina PC

🇺🇸

Marietta, Georgia, United States

University Retina and Macula Associates, PC

🇺🇸

Lemont, Illinois, United States

Raj K. Maturi, MD PC

🇺🇸

Indianapolis, Indiana, United States

The Retina Care Center

🇺🇸

Baltimore, Maryland, United States

Johns Hopkins Hospital

🇺🇸

Baltimore, Maryland, United States

Retina Group of Washington

🇺🇸

Chevy Chase, Maryland, United States

Cumberland Valley Retina Consultants

🇺🇸

Hagerstown, Maryland, United States

Long Island Vitreoretinal Consultants;Opthalmology

🇺🇸

Hauppauge, New York, United States

Western Carolina Retinal Associate PA

🇺🇸

Asheville, North Carolina, United States

Duke University Medical Center

🇺🇸

Durham, North Carolina, United States

Graystone Eye

🇺🇸

Hickory, North Carolina, United States

Piedmont Retina Specialists

🇺🇸

Winston-Salem, North Carolina, United States

Cincinnati Eye Institute

🇺🇸

Blue Ash, Ohio, United States

Ohio State Eye and Ear Institute

🇺🇸

Columbus, Ohio, United States

Tulsa Retina Consultants

🇺🇸

Tulsa, Oklahoma, United States

Cascade Medical Research Institute LLC

🇺🇸

Springfield, Oregon, United States

Erie Retina Research

🇺🇸

Erie, Pennsylvania, United States

Sewickely Eye Group

🇺🇸

Sewickley, Pennsylvania, United States

Palmetto Retina Center

🇺🇸

West Columbia, South Carolina, United States

Charles Retina Institute

🇺🇸

Germantown, Tennessee, United States

Retina Research Institute of Texas

🇺🇸

Abilene, Texas, United States

Texas Retina Associates

🇺🇸

Dallas, Texas, United States

Austin Retina Associates

🇺🇸

Austin, Texas, United States

Austin Clinical Research LLC

🇺🇸

Austin, Texas, United States

Retina & Vitreous of Texas

🇺🇸

Bellaire, Texas, United States

Valley Retina Institute P.A.

🇺🇸

McAllen, Texas, United States

Medical Center Ophthalmology Associates

🇺🇸

San Antonio, Texas, United States

Retina Consultants of Texas - San Antonio

🇺🇸

San Antonio, Texas, United States

Brown Retina Institute

🇺🇸

San Antonio, Texas, United States

Retina Consultants of Texas

🇺🇸

The Woodlands, Texas, United States

Strategic Clinical Research Group, LLC

🇺🇸

Willow Park, Texas, United States

Retina Associates of Utah, PLLC;Clinical Research

🇺🇸

Salt Lake City, Utah, United States

Piedmont Eye Center

🇺🇸

Lynchburg, Virginia, United States

Wagner Kapoor Institute

🇺🇸

Norfolk, Virginia, United States

Retina Institute of Virginia

🇺🇸

Richmond, Virginia, United States

Spokane Eye Clinical Research

🇺🇸

Spokane, Washington, United States

Emanuelli Research and Development Center LLC

🇵🇷

Arecibo, Puerto Rico

© Copyright 2025. All Rights Reserved by MedPath