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Study to Assess Long-term Effectiveness of Zomacton® and Treatment Adherence in Patients With Growth Hormone Deficiency or Ullrich-Turner Syndrome

Terminated
Conditions
Growth Disorders
Interventions
Registration Number
NCT03274973
Lead Sponsor
Ferring Pharmaceuticals
Brief Summary

Assessment of long-term effectiveness of ZOMACTON in treatment of Growth Hormone Deficiency or growth retardation due to Ullrich-Turner Syndrome and assessment of compliance and adherence, optionally with the aid of an electronic app or patient diary.

Detailed Description

Not available

Recruitment & Eligibility

Status
TERMINATED
Sex
All
Target Recruitment
4
Inclusion Criteria
  • Pediatric patients (< 18 years) with growth hormone deficiency or growth retardation due to Ullrich-Turner-Syndrome
  • Patients already receiving or who have been prescribed Zomacton® de novo according to its German label; the decision to prescribe Zomacton® was made independently from participation and prior to enrollment in this study.
  • Patient and their parents (or legal representatives) who are willing and able to provide signed informed consent for use of their personal data.
Exclusion Criteria
  • Participation in an interventional clinical study within the last 30 days prior to baseline visit or during the follow-up period

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Arm && Interventions
GroupInterventionDescription
ZomactonZomacton-
Primary Outcome Measures
NameTimeMethod
Linear growth (change in height)Over the first 12 months (month 0, 3, 6, 9 and 12)

Change in height defined as the change of the standard deviation score of body height vs. baseline

Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (1)

Klinik fuer Allgemeine Paediatrie der Christian-Albrechts-Universitaet zu Kiel (there might be other sites in this country)

🇩🇪

Kiel, Germany

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