MedPath

Tucatinib Plus Trastuzumab and Oxaliplatin-based Chemotherapy or Pembrolizumab-containing Combinations for HER2+ Gastrointestinal Cancers

Phase 2
Active, not recruiting
Conditions
GEJ Adenocarcinoma
Cholangiocarcinoma
Gallbladder Carcinoma
Colorectal Carcinoma
Esophageal Adenocarcinoma
Gastric Adenocarcinoma
Interventions
Registration Number
NCT04430738
Lead Sponsor
Seagen, a wholly owned subsidiary of Pfizer
Brief Summary

This trial studies tucatinib to find out if it is safe when given with trastuzumab and other anti-cancer drugs (pembrolizumab, FOLFOX, and CAPOX). It will look at what side effects happen when participants take this combination of drugs. A side effect is anything the drug does other than treating cancer. It will also look at whether tucatinib works with these drugs to treat certain types of cancer.

The participants in this trial have HER2-positive (HER2+) cancer in their gut, stomach, intestines, or gallbladder (gastrointestinal cancer).

Detailed Description

Not available

Recruitment & Eligibility

Status
ACTIVE_NOT_RECRUITING
Sex
All
Target Recruitment
41
Inclusion Criteria
  • Participants must have an unresectable or metastatic solid malignancy that is histologically or cytologically confirmed to be one of the tumor types listed below:

    • Cohorts 1A, 1B, 1C, and 1D

      • CRC
      • Gastric adenocarcinoma
      • GEJ adenocarcinoma
      • Esophageal adenocarcinoma
      • Cholangiocarcinoma
      • Gallbladder carcinoma
    • Cohorts 1E, 1F, 1G, and 2A

      • Gastric adenocarcinoma
      • GEJ adenocarcinoma
      • Esophageal adenocarcinoma
    • Cohort 2B

      • CRC
  • Participants must be candidates to receive an oxaliplatin-based regimen as part of their standard-of-care treatment for all cohorts, except Cohort 1G.

  • HER2+ disease, as determined by historic or local laboratory testing

  • Phase 1b cohorts: measurable or non-measurable disease according to RECIST v1.1 as determined by the investigator

  • Phase 2 cohorts: measurable disease according to RECIST v1.1 as determined by the investigator

  • Eastern Cooperative Oncology Group Performance Status score of 0 or 1.

Exclusion Criteria
  • History of known hypersensitivity to planned study treatment
  • Known to be positive for Hepatitis B or C
  • For Cohorts 2A and 2B: prior anti-HER2 therapies
  • For Cohorts 1E, 1F, 1G, 2A: Prior therapy with an anti-PD-1, anti-PD-L1, or anti PD L2 agent or with an agent directed to another stimulatory or co-inhibitory T-cell receptor (eg, CTLA-4, OX 40, CD137), and was discontinued from that treatment due to a Grade 3 or higher immune-related adverse event (irAE)

There are additional inclusion criteria. The study center will determine if criteria for participations are met.

Study & Design

Study Type
INTERVENTIONAL
Study Design
SEQUENTIAL
Arm && Interventions
GroupInterventionDescription
Cohort 1BtrastuzumabTucatinib + trastuzumab + FOLFOX given in 14-day cycles
Cohort 1AtucatinibTucatinib + trastuzumab + FOLFOX given in 14-day cycles
Cohort 1AoxaliplatinTucatinib + trastuzumab + FOLFOX given in 14-day cycles
Cohort 1AfluorouracilTucatinib + trastuzumab + FOLFOX given in 14-day cycles
Cohort 1BtucatinibTucatinib + trastuzumab + FOLFOX given in 14-day cycles
Cohort 1CtrastuzumabTucatinib + trastuzumab + CAPOX given in 21-day cycles
Cohort 1DtucatinibTucatinib + trastuzumab + FOLFOX. Tucatinib and FOLFOX given in 14-day cycles and trastuzumab given every 21 days
Cohort 1AtrastuzumabTucatinib + trastuzumab + FOLFOX given in 14-day cycles
Cohort 1CtucatinibTucatinib + trastuzumab + CAPOX given in 21-day cycles
Cohort 1DoxaliplatinTucatinib + trastuzumab + FOLFOX. Tucatinib and FOLFOX given in 14-day cycles and trastuzumab given every 21 days
Cohort 1EfluorouracilTucatinib + trastuzumab + pembrolizumab + FOLFOX. Tucatinib and FOLFOX given in 14-day cycles, trastuzumab given in 21-day cycles, and pembrolizumab given in 42-day cycles
Cohort 2AcapecitabineTucatinib + trastuzumab + pembrolizumab + (FOLFOX or CAPOX). Either (1) tucatinib and FOLFOX given in 14-day cycles or (2) tucatinib and CAPOX given in 21-day cycles. Trastuzumab given in 21-day cycles and pembrolizumab given in 42-day cycles.
Cohort 1FpembrolizumabTucatinib + trastuzumab + pembrolizumab + CAPOX. Tucatinib, trastuzumab, and CAPOX given in 21-day cycles and pembrolizumab given in 42-day cycles.
Cohort 1FtucatinibTucatinib + trastuzumab + pembrolizumab + CAPOX. Tucatinib, trastuzumab, and CAPOX given in 21-day cycles and pembrolizumab given in 42-day cycles.
Cohort 2AleucovorinTucatinib + trastuzumab + pembrolizumab + (FOLFOX or CAPOX). Either (1) tucatinib and FOLFOX given in 14-day cycles or (2) tucatinib and CAPOX given in 21-day cycles. Trastuzumab given in 21-day cycles and pembrolizumab given in 42-day cycles.
Cohort 2AfluorouracilTucatinib + trastuzumab + pembrolizumab + (FOLFOX or CAPOX). Either (1) tucatinib and FOLFOX given in 14-day cycles or (2) tucatinib and CAPOX given in 21-day cycles. Trastuzumab given in 21-day cycles and pembrolizumab given in 42-day cycles.
Cohort 1GpembrolizumabTucatinib + trastuzumab + pembrolizumab. Tucatinib and trastuzumab given in 21-day cycles and pembrolizumab given in 42-day cycles.
Cohort 2AtucatinibTucatinib + trastuzumab + pembrolizumab + (FOLFOX or CAPOX). Either (1) tucatinib and FOLFOX given in 14-day cycles or (2) tucatinib and CAPOX given in 21-day cycles. Trastuzumab given in 21-day cycles and pembrolizumab given in 42-day cycles.
Cohort 2AoxaliplatinTucatinib + trastuzumab + pembrolizumab + (FOLFOX or CAPOX). Either (1) tucatinib and FOLFOX given in 14-day cycles or (2) tucatinib and CAPOX given in 21-day cycles. Trastuzumab given in 21-day cycles and pembrolizumab given in 42-day cycles.
Cohort 2BoxaliplatinTucatinib + trastuzumab + FOLFOX given in 14-day cycles.
Cohort 1DfluorouracilTucatinib + trastuzumab + FOLFOX. Tucatinib and FOLFOX given in 14-day cycles and trastuzumab given every 21 days
Cohort 1AleucovorinTucatinib + trastuzumab + FOLFOX given in 14-day cycles
Cohort 1BoxaliplatinTucatinib + trastuzumab + FOLFOX given in 14-day cycles
Cohort 1BfluorouracilTucatinib + trastuzumab + FOLFOX given in 14-day cycles
Cohort 1BleucovorinTucatinib + trastuzumab + FOLFOX given in 14-day cycles
Cohort 1CoxaliplatinTucatinib + trastuzumab + CAPOX given in 21-day cycles
Cohort 1CcapecitabineTucatinib + trastuzumab + CAPOX given in 21-day cycles
Cohort 1DtrastuzumabTucatinib + trastuzumab + FOLFOX. Tucatinib and FOLFOX given in 14-day cycles and trastuzumab given every 21 days
Cohort 1DleucovorinTucatinib + trastuzumab + FOLFOX. Tucatinib and FOLFOX given in 14-day cycles and trastuzumab given every 21 days
Cohort 1EleucovorinTucatinib + trastuzumab + pembrolizumab + FOLFOX. Tucatinib and FOLFOX given in 14-day cycles, trastuzumab given in 21-day cycles, and pembrolizumab given in 42-day cycles
Cohort 1EtucatinibTucatinib + trastuzumab + pembrolizumab + FOLFOX. Tucatinib and FOLFOX given in 14-day cycles, trastuzumab given in 21-day cycles, and pembrolizumab given in 42-day cycles
Cohort 1EtrastuzumabTucatinib + trastuzumab + pembrolizumab + FOLFOX. Tucatinib and FOLFOX given in 14-day cycles, trastuzumab given in 21-day cycles, and pembrolizumab given in 42-day cycles
Cohort 1EoxaliplatinTucatinib + trastuzumab + pembrolizumab + FOLFOX. Tucatinib and FOLFOX given in 14-day cycles, trastuzumab given in 21-day cycles, and pembrolizumab given in 42-day cycles
Cohort 1FtrastuzumabTucatinib + trastuzumab + pembrolizumab + CAPOX. Tucatinib, trastuzumab, and CAPOX given in 21-day cycles and pembrolizumab given in 42-day cycles.
Cohort 1EpembrolizumabTucatinib + trastuzumab + pembrolizumab + FOLFOX. Tucatinib and FOLFOX given in 14-day cycles, trastuzumab given in 21-day cycles, and pembrolizumab given in 42-day cycles
Cohort 1FoxaliplatinTucatinib + trastuzumab + pembrolizumab + CAPOX. Tucatinib, trastuzumab, and CAPOX given in 21-day cycles and pembrolizumab given in 42-day cycles.
Cohort 1FcapecitabineTucatinib + trastuzumab + pembrolizumab + CAPOX. Tucatinib, trastuzumab, and CAPOX given in 21-day cycles and pembrolizumab given in 42-day cycles.
Cohort 1GtucatinibTucatinib + trastuzumab + pembrolizumab. Tucatinib and trastuzumab given in 21-day cycles and pembrolizumab given in 42-day cycles.
Cohort 1GtrastuzumabTucatinib + trastuzumab + pembrolizumab. Tucatinib and trastuzumab given in 21-day cycles and pembrolizumab given in 42-day cycles.
Cohort 2AtrastuzumabTucatinib + trastuzumab + pembrolizumab + (FOLFOX or CAPOX). Either (1) tucatinib and FOLFOX given in 14-day cycles or (2) tucatinib and CAPOX given in 21-day cycles. Trastuzumab given in 21-day cycles and pembrolizumab given in 42-day cycles.
Cohort 2ApembrolizumabTucatinib + trastuzumab + pembrolizumab + (FOLFOX or CAPOX). Either (1) tucatinib and FOLFOX given in 14-day cycles or (2) tucatinib and CAPOX given in 21-day cycles. Trastuzumab given in 21-day cycles and pembrolizumab given in 42-day cycles.
Cohort 2BtucatinibTucatinib + trastuzumab + FOLFOX given in 14-day cycles.
Cohort 2BtrastuzumabTucatinib + trastuzumab + FOLFOX given in 14-day cycles.
Cohort 2BfluorouracilTucatinib + trastuzumab + FOLFOX given in 14-day cycles.
Cohort 2BleucovorinTucatinib + trastuzumab + FOLFOX given in 14-day cycles.
Primary Outcome Measures
NameTimeMethod
Incidence of laboratory abnormalities (Cohorts 1C, 1D, 1E, 1F, 1G, 2A, and 2B)Up to approximately 12 months
Incidence of DLTs (Cohorts 1C, 1D, 1E, 1F, and 1G)Up to approximately 12 months
Incidence of dose alterations (Cohort 1D)Up to approximately 12 months
Incidence of renal dose-limiting toxicities (DLTs) (Cohorts 1A and 1B)Up to one month; 2 cycles after receiving all study treatment (each cycle is 14 days)
Incidence of adverse events (AEs) (Cohorts 1C, 1D, 1E, 1F, 1G, 2A, and 2B)Up to approximately 12 months

An AE is defined as any untoward medical occurrence in a clinical investigational participant administered a medicinal product and which does not necessarily have a causal relationship with this treatment.

Secondary Outcome Measures
NameTimeMethod
PK parameter of oxaliplatin - AUClast (Cohorts 1A and 1B)Up to 15 days; through Cycle 2, Day 1 (each cycle is 14 days)

To be summarized using descriptive statistics

Duration of response (DOR) according to RECIST v1.1 per INV (Cohorts 1C, 1E, 1F, 1G, and 2A)Up to approximately 2.5 years

DOR is defined as the time from first documentation of objective response of confirmed CR or confirmed PR to the first documentation of disease progression or death from any cause, whichever occurs first.

Overall survival (OS) (Cohort 1C, 1E, 1F, 1G, and 2A)Up to approximately 2.5 years

OS is defined as the time from treatment initiation to death due to any cause

Objective response rate (ORR) (Cohorts 1C, 1E, 1F, and 1G)Up to approximately 2.5 years

ORR is defined as the proportion of subjects with confirmed CR or PR, according to RECIST v1.1.

Incidence of AEs (Cohorts 1A and 1B)Up to approximately 12 months

An AE is defined as any untoward medical occurrence in a clinical investigational participant administered a medicinal product and which does not necessarily have a causal relationship with this treatment.

Incidence of laboratory abnormalities (Cohorts 1A and 1B)Up to approximately 12 months
Change in glomerular filtration rate (GFR) from baseline through 2 cycles of combination therapy (Cohorts 1A and 1B)Up to approximately 6 weeks

To be summarized using descriptive statistics

PK parameter of tucatinib - Tmax (Cohorts 1A and 1B)Up to approximately 2.5 months; through predose of Cycle 2, Day 1 (each cycle is 14 days)

To be summarized using descriptive statistics

PK parameter of oxaliplatin - Cmax (Cohorts 1A and 1B)Up to 15 days; through Cycle 2, Day 1 (each cycle is 14 days)

To be summarized using descriptive statistics

Pharmacokinetic (PK) parameter of tucatinib - AUClast (Cohorts 1A and 1B)Up to approximately 2.5 months; through predose of Cycle 2, Day 1 (each cycle is 14 days)

To be summarized using descriptive statistics

PK parameter of tucatinib - Cmax (Cohorts 1A and 1B)Up to approximately 2.5 months; through predose of Cycle 2, Day 1 (each cycle is 14 days)

To be summarized using descriptive statistics

PK parameter of tucatinib - Ctrough (Cohorts 1A, 1B, 1C, 1E, 1F, and 1G)Up to approximately 2.5 months; through predose of Cycle 6, Day 1

To be summarized using descriptive statistics

PK parameter of oxaliplatin - Tmax (Cohorts 1A and 1B)Up to 15 days; through Cycle 2, Day 1 (each cycle is 14 days)

To be summarized using descriptive statistics

Confirmed objective response rate (cORR) according to Response Evaluation Criteria in Solid Tumors (RECIST) v1.1 per investigator assessment (INV) (Cohort 2A)Up to approximately 2.5 years

cORR is defined as the proportion of participants with confirmed complete response (CR) or partial response (PR)

Progression-free survival (PFS) according to RECIST v1.1 per INV (Cohorts 1C, 1E, 1F, 1G, and 2A)Up to approximately 2.5 years

PFS is defined as the time from the date of treatment initiation to the date of disease progression or death from any cause, which occurs first.

Trial Locations

Locations (28)

Mayo Clinic Hospital

🇺🇸

Phoenix, Arizona, United States

Mayo Clinic

🇺🇸

Scottsdale, Arizona, United States

University of Colorado Denver CTO(CTRC)

🇺🇸

Aurora, Colorado, United States

University of Colorado Hospital - Anschutz Cancer Pavilion (ACP)

🇺🇸

Aurora, Colorado, United States

University of Colorado Hospital - Anschutz Inpatient Pavilion (AIP)

🇺🇸

Aurora, Colorado, United States

University of Colorado Hospital - Anschutz Outpatient Pavilion (AOP)

🇺🇸

Aurora, Colorado, United States

PCM Trials

🇺🇸

Denver, Colorado, United States

Sibley Memorial Hospital

🇺🇸

Washington, District of Columbia, United States

Siteman Cancer Center - West County

🇺🇸

Creve Coeur, Missouri, United States

Siteman Cancer Center - North County

🇺🇸

Florissant, Missouri, United States

Siteman Cancer Center

🇺🇸

Saint Louis, Missouri, United States

Barnes-Jewish Hospital

🇺🇸

Saint Louis, Missouri, United States

Washington University School of Medicine

🇺🇸

Saint Louis, Missouri, United States

Siteman Cancer Center - South County

🇺🇸

Saint Louis, Missouri, United States

Siteman Cancer Center - St Peters

🇺🇸

Saint Peters, Missouri, United States

University of New Mexico Comprehensive Cancer Center

🇺🇸

Albuquerque, New Mexico, United States

Duke University Medical Center, Duke Cancer Center

🇺🇸

Durham, North Carolina, United States

Cleveland Clinic Taussig Cancer Center Investigational Pharmacy

🇺🇸

Cleveland, Ohio, United States

Cleveland Clinic

🇺🇸

Cleveland, Ohio, United States

Fred Hutchinson Cancer Center

🇺🇸

Seattle, Washington, United States

University of Washington Medical Center

🇺🇸

Seattle, Washington, United States

Aichi Cancer Center Hospital

🇯🇵

Nagoya, Aichi, Japan

St. Marianna University Hospital

🇯🇵

Kawasaki, Kanagawa, Japan

Cancer Institute Hospital of Japanese Foundation for Cancer Research.

🇯🇵

Koto-ku, Tokyo, Japan

Duke University Medical Center

🇺🇸

Durham, North Carolina, United States

National Cancer Center Hospital East

🇯🇵

Kashiwa-shi, Chiba, Japan

Osaka International Cancer Institute

🇯🇵

Osaka-shi, Osaka, Japan

National Cancer Center Hospital

🇯🇵

Chuo-ku, Tokyo, Japan

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