MedPath

Combination Chemotherapy in Treating Patients With Newly Diagnosed Metastatic Ewing's Sarcoma or Primitive Neuroectodermal Tumor

Phase 2
Completed
Conditions
Neutropenia
Sarcoma
Interventions
Biological: filgrastim
Procedure: conventional surgery
Radiation: low-LET cobalt-60 gamma ray therapy
Radiation: low-LET electron therapy
Radiation: low-LET photon therapy
Registration Number
NCT00002643
Lead Sponsor
National Cancer Institute (NCI)
Brief Summary

Phase II trial to study the effectiveness of combination chemotherapy in treating patients with newly diagnosed metastatic Ewing's sarcoma or primitive neuroectodermal tumor. Drugs used in chemotherapy use different ways to stop tumor cells from dividing so they stop growing or die. Combining more than one drug may kill more tumor cells.

Detailed Description

OBJECTIVES:

I. Evaluate the response rate and duration of response of patients with newly diagnosed, metastatic Ewing's sarcoma or primitive neuroectodermal tumor treated with maximally intensified VAdrC (vincristine, doxorubicin, cyclophosphamide) alternating with IE (ifosfamide, etoposide).

II. Evaluate the response to new agents (first topotecan, then topotecan with cyclophosphamide) utilized in an upfront treatment window.

III. Assess the role of surgery with regard to local control of primary and metastatic sites and disease course.

IV. Evaluate whether individual variability in ifosfamide and cyclophosphamide metabolism correlates with toxicity and/or response.

V. Evaluate the rise in the absolute neutrophil count following one dose of filgrastim (G-CSF) given immediately prior to a chemotherapy course as an indicator of bone marrow reserve and subsequent myelosuppression.

VI. Determine if amifostine provides significant chemo-radio protection, particularly against the cumulative toxicities of this intensive therapy.

OUTLINE: This is a partially randomized, multicenter study.

Patients are treated on the investigational window first or proceed to induction therapy immediately, if aggressive treatment is necessary.

INVESTIGATIONAL WINDOW: Patients receive cyclophosphamide IV and topotecan IV over 30 minutes on days 1-5. Filgrastim (G-CSF) is administered subcutaneously (SQ) beginning day 6 until blood cell counts recover. Treatment is repeated at week 3.

INDUCTION THERAPY: Patients over 12 months old are randomized to receive amifostine or not. Patients receive etoposide IV over 45 minutes and ifosfamide IV over 2 hours on days 1-5. Amifostine IV over 15 minutes is also administered prior to ifosfamide. Patients receive G-CSF SQ (or IV over 2 hours) beginning on day 6. This course of treatment is administered on weeks 6, 12, and 18. Patients receive the VAdrC chemotherapy regimen on weeks 9 and 15. This regimen consists of vincristine IV and amifostine IV over 15 minutes on days 1, 8, and 15, cyclophosphamide IV over 30 minutes and doxorubicin IV over 48 hours on days 1 and 2, and G-CSF beginning on day 3. The VAdrC regimen is continued during local therapy on weeks 21-29 and 39-47, except the day 15 dose of vincristine is omitted, cyclophosphamide is administered on day 1 only on weeks 21, 24, 27, 39, 42, and 45, and doxorubicin is replaced with etoposide IV over 60 minutes on days 1-3 on weeks 24, 28, 42, and 45. Local therapy begins after 21 weeks of chemotherapy. Patients who respond to chemotherapy and have resectable disease undergo a complete resection with negative margins. Patients with unresectable disease or bulky lesions undergo radiotherapy. Some patients may undergo both surgery and radiotherapy. Local therapy of metastases is delayed until after week 39. Patients are followed every 3 months for 1 year, every 6 months for 2 years, then annually thereafter.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
130
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
Arm Ilow-LET electron therapySee detailed description.
Arm Ilow-LET photon therapySee detailed description.
Arm Iconventional surgerySee detailed description.
Arm Ilow-LET cobalt-60 gamma ray therapySee detailed description.
Arm IfilgrastimSee detailed description.
Arm Iamifostine trihydrateSee detailed description.
Arm IcyclophosphamideSee detailed description.
Arm Idoxorubicin hydrochlorideSee detailed description.
Arm IetoposideSee detailed description.
Arm IifosfamideSee detailed description.
Arm Itopotecan hydrochlorideSee detailed description.
Arm Ivincristine sulfateSee detailed description.
Primary Outcome Measures
NameTimeMethod
Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (49)

Children's Hospital of Philadelphia

🇺🇸

Philadelphia, Pennsylvania, United States

Medical City Dallas Hospital

🇺🇸

Dallas, Texas, United States

Long Beach Memorial Medical Center

🇺🇸

Long Beach, California, United States

Jonsson Comprehensive Cancer Center, UCLA

🇺🇸

Los Angeles, California, United States

Via Christi Regional Medical Center-Saint Francis Campus

🇺🇸

Wichita, Kansas, United States

CCOP - Kalamazoo

🇺🇸

Kalamazoo, Michigan, United States

Montreal Children's Hospital

🇨🇦

Montreal, Quebec, Canada

MBCCOP - LSU Medical Center

🇺🇸

New Orleans, Louisiana, United States

Princess Margaret Hospital for Children

🇦🇺

Perth, Western Australia, Australia

University of Puerto Rico School of Medicine Medical Sciences Campus

🇵🇷

San Juan, Puerto Rico

University of Iowa Hospitals and Clinics

🇺🇸

Iowa City, Iowa, United States

Veterans Affairs Medical Center - Fargo

🇺🇸

Fargo, North Dakota, United States

University of Wisconsin Comprehensive Cancer Center

🇺🇸

Madison, Wisconsin, United States

University of Minnesota Cancer Center

🇺🇸

Minneapolis, Minnesota, United States

UCSF Cancer Center and Cancer Research Institute

🇺🇸

San Francisco, California, United States

Children's Hospital of Denver

🇺🇸

Denver, Colorado, United States

University of Chicago Cancer Research Center

🇺🇸

Chicago, Illinois, United States

Indiana University Cancer Center

🇺🇸

Indianapolis, Indiana, United States

Children's Hospital Medical Center - Cincinnati

🇺🇸

Cincinnati, Ohio, United States

Ireland Cancer Center

🇺🇸

Cleveland, Ohio, United States

University of Texas - MD Anderson Cancer Center

🇺🇸

Houston, Texas, United States

Fred Hutchinson Cancer Research Center

🇺🇸

Seattle, Washington, United States

Children's Hospital of Columbus

🇺🇸

Columbus, Ohio, United States

Doernbecher Children's Hospital

🇺🇸

Portland, Oregon, United States

University of Texas Health Science Center at San Antonio

🇺🇸

San Antonio, Texas, United States

Children's Hospital of Pittsburgh

🇺🇸

Pittsburgh, Pennsylvania, United States

Vanderbilt Cancer Center

🇺🇸

Nashville, Tennessee, United States

Children's Hospital and Regional Medical Center - Seattle

🇺🇸

Seattle, Washington, United States

Children's Hospital Los Angeles

🇺🇸

Los Angeles, California, United States

Children's Hospital of Orange County

🇺🇸

Orange, California, United States

David Grant Medical Center

🇺🇸

Travis Air Force Base, California, United States

Kaplan Cancer Center

🇺🇸

New York, New York, United States

Memorial Sloan-Kettering Cancer Center

🇺🇸

New York, New York, United States

Herbert Irving Comprehensive Cancer Center

🇺🇸

New York, New York, United States

Memorial Mission Hospital

🇺🇸

Asheville, North Carolina, United States

CCOP - Merit Care Hospital

🇺🇸

Fargo, North Dakota, United States

Cancer Institute of New Jersey

🇺🇸

New Brunswick, New Jersey, United States

Cancer Center, University of Virginia HSC

🇺🇸

Charlottesville, Virginia, United States

San Antonio Military Pediatric Cancer and Blood Disorders Center

🇺🇸

Lackland Air Force Base, Texas, United States

IWK Grace Health Centre

🇨🇦

Halifax, Nova Scotia, Canada

Huntsman Cancer Institute

🇺🇸

Salt Lake City, Utah, United States

Clinique de Pediatrie

🇨🇭

Geneva, Switzerland

British Columbia Children's Hospital

🇨🇦

Vancouver, British Columbia, Canada

Children's National Medical Center

🇺🇸

Washington, District of Columbia, United States

University of Michigan Comprehensive Cancer Center

🇺🇸

Ann Arbor, Michigan, United States

Mayo Clinic Cancer Center

🇺🇸

Rochester, Minnesota, United States

Children's Mercy Hospital - Kansas City

🇺🇸

Kansas City, Missouri, United States

University of Nebraska Medical Center

🇺🇸

Omaha, Nebraska, United States

Lineberger Comprehensive Cancer Center, UNC

🇺🇸

Chapel Hill, North Carolina, United States

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