MedPath

Randomized Trial in Adult de Novo Ph Positive ALL With Chemotherapy, Imatinib or Ponatinib, Blinatumomab and SCT

Phase 2
Recruiting
Conditions
Philadelphia Chromosome Positive Acute Lymphoblastic Leukemia
Interventions
Other: Indication for stem cell transplantation
Registration Number
NCT06061094
Lead Sponsor
Goethe University
Brief Summary

The current Standard of Care (SoC) in younger patients with Ph+ ALL is Imatinib in combination with low-dose chemotherapy, change of TKI in case of persistent MRD above 10-3 after consolidation I and indication for stem cell transplantation.

The EVOLVE trial aims to answer three questions challenging the current SoC:

Use of Ponatinib compared to Imatinib both in combination with low-dose chemotherapy and consolidation I (randomization I).

In MRD good responders: Omit end of therapy in primary care and indication for SCT but continue therapy with TKI, chemotherapy and Blinatumomab as additional antileukemic compound (randomization II).

In MRD poor responders: Omit indication for TKI change but give instead Blinatumomab followed by end of therapy in primary care and indication for SCT (non-randomized).

Detailed Description

Not available

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
220
Inclusion Criteria
  • Male or female patients >= 18 years, <=65 years
  • Philadelphia chromosome or BCR-ABL1 positive ALL
  • Not previously treated except with corticosteroids ≤ 7 days, standard GMALL prephase with dexamethasone and cyclophosphamide including intrathecal therapy, hydroxyurea, a single dose vincristine or other cytostatic drugs and start of standard induction for Ph-positive ALL (1 dose vincristine, 1 dose of Rituximab, 2 doses dexamethasone and up to 5 days Imatinib)
  • ECOG performance status ≤2
  • Signed written inform consent
  • Molecular evaluation for BCR-ABL1 performed
  • Negative pregnancy test in women of childbearing potential
  • Woman of childbearing potential willing to use 2 highly effective methods of contraception while receiving study treatment and for an additional 3 months after the last dose of study treatment (Pearl-Index <1%). Male who has a female partner of childbearing potential willing to use 2 highly effective forms of contraception while receiving study treatment and for at least an additional 3 months after the last dose of study treatment (Pearl-Index <1%).
  • Normal serum levels > LLN (lower limit of normal) of potassium and magnesium, or corrected to within normal limits with supplements, prior to the first dose of study medication
  • Serum lipase ≤ 1.5 x ULN. For serum lipase > ULN - ≤ 1.5 x ULN, value must be considered not clinically significant and not associated with risk factors for acute pancreatitis
  • Normal QTcF interval ≤450 ms for males and ≤470 ms for females
  • Signed and dated written informed consent is available
  • Participation in the registry of the German Multicenter Study Group for Adult ALL (GMALL)
Exclusion Criteria
  • History of malignancy other than ALL diagnosed within 5 years (yrs) prior to start of protocol-specified therapy with defined exceptions
  • Contraindications against the use of Imatinib, Ponatinib, chemotherapy or Blinatumomab
  • Patient previously treated with tyrosine kinase inhibitors
  • Nursing women
  • Known impaired cardiac function, including any of the following: as detailed in protocol
  • Symptomatic peripheral vascular disease
  • Any history of ischemic stroke or transient ischemic attacks (TIAs)
  • Uncontrolled hypertriglyceridaemia
  • History or presence of clinically relevant CNS pathology as detailed in protocol
  • History or active relevant autoimmune disease
  • Known hypersensitivity to immunoglobulins or to any other component of the study drug formulation
  • Known diagnosis of human immunodeficiency virus (HIV) infection (HIV testing is not mandatory) or active infection with Hepatitis B or C
  • History of pancreatitis within 6 months previous to start of treatment within the trial
  • Treatment with any other investigational agent or participating in another trial within 30 days prior to entering this study
  • Inadequate hepatic functions defined as ASAT or ALAT > 2,5 times the institutional upper limit of normal or > 5 times ULN if considered due to leukemia
  • Total bilirubin > 1.5-fold the institutional upper limit unless considered to be due to organ involvement by the leukemia or to M. Gilbert / M. Meulengracht
  • Concurrent severe diseases which exclude the administration of therapy e.g. severe, uncontrolled acute or chronic infections
  • Inability to understand and/or unwillingness to sign a written informed consent

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
D: Molecular CR: continuation with Imatinib/Ponatinib (per Rando I), chemotherapy and BlinatumomabImatinibMolecular CR: No end of therapy with indication for SCT but and continuation with Imatinib/Ponatinib (per Randomization I), chemotherapy and Blinatumomab (Experimental Arm of Randomization II)
C: Molecular CR: End of therapy with indication for SCTIndication for stem cell transplantationMolecular CR: End of therapy with indication for SCT (Standard Arm of Randomization II)
A: Imatinib + low dose chemotherapyImatinibImatinib 600mg QD + low dose chemotherapy induction and consolidation I (Standard Arm of Randomization I)
E: Mol Fail / Mol NE: Continuation with Imatinib/Ponatinib (per Rando I) and addition of BlinaIndication for stem cell transplantationMolecular Failure / Molecular Not Evaluable: Continuation with Imatinib/Ponatinib (per Randomization I) and addition of Blinatumomab (Experimental Arm)
B: Ponatinib + low dose chemotherapyPonatinibPonatinib 45mg QD (reduction to 30mg QD after Induction) + low dose chemotherapy induction and consolidation I (Experimental Arm of Randomization I)
D: Molecular CR: continuation with Imatinib/Ponatinib (per Rando I), chemotherapy and BlinatumomabPonatinibMolecular CR: No end of therapy with indication for SCT but and continuation with Imatinib/Ponatinib (per Randomization I), chemotherapy and Blinatumomab (Experimental Arm of Randomization II)
D: Molecular CR: continuation with Imatinib/Ponatinib (per Rando I), chemotherapy and BlinatumomabBlinatumomabMolecular CR: No end of therapy with indication for SCT but and continuation with Imatinib/Ponatinib (per Randomization I), chemotherapy and Blinatumomab (Experimental Arm of Randomization II)
E: Mol Fail / Mol NE: Continuation with Imatinib/Ponatinib (per Rando I) and addition of BlinaPonatinibMolecular Failure / Molecular Not Evaluable: Continuation with Imatinib/Ponatinib (per Randomization I) and addition of Blinatumomab (Experimental Arm)
E: Mol Fail / Mol NE: Continuation with Imatinib/Ponatinib (per Rando I) and addition of BlinaImatinibMolecular Failure / Molecular Not Evaluable: Continuation with Imatinib/Ponatinib (per Randomization I) and addition of Blinatumomab (Experimental Arm)
E: Mol Fail / Mol NE: Continuation with Imatinib/Ponatinib (per Rando I) and addition of BlinaBlinatumomabMolecular Failure / Molecular Not Evaluable: Continuation with Imatinib/Ponatinib (per Randomization I) and addition of Blinatumomab (Experimental Arm)
Primary Outcome Measures
NameTimeMethod
OS in MolCR patients treated with TKI-Chemo-Blina versus (vs) EOT with indication for SCT (Standard of Care)up to 4 years from randomization I

Probability of overall survival up to 4 years from randomization I in patients with mo-lecular remission after consolidation 1 comparing a combination treatment of TKI, Blina-tumomab and chemotherapy versus EOT with indication for SCT

Secondary Outcome Measures
NameTimeMethod
Rate of molecular complete remission at week 11 after consolidationweek 11 after consolidation

Rate of molecular complete remission at week 11 after consolidation with chemotherapy in combination with Ponatinb versus Imatinib

Trial Locations

Locations (85)

Evangelische Kliniken Bonn

🇩🇪

Bonn, Germany

Klinikum Bayreuth

🇩🇪

Bayreuth, Germany

Vivantes Klinikum am Urban

🇩🇪

Berlin, Germany

Medizinische Hochschule Hannover

🇩🇪

Hannover, Germany

Helios Klinikum Bad Saarow

🇩🇪

Bad Saarow, Germany

Uniklinik RWTH Aachen

🇩🇪

Aachen, Germany

Klinikum Aschaffenburg

🇩🇪

Aschaffenburg, Germany

Klinikum Augsburg

🇩🇪

Augsburg, Germany

Charité Universitätsmedizin Berlin

🇩🇪

Berlin, Germany

Vivantes Klinikum Neukölln

🇩🇪

Berlin, Germany

Helios Klinikum Berlin-Buch

🇩🇪

Berlin, Germany

Charite Berlin Virchow Klinikum

🇩🇪

Berlin, Germany

Evangelisches Krankenhaus Bielefeld

🇩🇪

Bielefeld, Germany

UK Knappschaftskrankenhaus Bochum

🇩🇪

Bochum, Germany

Universitätsklinikum Bonn

🇩🇪

Bonn, Germany

Städtisches Klinikum Braunschweig

🇩🇪

Braunschweig, Germany

Klinikum Bremen-Mitte

🇩🇪

Bremen, Germany

Klinikum Chemnitz

🇩🇪

Chemnitz, Germany

Klinikum Darmstadt

🇩🇪

Darmstadt, Germany

Städtisches Klinikum Dessau

🇩🇪

Dessau-Roßlau, Germany

Klinikum Dortmund

🇩🇪

Dortmund, Germany

St. Johannes Hospital Dortmund

🇩🇪

Dortmund, Germany

Universitätsklinikum Carl Gustav Carus Dresden

🇩🇪

Dresden, Germany

Helios Klinikum Duisburg

🇩🇪

Duisburg, Germany

Universitätsklinikum Düsseldorf

🇩🇪

Düsseldorf, Germany

Marien Hospital Düsseldorf

🇩🇪

Düsseldorf, Germany

Universitätsklinikum Erlangen

🇩🇪

Erlangen, Germany

St.-Antonius-Hospital

🇩🇪

Eschweiler, Germany

Universitätsklinikum Essen

🇩🇪

Essen, Germany

Evangelisches Krankenhaus Essen-Werden

🇩🇪

Essen, Germany

Department of Medicine, Hematology and Oncology, Goethe University Hospital Frankfurt

🇩🇪

Frankfurt, Germany

Universitätsklinikum Freiburg

🇩🇪

Freiburg, Germany

Niels-Stensen-Kliniken Georgsmarienhütte

🇩🇪

Georgsmarienhütte, Germany

Wilhelm-Anton-Hospital

🇩🇪

Goch, Germany

Universitätsmedizin Greifswald

🇩🇪

Greifswald, Germany

Universitätsmedizin Göttingen

🇩🇪

Göttingen, Germany

Klinikum Gütersloh

🇩🇪

Gütersloh, Germany

Katholisches Krankenhaus Hagen

🇩🇪

Hagen, Germany

Universitätsklinikum Halle

🇩🇪

Halle, Germany

Asklepios Klinik St. Georg Hamburg

🇩🇪

Hamburg, Germany

Universitätsklinikum Hamburg-Eppendorf

🇩🇪

Hamburg, Germany

Universitätsklinikum Heidelberg

🇩🇪

Heidelberg, Germany

Marien Hospital Herne

🇩🇪

Herne, Germany

Universitätsklinikum des Saarlandes

🇩🇪

Homburg, Germany

Klinikum Idar-Oberstein

🇩🇪

Idar-Oberstein, Germany

Universitätsklinikum Jena

🇩🇪

Jena, Germany

Städtisches Klinikum Karlsruhe

🇩🇪

Karlsruhe, Germany

St. Vincentius-Kliniken Karlsruhe

🇩🇪

Karlsruhe, Germany

Klinikum Kassel

🇩🇪

Kassel, Germany

Universitätsklinikum Kiel

🇩🇪

Kiel, Germany

Gemeinschaftsklinikum Mittelrhein

🇩🇪

Koblenz, Germany

Universitätsklinikum Köln

🇩🇪

Köln, Germany

Universitätsklinikum Leipzig

🇩🇪

Leipzig, Germany

Märkische Kliniken Lüdenscheid

🇩🇪

Lüdenscheid, Germany

Universitätsklinikum Magdeburg

🇩🇪

Magdeburg, Germany

UNIVERSITÄTSMEDIZIN der Johannes Gutenberg-Universität Mainz

🇩🇪

Mainz, Germany

Universitätsklinikum Mannheim

🇩🇪

Mannheim, Germany

Philipps-Universität Marburg

🇩🇪

Marburg, Germany

Kliniken Maria Hilf Möchengladbach

🇩🇪

Möchengladbach, Germany

LMU Klinikum München

🇩🇪

München, Germany

Klinikum Rechts der Isar TU München

🇩🇪

München, Germany

Universitätsklinikum Münster

🇩🇪

Münster, Germany

Klinikum Nürnberg

🇩🇪

Nürnberg, Germany

Ortenau Klinikum Offenburg

🇩🇪

Offenburg, Germany

Klinikum Oldenburg

🇩🇪

Oldenburg, Germany

Brüderkrankenhaus St. Josef Paderborn

🇩🇪

Paderborn, Germany

Klinikum Passau

🇩🇪

Passau, Germany

Klinikum Ernst von Bergmann

🇩🇪

Potsdam, Germany

Krankenhaus Barmherzige Brüder Regensburg

🇩🇪

Regensburg, Germany

Universitätsklinikum Regensburg

🇩🇪

Regensburg, Germany

Universitätsklinikum Rostock

🇩🇪

Rostock, Germany

Agaplesion Diakonieklinikum Rotenburg

🇩🇪

Rotenburg/Wümme, Germany

Diakonie-Krankenhaus Schwäbisch-Hall

🇩🇪

Schwäbisch-Hall, Germany

Katharinenhospital Stuttgart

🇩🇪

Stuttgart, Germany

Diakonissenkrankenhaus Stuttgart

🇩🇪

Stuttgart, Germany

Robert-Bosch-Krankenhaus Stuttgart

🇩🇪

Stuttgart, Germany

Klinikum Traunstein

🇩🇪

Traunstein, Germany

Mutterhaus der Borromäerinnen Trier

🇩🇪

Trier, Germany

Krankenhaus d. Barmherzigen Brüder

🇩🇪

Trier, Germany

Universitätsklinikum Tübingen

🇩🇪

Tübingen, Germany

Universitätsklinikum Ulm

🇩🇪

Ulm, Germany

Klinikum Schwarzwald-Baar

🇩🇪

Villingen-Schwenningen, Germany

Helios Klinikum Wuppertal

🇩🇪

Wuppertal, Germany

Universitätsklinikum Würzburg

🇩🇪

Würzburg, Germany

Heinrich-Braun Klinikum

🇩🇪

Zwickau, Germany

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