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Ovarian Function and Gynecological Profile of Patients Carrying a Pathogenic Variant of the HNF1B Gene (GYN-HNF1)

Not Applicable
Completed
Conditions
Genital Diseases, Female
Interventions
Other: Pelvic ultrasound
Biological: blood sample
Registration Number
NCT04746053
Lead Sponsor
University Hospital, Toulouse
Brief Summary

The main objective of this study is to study the ovarian function of patients with hepatocyte nuclear factor-1beta (HNF1B) abnormality, followed in the reference centers of Toulouse and Paris University Hospitals. The secondary objectives are to know the gynecological profile of these patients.

A dosage of anti-mullerian hormone (AMH) will be added to the usual balance, whatever the phase of the cycle and a pelvic ultrasound will be performed by the same operator by center. Patients will be received in a dedicated consultation to complete a questionnaire on gynecological and obstetric history, as well as their personal and family history. There will be no gynecological examination during this consultation.

Detailed Description

HNF1B mutations can be responsible for genital malformations associated with renal development abnormalities. HNF1b is also a candidate gene involved in the development of the renal tract and the Mullerian system but there is no data in the literature regarding the ovarian function and clinical gynecological profile of these patients.

The main objective of this study is to study the ovarian function of patients with HNF1B abnormality, followed in the reference centers of Toulouse and Paris University Hospitals. The secondary objectives are to know the gynecological profile of these patients.

A dosage of AMH will be added to the usual balance, whatever the phase of the cycle and a pelvic ultrasound will be performed. Patients will be received in a dedicated consultation to complete a questionnaire on gynecological and obstetric history, as well as their personal and family history. There will be no gynecological examination during this consultation.

Recruitment & Eligibility

Status
COMPLETED
Sex
Female
Target Recruitment
26
Inclusion Criteria
  • Girls from 12 years of age carrying a pathogenic variant of the HNF1 B gene and monitored in the reference center for rare renal diseases
  • Person affiliated or beneficiary of a social security scheme.
  • Free, informed and written consent signed by the participant or her legal representative if a minor patient and the investigator (at the latest on the day of inclusion and before any examination required by the research).
Exclusion Criteria
  • Woman unable to answer
  • Pregnant or breastfeeding woman
  • Refusal of participation by the patient or her legal representative
  • Person under a protection system for adults (such as safeguard of justice, guardianship or curatorship)
  • History of chemotherapy, radiotherapy, brachytherapy
  • History of ovarian endometrium

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
patient with a mutation in the HNF1B geneblood samplePatient with a mutation in the HNF1B gene and which are followed in the reference centers
patient with a mutation in the HNF1B genePelvic ultrasoundPatient with a mutation in the HNF1B gene and which are followed in the reference centers
Primary Outcome Measures
NameTimeMethod
serum level of Antimullerian Hormone levelsday 1

serum level of antimullerian hormone levels in ng/mL

Secondary Outcome Measures
NameTimeMethod
ultrasound resultday 1

ultrasound (pelvic or vaginal) will allow the team to look at whether or not there is a genital defect and the type of defect.

Trial Locations

Locations (3)

Pitié Salpêtrière Hospital -

🇫🇷

Paris, France

Toulouse University Hospital

🇫🇷

Toulouse, France

Necker Hospital

🇫🇷

Paris, France

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