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Study of Ravulizumab in Immunoglobulin A Nephropathy (IgAN)

Phase 3
Recruiting
Conditions
Immunoglobulin A Nephropathy
IgAN
Interventions
Drug: Placebo
Registration Number
NCT06291376
Lead Sponsor
Alexion Pharmaceuticals, Inc.
Brief Summary

The primary objective of this study to evaluate efficacy of ravulizumab compared with placebo on proteinuria reduction and change in eGFR in adult participants with IgAN who are at risk of disease progression.

Detailed Description

The I CAN study will enroll approximately 510 eligible participants with IgAN who are high risk of disease progression. Participants will be on stable concomitant IgAN treatment(s) consistent with standard of care for patients with IgAN for at least 3 months prior to Screening. Approximately 450 participants will be randomized in a 1:1 allocation ratio to receive a weight-based IV infusion of either ravulizumab or placebo. An interim analysis may be conducted at Week 34 to evaluate change in proteinuria and the final analysis will be conducted at Week 106 to evaluate eGFR. In addition, approximately 60 participants with eGFR 20-29 mL/min/1.73m2 will be enrolled in an Advanced Kidney Disease (AdKD) Cohort After Week 106, all participants have the option to enter an Open-label Ravulizumab Access Period.

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
510
Inclusion Criteria
  • Documentation of IgAN diagnosis established on kidney biopsy obtained any time prior to or during the Screening Period for participants with eGFR ≥ 30 mL/min/1.73 m^2.
  • For participants in the AdKD cohorts, eGFR 20 to 29 mL/min/1.73 m2 a kidney biopsy is required within 6 months prior to Screening or during the Screening Period.
  • UPCR ≥ 0.75 g/g or UP ≥1 g/day calculated from the mean of two 24-hour urine during the Screening Period.
  • Estimated GFR ≥ 30 mL/min/1.73 m2 at Screening.
  • Stable and maximum allowed or tolerated RASI (ACEI and/or ARB) dose for ≥ 3 months prior to Screening with no planned change during Screening through Week 106.
  • Participants who are receiving SGLT2I, DEARA, MRA or ERA must be on a stable and maximum allowed or tolerated dose for ≥ 3 months prior to Screening with no planned change in dose through Week 106.
Exclusion Criteria
  • Diagnosis of rapid progressive glomerulonephritis as measured by eGFR loss ≥ 50% over a period of 3 months prior to Screening.
  • Secondary IgAN (eg, due to systemic lupus erythematosus (SLE), cirrhosis, or celiac disease; IgAV-N may be eligible).
  • Concomitant clinically significant renal disease other than IgAN.
  • Prior use of immunosuppressive treatment within 3 months of screening.
  • Uncontrolled diabetes mellitus with glycosylated hemoglobin (HbA1c) > 8.5%.
  • Henoch-Schonlein purpura (IgAV) requiring systemic immunosuppressive therapy within 12 months of Screening.
  • History of kidney transplant or planned kidney transplant during the Treatment Period.
  • Splenectomy or functional asplenia.
  • History of Neisseria meningitidis infection.
  • Active systemic bacterial, viral, or fungal infection within 14 days prior to randomization.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Ravulizumab IV q8wRavulizumabParticipants will receive a weight-based loading dose on Day 1 followed by weight-based maintenance dosing initiated on Day 15, and then administered every 8 weeks (q8w).
Placebo IV q8wPlaceboParticipants will receive a weight-based loading dose on Day 1 followed by weight-based maintenance dosing initiated on Day 15, and then administered q8w.
Primary Outcome Measures
NameTimeMethod
Change from Baseline in Proteinuria Based on 24-hour Urine Protein Creatinine Ratio (UPCR) at Week 34Baseline, Week 34

Evaluated at interim analysis only

Change from Baseline in Glomerular Filtration Rate (eGFR) at Week 106Baseline, Week 106

Evaluated at final analysis only

Secondary Outcome Measures
NameTimeMethod
Change from Baseline in Proteinuria Based on 24-hour Urine Protein Creatinine Ratio (UPCR) at Weeks 10, 26, 34, 50, and 106Baseline, Weeks 10, 26, 34, 50, and 106

Evaluated at interim and final analysis

Change From Baseline in eGFR at Weeks 34 and 50Baseline, Weeks 34 and 50

Evaluated at interim and final analysis

Change From Baseline in Albuminuria at Each Scheduled Visit Up to Week 106Baseline, at Each Scheduled Visit Up to Week 106

Evaluated at interim and final analysis

Reduction in 24-hour UPCR ≥ 50% From Baseline at Each Scheduled Visit Up to Week 106Baseline, at Each Scheduled Visit Up to Week 106

Evaluated at interim and final analysis

Number of Participants With Partial Remission at Each Scheduled Visit Up to Week 106Baseline, at Each Scheduled Visit Up to Week 106

Evaluated at interim and final analysis

Change from Baseline in Functional Assessment of Chronic Illness Therapy (FACIT)-Fatigue at Weeks 34, 50, and 106Baseline, Weeks 34, 50, and 106

Evaluated at interim and final analysis

Annualized eGFR Slope Over 50 WeeksBaseline, Over 50 Weeks

Evaluated at interim analysis only

Time to First Composite Kidney Event Up to Week 106Baseline Up to Week 106

Composite kidney event endpoint is defined as reaching at least 1 of the following: Sustained ≥ 30% decline in eGFR relative to baseline; or Sustained eGFR \< 15 milliliter (mL)/minute (min)/1.73 square meter (m\^2); or Maintenance dialysis; or Receipt of kidney transplant; or Death from kidney failure.

Evaluated at final analysis only

Time to Sustained ≥ 30% eGFR Decline Up to Week 106Baseline Up to Week 106

Evaluated at final analysis only

Time to Sustained eGFR Decline ≥ 40% Up to Week 106Baseline Up to Week 106

Evaluated at final analysis only

Use of Alternative IgAN Therapy Up to Week 106Baseline, Up to Week 106

Evaluated at final analysis only

Trial Locations

Locations (1)

Research Site

🇬🇧

Stevenage, United Kingdom

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