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NOGO-A in Multiple Sclerosis FTIH

Phase 1
Terminated
Conditions
Multiple Sclerosis
Interventions
Drug: Placebo
Registration Number
NCT01424423
Lead Sponsor
GlaxoSmithKline
Brief Summary

The drug being tested in this study is GSK1223249. The drug works by inhibiting a protein that prevents nerve growth.

The trial is expected to involve approximately 36 patients. The study objective is to investigate the tolerability, safety and the way the body handles GSK1223249 after a range of single doses in patients with Multiple Sclerosis (MS).

Detailed Description

This is a phase I study of GSK1223249. The study design is randomized, placebo-controlled, double-blind, sequential dose escalation, single dose administration. Approximately 36 patients with relapsing forms of Multiple Sclerosis (having had at least two relapses over the previous 24 months, OR at least one relapse within the last 12 months, OR having had at least one documented gadolinium-enhancing lesion on brain magnetic resonance imaging (MRI) within 12 months prior to Screening) will be enrolled.

Recruitment & Eligibility

Status
TERMINATED
Sex
All
Target Recruitment
3
Inclusion Criteria
  • Suitable as determined by the Principal Investigator, based on his/her overall evaluation. A patient with a clinical abnormality or laboratory parameters outside the reference range for the population being studied may be included only if the Investigator and the GSK Medical Monitor agree that the finding is unlikely to introduce additional risk factors and will not interfere with the study procedures.
  • Diagnosed with a relapsing form of MS defined as either
  • Relapsing Remitting MS according to revised McDonald Criteria [McDonald, 2001; Polman, 2005] plus any one of the following:

Occurrence of at least one relapse in the previous 12 months OR at least 2 relapses in the previous 24 months OR at least one documented Gd-enhancing lesion by magnetic resonance imaging (MRI) within 12 months prior to screening.

OR

-Secondary Progressive MS, plus any one of the following: Occurrence of at least one relapse in the previous 12 months OR at least 2 relapses in the previous 24 months OR at least one documented Gd-enhancing lesion by magnetic resonance imaging (MRI) within 12 months prior to screening.

  • Expanded Disability Status Scale (EDSS) score ≤5.5
  • Male or female between 18 and 55 years of age inclusive, at the time of signing the informed consent.
Exclusion Criteria
  • Abnormal baseline blood tests
  • Treatment with interferon-beta-1b (Betaferon), interferon-beta-1a (Rebif or Avonex), or glatiramer acetate (Copaxone) within 90 days of dosing.
  • Treatment with methylprednisolone or any other systemic steroids within 60 days of dosing.
  • Treatment within the past 12 months or currently with any of the following agents: cyclosporine, azathioprine, methotrexate, cladribine, natalizumab (Tysabri®) or other monoclonal antibodies, murine protein, T-cell vaccination, plasmapheresis, IVI gG, ,stem cell transplantation.
  • History of intolerance to acetominophen, ibuprofen, naproxen or any other non-steroidal anti-inflammatory agent which would preclude use of at least one of these during the study.
  • Previous history of anaphylaxis, severe allergic reaction, or hypersensitivity to albumin or a protein-based therapeutic, including natalizumab (Tysabri) or any other monoclonal antibody. History of hypersensitivity to any of the components of the formulation.
  • A positive pre-study Hepatitis B surface antigen or positive Hepatitis C antibody result.
  • Patients with evidence of dementia or psychiatric illness which, in the Investigator's opinion, is likely to prevent them from a full understanding of and/or compliance with the study requirements and procedures.

Study & Design

Study Type
INTERVENTIONAL
Study Design
SEQUENTIAL
Arm && Interventions
GroupInterventionDescription
Subjects receiving GSK1223249 in cohort 1GSK1223249Eligible subjects will receive intravenous infusion of GSK1223249 with a starting dose of 0.02 milligrams per kilograms, followed by 0.2, 2, 10 and 30 milligrams per kilograms, administered by a programmable syringe pump.
Subjects receiving placebo in cohort 1PlaceboEligible subjects will receive intravenous infusion of placebo, administered by a programmable syringe pump.
Subjects receiving placebo in cohort 2PlaceboEligible subjects will receive intravenous infusion of placebo, administered by a programmable syringe pump.
Subjects receiving placebo in cohort 3PlaceboEligible subjects will receive intravenous infusion of placebo, administered by a programmable syringe pump.
Subjects receiving GSK1223249 in cohort 4GSK1223249Eligible subjects will receive intravenous infusion of GSK1223249 with a dose of 10 milligrams per kilograms administered by a programmable syringe pump.
Subjects receiving placebo in cohort 4PlaceboEligible subjects will receive intravenous infusion of placebo, administered by a programmable syringe pump.
Subjects receiving GSK1223249 in cohort 5GSK1223249Eligible subjects will receive intravenous infusion of GSK1223249 with a dose of 30 milligrams per kilograms administered by a programmable syringe pump.
Subjects receiving placebo in cohort 5PlaceboEligible subjects will receive intravenous infusion of placebo, administered by a programmable syringe pump.
Subjects receiving GSK1223249 in cohort 2GSK1223249Eligible subjects will receive intravenous infusion of GSK1223249 with a dose of 0.2 milligrams per kilograms administered by a programmable syringe pump.
Subjects receiving GSK1223249 in cohort 3GSK1223249Eligible subjects will receive intravenous infusion of GSK1223249 with a dose of 2 milligrams per kilograms administered by a programmable syringe pump.
Primary Outcome Measures
NameTimeMethod
The preliminary safety and tolerability of single doses of GSK1223249screening, baseline (pre-dose) and up to 84 days post dose

changes in Vital signs, Electocardiogram, safety laboratory samples, adverse event (AE), neurological examination and MS relapses

Secondary Outcome Measures
NameTimeMethod
Single dose pharmacokinetics.screening, baseline (pre-dose) and up to 84 days post dose

(AUC(0-∞)

Trial Locations

Locations (1)

GSK Investigational Site

🇦🇺

Heidelberg, Victoria, Australia

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