MedPath

NGS Screening Protocol to Detect Mutation of KEAP1 or NRF2/NFE2L2 Genes for the KEAPSAKE (CX-839-014) Trial

Terminated
Conditions
Non-Small Cell Lung Cancer
NFE2L2 Gene Mutation
KEAP1 Gene Mutation
NRF2 Mutation
Non-Squamous Non-Small Cell Neoplasm of Lung
Non-squamous Non-small-cell Lung Cancer
Registration Number
NCT04698681
Lead Sponsor
Calithera Biosciences, Inc
Brief Summary

This is a multicenter screening protocol designed to identify patients with NSCLC who have tumor mutations in the KEAP1 or NRF2/NFE2L2 genes in order to determine potential eligibility for a biomarker selected clinical trial (CX-839-014, otherwise known as the KEAPSAKE trial). Circulating tumor DNA (ctDNA) present in blood samples collected from eligible patients will be analyzed by next generation sequencing (NGS) for selected biomarkers. A commercial liquid biopsy NGS test will be provided to study participants free of charge.

Detailed Description

Not available

Recruitment & Eligibility

Status
TERMINATED
Sex
All
Target Recruitment
20
Inclusion Criteria

Patients with stage IV non-squamous non-small-cell lung cancer (NSCLC) who have not been previously treated with systemic therapy for metastatic disease, and meet all of the following:

  1. Signed and dated NGS Informed Consent Form (ICF) by the patient (or legally acceptable representative (LAR), if applicable).
  2. Biopsy-confirmed OR clinically suspected stage IV NSCLC not previously treated with systemic therapy for metastatic disease.
  3. Eastern Cooperative Oncology Group (ECOG) performance status of 0 or 1.
  4. Age ≥ 18 years old on the day of signing informed consent.
  5. Estimated life expectancy > 3 months.
  6. At least one radiographically measurable lesion per RECIST v1.1 defined as a lesion that is ≥ 10 mm in longest diameter or lymph node that is ≥ 15 mm in short axis imaged by computed tomography (CT) scan or magnetic resonance imaging (MRI).
  7. Clinically eligible to receive standard-of-care combination therapy with pemetrexed + carboplatin + Pembrolizumab (PCP) for stage IV disease.
Exclusion Criteria

Any contraindication to pemetrexed, carboplatin, and Pembrolizumab treatment.

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Positive KEAP1 or NRF2/NFE2L2 mutational status, assessed by NGS of blood ctDNAUp to 16 months

The percentage of patients with nonsquamous NSCLC containing pathogenic NRF2/NFE2L2 and/or KEAP1 mutations

Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (58)

Southern Cancer Center

🇺🇸

Daphne, Alabama, United States

Arizona Oncology Associates - Glendale

🇺🇸

Glendale, Arizona, United States

Rocky Mountain Cancer Centers - Lakewood

🇺🇸

Lakewood, Colorado, United States

Arizona Oncology Associates

🇺🇸

Scottsdale, Arizona, United States

Rocky Mountain Cancer Centers - Colorado Springs

🇺🇸

Colorado Springs, Colorado, United States

Rocky Mountain Cancer Centers - Aurora

🇺🇸

Aurora, Colorado, United States

Rocky Mountain Cancer Centers - Centennial

🇺🇸

Centennial, Colorado, United States

Maryland Hematology Oncology - Silver Spring

🇺🇸

Silver Spring, Maryland, United States

Medical Oncology Hematology Consultants

🇺🇸

Newark, Delaware, United States

Rocky Mountain Cancer Centers - Boulder

🇺🇸

Boulder, Colorado, United States

Woodlands Medical Specialists

🇺🇸

Pensacola, Florida, United States

Rocky Mountain Cancer Centers - Lone Tree

🇺🇸

Lone Tree, Colorado, United States

Rocky Mountain Cancer Centers - Littleton

🇺🇸

Littleton, Colorado, United States

Rocky Mountain Cancer Centers - Thornton

🇺🇸

Thornton, Colorado, United States

Maryland Oncology Hematology - Bethesda

🇺🇸

Bethesda, Maryland, United States

Maryland Oncology Hematology - Brandywine

🇺🇸

Brandywine, Maryland, United States

Maryland Oncology Hematology - Clinton

🇺🇸

Clinton, Maryland, United States

Maryland Oncology Hematology - Lanham

🇺🇸

Lanham, Maryland, United States

Maryland Hematology Oncology - Frederick

🇺🇸

Frederick, Maryland, United States

Maryland Hematology Oncology - Rockville

🇺🇸

Rockville, Maryland, United States

Oncology Hematology Care - Fairfield

🇺🇸

Fairfield, Ohio, United States

Northwest Cancer Specialists

🇺🇸

Vancouver, Washington, United States

Texas Oncology - West Texas Amarillo

🇺🇸

Amarillo, Texas, United States

Consultants in Medical Oncology and Hematology

🇺🇸

Wynnewood, Pennsylvania, United States

Texas Oncology - Beaumont Mamie McFaddin Ward Cancer Center

🇺🇸

Beaumont, Texas, United States

Texas Oncology Cancer Care and Research

🇺🇸

Harlingen, Texas, United States

Virginia Oncology Associaties

🇺🇸

Chesapeake, Virginia, United States

Texas Oncology - Beaumont

🇺🇸

Beaumont, Texas, United States

Texas Oncology - Carrollton

🇺🇸

Carrollton, Texas, United States

Texas Oncology - Weslaco

🇺🇸

Weslaco, Texas, United States

Texas Oncology - Denton

🇺🇸

Denton, Texas, United States

Texas Oncology - Flower Mound

🇺🇸

Flower Mound, Texas, United States

Texas Oncology - Longview Cancer Center

🇺🇸

Longview, Texas, United States

Texas Oncology - McAllen

🇺🇸

McAllen, Texas, United States

Texas Oncology - Tyler

🇺🇸

Tyler, Texas, United States

Texas Oncology - West Texas Midland

🇺🇸

Midland, Texas, United States

Texas Oncology - West Texas Odessa

🇺🇸

Odessa, Texas, United States

Texas Oncology - Sherman

🇺🇸

Sherman, Texas, United States

Texas Oncology - West Texas Wichita Falls

🇺🇸

Wichita Falls, Texas, United States

Virginia Cancer Specialists

🇺🇸

Norfolk, Virginia, United States

Southern Cancer Center - 3 Mobile Infirmary Circle

🇺🇸

Mobile, Alabama, United States

Virginia Oncology Associates

🇺🇸

Virginia Beach, Virginia, United States

Southern Cancer Center - Dauphin St

🇺🇸

Mobile, Alabama, United States

Rocky Mountain Cancer Centers - Englewood

🇺🇸

Englewood, Colorado, United States

Southern Cancer Center - Providence Hospital

🇺🇸

Mobile, Alabama, United States

Arizona Oncology Associates - Tempe

🇺🇸

Tempe, Arizona, United States

Rocky Mountain Cancer Centers - Longmont

🇺🇸

Longmont, Colorado, United States

Rocky Mountain Cancer Centers - Pueblo

🇺🇸

Pueblo, Colorado, United States

Maryland Oncology Hematology

🇺🇸

Columbia, Maryland, United States

Arizona Oncology Associates - E. Highland Ave.

🇺🇸

Phoenix, Arizona, United States

Arizona Oncology Associates - N. 27th Ave.

🇺🇸

Phoenix, Arizona, United States

Oncology Hematology Care - Mercy Health Blvd

🇺🇸

Cincinnati, Ohio, United States

Oncology Hematology Care - Malsbary Rd

🇺🇸

Cincinnati, Ohio, United States

Oncology Hematology Care - Ivy Gateway

🇺🇸

Cincinnati, Ohio, United States

Rocky Mountain Cancer Centers - Williams Street

🇺🇸

Denver, Colorado, United States

Rocky Mountain Cancer Centers - E. Hale Parkway

🇺🇸

Denver, Colorado, United States

Northwest Cancer Specialists - NE Hoyt St

🇺🇸

Portland, Oregon, United States

Northwest Cancer Specialists - N. Broadway

🇺🇸

Portland, Oregon, United States

© Copyright 2025. All Rights Reserved by MedPath