MedPath

A Study of Erdafitinib in Participants With Metastatic or Locally Advanced Urothelial Cancer

Phase 1
Active, not recruiting
Conditions
Urothelial Carcinoma
Interventions
Registration Number
NCT03473743
Lead Sponsor
Janssen Research & Development, LLC
Brief Summary

The purpose of this study is to: (a) characterize the safety and tolerability of and to identify the recommended Phase 2 dose (RP2D) and schedule for erdafitinib in combination with cetrelimab, and for erdafitinib in combination with cetrelimab and platinum (cisplatin and carboplatin) chemotherapy and; (b) to evaluate the safety and clinical activity of erdafitinib alone and in combination with cetrelimab in cisplatin-ineligible participants with metastatic or locally advanced urothelial cancer (UC) with select fibroblast growth factor receptor (FGFR) gene alterations and no prior systemic therapy for metastatic disease.

Detailed Description

This open-label (all people know identity of intervention) and multicenter (when more than one hospital or medical school team work on a medical research study) study to establish the recommended phase 2 dose (RP2D) for erdafitinib and cetrelimab and/or platinum (cisplatin or carboplatin) chemotherapy, and to evaluate the safety of erdafitinib in combination with cetrelimab and platinum chemotherapy in Phase 1b and to evaluate the safety and efficacy of the RP2D of erdafitinib plus cetrelimab versus erdafitinib in Phase 2 in participants with advanced urothelial cancer with select fibroblast growth factor receptor (FGFR) gene alterations. Participants enrolled in Phase 1b erdafitinib + cetrelimab cohort may have received any number of lines of prior therapy, and participants enrolled in Phase 1b erdafitinib + cetrelimab + platinum chemotherapy cohort will have had no prior systemic therapy for metastatic disease and participants enrolled in Phase 2 will have had no prior systemic therapy for metastatic disease and will be cis-ineligible. Part 1 (Phase 1b: Dose Escalation) will identify safety and RP2Ds of erdafitinib + cetrelimab and erdafitinib + cetrelimab + platinum (cisplatin or carboplatin) chemotherapy, and Part 2 (Phase 2: Dose Expansion) will evaluate erdafitinib monotherapy and the RP2D regimen of the erdafitinib + cetrelimab combination to further characterize safety and clinical activity. The study will be conducted in 3 phases: screening phase, treatment phase, and follow-up phase. Study evaluations include efficacy, pharmacokinetics, pharmacodynamics, immunogenicity, biomarkers, and safety.

Recruitment & Eligibility

Status
ACTIVE_NOT_RECRUITING
Sex
All
Target Recruitment
125
Inclusion Criteria
  • Histologic demonstration of transitional cell carcinoma of the urothelium. Variant urothelial carcinoma histologies such as glandular or squamous differentiation, or evolution to more aggressive phenotypes such as sarcomatoid or micropapillary change are acceptable
  • Metastatic or locally advanced urothelial cancer
  • Must have measurable disease by radiological imaging according to the Response Evaluation Criteria in Solid Tumors (RECIST, version 1.1) at baseline
  • Prior systemic therapy for metastatic urothelial cancer: (a) For Phase 1b erdafitinib + cetrelimab cohort: Any number of lines of prior therapy; (b) For Phase 1b erdafitinib + cetrelimab + platinum chemotherapy cohort: No prior systemic therapy for metastatic disease; and renal function for participants must have a creatinine clearance (CrCl) greater than (>) 30 milliliter per minute (mL/min) to receive carboplatin and >60 mL/min to receive cisplatin as calculated by Cockcroft Gault and (c) Phase 2: No prior systemic therapy for metastatic disease and cisplatin-ineligible based on: ECOG PS 0-1 and at least one of the following criteria: Renal function defined as creatinine clearance (CrCl) less than (˂) 60 mL/min as calculated by Cockcroft-Gault; Grade 2 or higher peripheral neuropathy per NCI-CTCAE version 5.0; Grade 2 or higher hearing loss per NCI-CTCAE version 5.0 OR ECOG PS 2
  • Eastern Cooperative Oncology Group (ECOG) performance status (PS) grade of: (a) Phase 1b erdafitinib + cetrelimab cohort: ECOG 0-2; (b) Phase 1b erdafitinib + cetrelimab + platinum chemotherapy cohort: ECOG 0-1 for cisplatin and 0-2 for carboplatin (c) Phase 2: ECOG 0-2
Exclusion Criteria
  • Treatment with any other investigational agent or participation in another clinical study with therapeutic intent within 30 days prior to Cycle 1 Day 1. For Phase 1b, participants who have received the following prior antitumor therapy: received nitrosoureas and mitomycin C within 6 weeks
  • Phase 1b erdafitinib + cetrelimab cohort: Chemotherapy within 3 weeks of Cycle 1 Day 1; Phase 1b erdafitinib + cetrelimab + platinum chemotherapy cohort and Phase 2: Prior neoadjuvant/adjuvant chemotherapy is allowed if the last dose was given >12 months prior to recurrent disease progression and did not result in drug-related toxicity leading to treatment discontinuation
  • Prior anti-programmed death receptor-1 (PD-1), anti-programmed death ligand-1 (PD-L1), or anti-programmed death ligand-2 (PD-L2) therapy. Prior neoadjuvant/adjuvant checkpoint inhibitor therapy is allowed if the last dose was given more than (>)12 months prior to recurrent disease progression and did not result in drug-related toxicity leading to treatment discontinuation. PD-1 for non-muscle invasive bladder cancer is also allowed
  • Active malignancies requiring concurrent therapy other than urothelial cancer
  • Symptomatic central nervous system metastases

Study & Design

Study Type
INTERVENTIONAL
Study Design
SEQUENTIAL
Arm && Interventions
GroupInterventionDescription
Phase 1b: Dose EscalationErdafitinibTwo dosing cohorts (erdafitinib and cetrelimab; and erdafitinib, cetrelimab and cisplatin/carboplatin) are explored in Phase 1b of the study. Participants will receive erdafitinib orally followed by cetrelimab intravenously (IV) and carboplatin/cisplatin IV as a part of platinum chemotherapy. The dose levels will be escalated sequentially based on the decisions of the Study Evaluation Team (SET) until the recommended Phase 2 Dose (RP2D) has been identified.
Phase 2: Dose ExpansionCetrelimabThe participants will be randomized in a 1:1 manner to receive either erdafitinib alone (orally) or the identified RP2D of Phase 1b for erdafitinib (orally) in combination with cetrelimab (IV).
Phase 1b: Dose EscalationCisplatinTwo dosing cohorts (erdafitinib and cetrelimab; and erdafitinib, cetrelimab and cisplatin/carboplatin) are explored in Phase 1b of the study. Participants will receive erdafitinib orally followed by cetrelimab intravenously (IV) and carboplatin/cisplatin IV as a part of platinum chemotherapy. The dose levels will be escalated sequentially based on the decisions of the Study Evaluation Team (SET) until the recommended Phase 2 Dose (RP2D) has been identified.
Phase 2: Dose ExpansionErdafitinibThe participants will be randomized in a 1:1 manner to receive either erdafitinib alone (orally) or the identified RP2D of Phase 1b for erdafitinib (orally) in combination with cetrelimab (IV).
Phase 1b: Dose EscalationCetrelimabTwo dosing cohorts (erdafitinib and cetrelimab; and erdafitinib, cetrelimab and cisplatin/carboplatin) are explored in Phase 1b of the study. Participants will receive erdafitinib orally followed by cetrelimab intravenously (IV) and carboplatin/cisplatin IV as a part of platinum chemotherapy. The dose levels will be escalated sequentially based on the decisions of the Study Evaluation Team (SET) until the recommended Phase 2 Dose (RP2D) has been identified.
Phase 1b: Dose EscalationCarboplatinTwo dosing cohorts (erdafitinib and cetrelimab; and erdafitinib, cetrelimab and cisplatin/carboplatin) are explored in Phase 1b of the study. Participants will receive erdafitinib orally followed by cetrelimab intravenously (IV) and carboplatin/cisplatin IV as a part of platinum chemotherapy. The dose levels will be escalated sequentially based on the decisions of the Study Evaluation Team (SET) until the recommended Phase 2 Dose (RP2D) has been identified.
Primary Outcome Measures
NameTimeMethod
Phase 2: Number of Participants With Treatment-emergent Adverse Event (TEAEs)From Day 1 up to 36 months

Number of participants with TEAEs were reported. An adverse event is any untoward medical event that occurs in a participant administered an investigational product and it does not necessarily indicate only events with clear causal relationship with the relevant investigational product. TEAEs were defined as adverse events with onset or worsening on or after date of first dose of study treatment.

Phase 1b: Number of Participants With Dose-Limiting Toxicity (DLTs)Up to 8 weeks

Number of participants with DLTs were reported. The DLTs as per National Cancer Institute Common Terminology Criteria for Adverse Events Version 5.0 (NCI-CTCAE version 5.0) are specific adverse events defined as grade 3 (severe), grade 4 (life-threatening), and grade 5 (death) non-hematological toxicity or hematological toxicity.

Phase 2: Objective Response Rate (ORR) Per Response Evaluation Criteria in Solid Tumors (RECIST) 1.1 by Investigator AssessmentFrom Day 1 up to 36 months

ORR is defined as the percentage of participants who achieved confirmed complete response (CR) or confirmed partial response (PR), according to response evaluation criteria in solid tumors (RECIST) version1.1. As per RECIST version 1.1, CR: disappearance of all lesions; all lymph nodes were non-pathological in size and normalization of tumor marker level; PR: greater than or equal to (\>=) 30 percent (%) decrease in the sum of the diameters of all target lesions compared with baseline, in absence of new lesions or unequivocal progression of nontarget lesions.

Secondary Outcome Measures
NameTimeMethod
Phase 1b and Phase 2: Serum Concentration of CetrelimabUp to 6 years 1 month
Phase 2: Number of Participants With Abnormal Laboratory ValuesUp to 6 years 1 month
Phase 2: Progression-free Survival (PFS)Up to 6 years 1 month
Phase 1b and Phase 2: Plasma Concentration of ErdafitinibUp to 6 years 1 month
Phase 2: Number of Participants With Serious Adverse Events (SAEs)Up to 6 years 1 month
Phase 1b and Phase 2: Number of Participants With Anti-Cetrelimab AntibodiesUp to 6 years 1 month
Phase 1b: Plasma Concentration of Platinum (Cisplatin and Carboplatin) ChemotherapyUp to 6 years 1 month
Phase 2: Duration of Response (DoR)Up to 6 years 1 month
Phase 2: Overall Survival (OS)Up to 6 years 1 month
Phase 2: Time to Response (TTR)Up to 6 years 1 month

Trial Locations

Locations (127)

Grodno University Hospital

🇧🇾

Grodno, Belarus

State Institution N.N. Alexandrov Republican Scientific and

🇧🇾

Lesnoy, Belarus

Minsk city Clinical Oncological Dispensary

🇧🇾

Minsk, Belarus

Mogilev Regional Hospital

🇧🇾

Mogilev, Belarus

Vitebsk Regional Clinical Hospital

🇧🇾

Vitebsk, Belarus

ULB Hôpital Erasme

🇧🇪

Bruxelles, Belgium

Cliniques Universitaires Saint Luc

🇧🇪

Bruxelles, Belgium

Jolimont

🇧🇪

Haine-Saint-Paul, Belgium

Az Groeninge

🇧🇪

Kortrijk, Belgium

CHU de Liège - Domaine Universitaire du Sart Tilman

🇧🇪

Liege, Belgium

AZ Nikolaas - Campus Sint-Niklaas Moerland

🇧🇪

Sint-Niklaas, Belgium

GZA Ziekenhuizen- Campus St Augustinus

🇧🇪

Wilrijk, Belgium

Fundacao Pio XII

🇧🇷

Barretos, Brazil

Santa Casa de Misericordia de Belo Horizonte

🇧🇷

Belo Horizonte, Brazil

Liga Paranaense de Combate ao Cancer

🇧🇷

Curitiba, Brazil

Oncocentro Servicos Medicos e Hospitalares Ltda - Oncocentro

🇧🇷

Fortaleza, Brazil

Oncoclinicas Rio de Janeiro S A

🇧🇷

Rio de Janeiro, Brazil

Instituto de Educacao, Pesquisa e Gestao em Saude Instituto Americas (COI)

🇧🇷

Rio de Janeiro, Brazil

CEPHO Centro de Estudos e Pesquisa de Hematologia e Oncologia

🇧🇷

Santo Andre, Brazil

Institut de Cancerologie de Ouest (ICO) Site Paul Papin

🇫🇷

Angers Cedex 02, France

Hopital Saint André

🇫🇷

Bordeaux, France

Centre Francois Baclesse

🇫🇷

Caen, France

Centre Leon Berard

🇫🇷

Lyon, France

APHM Hopital Timone

🇫🇷

Marseille, France

Hopital Europeen Georges Pompidou

🇫🇷

Paris, France

Clinique Sainte Anne

🇫🇷

Strasbourg, France

CHRU de Tours

🇫🇷

Tours, France

Clinical Diagnostic Centre of Nizhny Novgorod Region

🇷🇺

Nizhny Novgorod, Russian Federation

Privolzhsky District Medical Centre

🇷🇺

Nizhny Novgorod, Russian Federation

Private Medical Institution Euromedservice

🇷🇺

Saint Petersburg, Russian Federation

Russian Scientific Center of Radiology and Surgical Technologies

🇷🇺

Sankt-Peterburg, Russian Federation

Tambov Regional Oncology Clinical Dispansary

🇷🇺

Tambov, Russian Federation

Multifunctional clinical medical center 'Medical city'

🇷🇺

Tyumen, Russian Federation

Hosp. Del Mar

🇪🇸

Barcelona, Spain

Hosp Clinic de Barcelona

🇪🇸

Barcelona, Spain

Hosp. Univ. Ramon Y Cajal

🇪🇸

Madrid, Spain

Hosp. Clinico San Carlos

🇪🇸

Madrid, Spain

Hosp Univ Fund Jimenez Diaz

🇪🇸

Madrid, Spain

Hosp Univ Hm Sanchinarro

🇪🇸

Madrid, Spain

Hosp Virgen de La Victoria

🇪🇸

Málaga, Spain

Complexo Hosp. Univ. de Ourense

🇪🇸

Ourense, Spain

Complejo Hospitalario de Vigo

🇪🇸

Pontevedra, Spain

Hosp. Quiron Madrid Pozuelo

🇪🇸

Pozuelo de Alarcon, Spain

Corporacio Sanitari Parc Tauli

🇪🇸

Sabadell, Spain

Hosp. Univ. Marques de Valdecilla

🇪🇸

Santander, Spain

H. Clinico Universitario de Santiago de Compostela

🇪🇸

Santiago de Compostela, Spain

Hosp. Virgen Macarena

🇪🇸

Sevilla, Spain

Hosp. Virgen Del Rocio

🇪🇸

Sevilla, Spain

Instituto Valenciano de Oncologia

🇪🇸

Valencia, Spain

Hosp. Clinico Univ. de Valencia

🇪🇸

Valencia, Spain

Centre hospitalier Saint Louis

🇫🇷

La Rochelle Cedex 1, France

Cliniche Humanitas Gavazzeni

🇮🇹

Bergamo, Italy

Istituto di Candiolo, IRCCS

🇮🇹

Candiolo, Italy

Ospedale Di Zona B Ramazzini

🇮🇹

Carpi, Italy

UOS Oncologia Medica, A.O. Cannizzaro

🇮🇹

Catania, Italy

Arcispedale S. Anna Ferrara

🇮🇹

Ferrara, Italy

PO A.Manzoni di Lecco, ASST Lecco - Oncologia Medica - Lecco

🇮🇹

Lecco, Italy

Ospedale Civile Di Livorno

🇮🇹

Livorno, Italy

IRCCS Ospedale San Raffaele

🇮🇹

Milano, Italy

ASST Grande Ospedale Metropolitano Niguarda

🇮🇹

Milano, Italy

Clinical Oncology Dispensary

🇷🇺

Omsk, Russian Federation

LLC Novaya Clinica

🇷🇺

Pyatigorsk, Russian Federation

Adnan Menderes University Training and Research Hospital

🇹🇷

Aydin, Turkey

Trakya University Medical Faculty

🇹🇷

Edirne, Turkey

Istanbul University Cerrahpasa Medical Faculty

🇹🇷

Istanbul, Turkey

Royal Lancaster Infirmary

🇬🇧

Lancaster, United Kingdom

St Bartholomew's Hospital

🇬🇧

London, United Kingdom

White Plains Hospital Center for Cancer Care

🇺🇸

White Plains, New York, United States

Gomel Regional Clinical Oncology Dispensary

🇧🇾

Gomel, Belarus

Rocky Mountain Cancer Centers

🇺🇸

Aurora, Colorado, United States

Norton Cancer Institute

🇺🇸

Louisville, Kentucky, United States

Maryland Oncology Hematology, PA

🇺🇸

Rockville, Maryland, United States

Hackensack University Medical Center

🇺🇸

Hackensack, New Jersey, United States

Weill Cornell Medical College - NY Presbyterian Hospital

🇺🇸

New York, New York, United States

Levine Cancer Institute, Carolinas HealthCare System

🇺🇸

Charlotte, North Carolina, United States

Toledo Clinic Cancer Centers

🇺🇸

Toledo, Ohio, United States

Penn State Hershey Cancer Institute

🇺🇸

Hershey, Pennsylvania, United States

Texas Oncology, P.A.

🇺🇸

Fort Worth, Texas, United States

The University of Texas MD Anderson Cancer Center

🇺🇸

Houston, Texas, United States

Virginia Oncology Associates

🇺🇸

Norfolk, Virginia, United States

Brest Regional Oncology Dispensary

🇧🇾

Brest, Belarus

Institut de Cancerologie de Lorraine

🇫🇷

Vandoeuvre lès Nancy, France

Institut Gustave Roussy

🇫🇷

Villejuif, France

Ospedale S. Maria Della Misericordia Centro Operativo Studi Clinici SC Oncologia Medica

🇮🇹

Perugia, Italy

AUSL DI PIACENZA - Ospedale Guglielmo da Saliceto

🇮🇹

Piacenza, Italy

Campus Bio Medico di Roma

🇮🇹

Roma, Italy

Azienda Socio Sanitaria Territoriale (ASST) della Valtellin

🇮🇹

Sondrio, Italy

Azienda Ospedaliera S. Maria Terni

🇮🇹

Terni, Italy

Azienda Ospedaliero Universitaria S.Maria Della Misericordia

🇮🇹

Udine, Italy

Chungnam National University Hospital

🇰🇷

Daejeon, Korea, Republic of

Chonnam National University Hospital

🇰🇷

Gwangju, Korea, Republic of

The Catholic university of Korea, St. Vincent's Hospital

🇰🇷

Gyeonggi-do, Korea, Republic of

Seoul National University Hospital

🇰🇷

Seoul, Korea, Republic of

Kangbuk Samsung Hospital

🇰🇷

Seoul, Korea, Republic of

Severance Hospital Yonsei University Health System

🇰🇷

Seoul, Korea, Republic of

Asan Medical Center

🇰🇷

Seoul, Korea, Republic of

The Catholic University of Korea Seoul St Marys Hospital

🇰🇷

Seoul, Korea, Republic of

Seoul Metropolitan Government Seoul National University Boramae Medical Center

🇰🇷

Seoul, Korea, Republic of

Pusan National University Yangsan Hospital

🇰🇷

Yangsan-si, Korea, Republic of

Przychodnia Lekarska KOMED Roman Karaszewski

🇵🇱

Konin, Poland

Wojewodzkie Wielospecjalistyczne Centrum Onkologii i Traumatologii im M Kopernika w Lodzi

🇵🇱

Lodz, Poland

LUX MED Onkologia Sp. z o.o.

🇵🇱

Warszawa, Poland

Centralny Szpital Kliniczny MSWiA w Warszawie

🇵🇱

Warszawa, Poland

Altai Regional Oncology Dispensary

🇷🇺

Barnaul, Russian Federation

Ivanovo Regional Oncology Dispensary

🇷🇺

Ivanovo, Russian Federation

GUZ Kursk Regional Oncology Dispensary

🇷🇺

Kislino Village, Russian Federation

Leningrad Regional Oncology Dispensary

🇷🇺

Kuzmolovsky, Russian Federation

City Clinical Hospital n.a. D.D.Pletnev

🇷🇺

Moscow, Russian Federation

Russian Scientific Center of Roentgenoradiology

🇷🇺

Moscow, Russian Federation

Moscow City Clinical Hospital # 62

🇷🇺

Moscow, Russian Federation

Kaohsiung Chang Gung Memorial Hospital

🇨🇳

Kaohsiung City, Taiwan

Kaohsiung Medical University Chung Ho Memorial Hospital

🇨🇳

Kaohsiung, Taiwan

China Medical University Hospital

🇨🇳

Taichung City, Taiwan

National Cheng Kung University Hospital

🇨🇳

Tainan, Taiwan

National Taiwan University Hospital

🇨🇳

Taipei City, Taiwan

Chang-Gung Memorial Hospital, LinKou Branch

🇨🇳

Taoyuan, Taiwan

Adana Acibadem Hospital

🇹🇷

Adana, Turkey

Memorial Ankara Hastanesi

🇹🇷

Ankara, Turkey

Hacettepe University Medical Faculty

🇹🇷

Ankara, Turkey

Dr Abdurrahman Yurtaslan Oncology Training and Research Hospital

🇹🇷

Ankara, Turkey

Istanbul Medeniyet University Goztepe Training and Research Hospital

🇹🇷

Istanbul, Turkey

Ege University

🇹🇷

Izmir, Turkey

Kocaeli University Medical Faculty

🇹🇷

Kocaeli, Turkey

Necmettin Erbakan University Meram Medical Faculty

🇹🇷

Konya, Turkey

Karadeniz Teknik University Medical Faculty

🇹🇷

Trabzon, Turkey

University College London Hospitals Nhs Foundation Trust

🇬🇧

London, United Kingdom

Nottingham University Hospitals NHS Trust

🇬🇧

Nottingham, United Kingdom

© Copyright 2025. All Rights Reserved by MedPath