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The Alpha-1 Foundation's and University of Florida's Alpha-1 Coded Testing (ACT) Study

Recruiting
Conditions
Alpha-1 Antitrypsin Deficiency
Registration Number
NCT00500123
Lead Sponsor
University of Florida
Brief Summary

The Alpha-1 Coded Testing (ACT) Study was established to study genetic testing and outcomes of individuals at risk for alpha-1 antitrypsin deficiency.

Detailed Description

Genetic testing for alpha-1 antitrypsin deficiency is sometimes delayed despite established testing indications. All genetic tests have risks and possible benefits. The ACT study evaluates the population demographics, reasons for testing, and outcomes through a confidential testing program. Co-morbidities of alpha-1 antitrypsin deficiency other than lung and liver disease are being investigated. Concerns about genetic confidentiality are lessened in this study by a coded testing procedure that returns results through the mail to study participants.

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
50000
Inclusion Criteria
  • Individuals of any age at risk for alpha-1 antitrypsin deficiency on the basis of symptoms or family genetic risk.
Exclusion Criteria
  • Any person who has already had genotype and AAT level testing completed and has a qualified result.

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Structured questionnaire responses on the risks and benefits of testing.Before and after alpha-1 antitrypsin testing

Rotating questionnaires assess the clinical course and co-morbidities associated with different genotypes of alpha-1 antitrypsin deficiency.

Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (1)

University of Florida

🇺🇸

Gainesville, Florida, United States

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