Physician Awareness and Understanding of Gaucher Disease: A Web based Study

Not Applicable

• Conditions: Gaucher Disease

• Registration Number: JPRN-UMIN000040117
• Lead Sponsor: Takeda Pharmaceutical Company Limited

Brief Summary

Survey results from 160 haematologists and 166 gastroenterologists indicated that more than 50% of haematologists were aware of GD symptoms, diagnostic criteria and/or treatments, and 38% of them had experienced or suspected GD. The majority of gastroenterologists were unaware of GD or knew the disease only by name, with 20% experiencing or suspecting GD in practice. Almost 70% of haematologists knew of ERT, while 47% of gastroenterologists were not aware of any treatments for GD.

Detailed Description

Not available

Study Timeline

• Results First Posted: 1900-01-01
• Study Start: 2020-04-13
• Study Completion: 2020-04-21
• Last Update Posted: 17 October 2023

Recruitment & Eligibility

• Status: Complete: follow-up complete
• Sex: All
• Target Recruitment: 326

Inclusion Criteria

Not provided

Exclusion Criteria

- Gastroenterologists that are not specialized in liver - Have less than 1 year of practice excluding training period - Work in a facility other than clinics, university hospitals, general hospitals and; national and public hospitals - Do not belong to any society, hematological nor gastroenterological

Study & Design

• Study Type: Others,meta-analysis etc
• Study Design: Not specified

Primary Outcome Measures

Name	Time	Method
- After reading case presentation in the survey, physicians select disease name, his/ her response from list in the survey by visualizing his/ her daily medical practice - Physicians select his/ her level of awareness, diagnosis experience, available knowledge and interest regarding Gaucher disease.