Buphenyl Therapy for Byler's Disease
- Conditions
- Byler Disease
- Registration Number
- NCT01784718
- Lead Sponsor
- University of Pittsburgh
- Brief Summary
This is a single patient compassionate use protocol to determine whether Buphenyl (4-phenylbutyrate) will improve the poor bile flow associated with Byler Disease.
- Detailed Description
Not available
Recruitment & Eligibility
- Status
- NO_LONGER_AVAILABLE
- Sex
- All
- Target Recruitment
- Not specified
Inclusion Criteria
- Byler Disease
- Cholestasis unresponsive to pharmacologic therapy
Exclusion Criteria
- Allergy/Hypersensitivity to Buphenyl
Study & Design
- Study Type
- EXPANDED_ACCESS
- Study Design
- Not specified
- Primary Outcome Measures
Name Time Method
- Secondary Outcome Measures
Name Time Method