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Safety & Pharmacokinetics Study of Inhaled Laninamivir Octanoate TwinCaps® Dry Powder Inhaler in Children With Influenza

Phase 1
Terminated
Conditions
Influenza
Interventions
Registration Number
NCT02014649
Lead Sponsor
Biota Scientific Management Pty Ltd
Brief Summary

This Phase 1/2 protocol is designed to collect safety, tolerability and pharmacokinetic data of two doses of Laninamivir Octanoate in children and adolescents. The protocol will also explore virology and efficacy endpoints.

Detailed Description

Approximately 48 subjects aged 5-17 years inclusive will be randomised into the study.

Subjects with recent onset of presumptive influenza will have influenza A or B infection confirm by Rapid Antigen Test.

The study will be conducted on an outpatient basis. The dose is administered in a single session in the clinic on Day 1. The subject will return to the clinic for assessments and follow up.

Recruitment & Eligibility

Status
TERMINATED
Sex
All
Target Recruitment
15
Inclusion Criteria
  • Subjects' parent/legally acceptable representative/guardian must give written informed consent to participate in the study and must understand the nature of the study and must be willing to comply with all protocol requirements. Subjects over 12 must provide assent to participate in the study and potential subjects below this age should provide assent if deemed appropriate to the maturity level of the subject or if required according to local guidance/regulations.

  • Males or females aged between 5 and 17 years inclusive, who weigh at least 15 kg at screening.

  • Confirmed influenza infection based on positive rapid antigen test (RAT) for Influenza A or B.

  • Fever, defined as either:

    1. Otic temperature ≥38.0° C (100.4°F) at the screening visit, OR,
    2. A history of fever within the 24 hours prior to the screening visit and has administered antipyretic(s) in the 6 hours prior to the screening visit.
  • Presence on the Screening questionnaire of, at least two, of the following influenza symptoms:

    1. Non-productive Cough, of at least moderate severity,
    2. Sore throat, of at least moderate severity,
    3. Nasal congestion/runny nose, of at least moderate severity,
    4. Headache, of at least moderate severity,
    5. Muscle aches and pain, of at least moderate severity,
    6. Feeling feverish, of at least moderate severity,
    7. Low energy, tired, fatigue, of at least moderate severity;
  • Onset of illness no more than 40 hours before randomization, defined as:

    1. time when the temperature was first measured as elevated ≥38.0°C (oral or otic) OR
    2. time when the subject first experienced at least one influenza symptom (non-productive cough, sore throat or nasal congestion/runny nose, headache, muscle aches and pain, feeling feverish, or low energy/tired/fatigue)
  • In the Investigator's opinion able to complete the required inhalations of the investigational medicinal product.

Exclusion Criteria
  • Use of antiviral treatment for influenza (e.g., zanamivir, oseltamivir, peramivir, rimantadine, or amantadine) within 14 days prior to screening
  • Received influenza virus vaccine in the previous 3 weeks.
  • History or presence of clinically significant pulmonary disease (e.g., chronic obstructive pulmonary disease, cystic fibrosis, or bronchiectasis)
  • Current asthma requiring treatment, or history of asthma requiring treatment in the last 5 years, or episode of wheezing in the 12 months prior to randomization.
  • History of congestive heart failure with symptoms consistent with New York Heart Association Class III or IV functional status.
  • Presence of an immune compromised status due to chronic illness, organ transplantation or use of daily systemic immunosuppressants
  • Presence of clinically significant signs of acute respiratory distress during screening.
  • Current use of inhaled medications (nasal or oral) or anticipated use of inhaled medications (nasal or oral) at any time during the study.
  • Current or a history of acute or chronic renal impairment/disease
  • Currently hospitalized or any planned hospitalizations within 1 month following the last dose of IMP.
  • Current clinical evidence of otitis, bronchitis, sinusitis, or pneumonia or active bacterial infection at any body site
  • Severe infection within 30 days prior to screening which required parenteral antibiotic use or hospitalization.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
20mg Laninamivir Octanoate20 mg laninamivir octanoateDry Powder plus placebo
40mg Laninamivir Octanoate40 mg laninamivir octanoateDry Powder
20mg Laninamivir OctanoatePlaceboDry Powder plus placebo
Primary Outcome Measures
NameTimeMethod
To Evaluate Time to First Alleviation of a Composite of Influenza Symptoms and Absence of Fever.Subjects are assessed at clinic visits and followed up to 28-days post dose.

For subjects aged 5 through 12 years, the subject or parent/legal guardian completed the Canadian Acute Respiratory Illness and Flu Scale (CARIFS) symptom diary and measured otic body temperature twice a day, in the morning between 6 and 10AM and evening between 6 and 10PM, until the Day 10 visit. Subjects aged 13 through 17 years completed the Influenza Symptom Questionnaire (ISQ) themselves and measured otic body temperature twice a day, in the morning between 6 and 10AM and evening between 6 and 10PM, until the Day 10 visit.

Secondary Outcome Measures
NameTimeMethod
To Evaluate the Pharmacokinetic (PK) Profiles (Concentration) of the Prodrug, Laninamivir Octanoate, and Its Active Metabolite, Laninamivir, Following Administration of a Single Dose (20 or 40 mg)Samples are collected at clinic visits over 5 days.

Pharmacokinetic parameters will be calculated and summarized, PK concentration data will add to population models.

Trial Locations

Locations (28)

Precision Trials LLC

🇺🇸

Phoenix, Arizona, United States

Arkansas Children's Hospital

🇺🇸

Little Rock, Arkansas, United States

Dayton Children's Hospital

🇺🇸

Dayton, Ohio, United States

The University of Toledo Medical Center

🇺🇸

Toledo, Ohio, United States

Sanford Research University of South Dakota

🇺🇸

Sioux Falls, South Dakota, United States

West Houston Clinical Research Service

🇺🇸

Houston, Texas, United States

SoCal Clinical Research Med Group

🇺🇸

Bellflower, California, United States

Connecticut Children's Medical Center

🇺🇸

Hartford, Connecticut, United States

A.G.A Clinical Trials

🇺🇸

Hialeah, Florida, United States

Lafayette Clinical Research Group

🇺🇸

Lafayette, Indiana, United States

Dr Haidar's Clinic

🇺🇸

Carriere, Mississippi, United States

Avant Research Assoc.

🇺🇸

Houston, Texas, United States

Dixie Pediatrics

🇺🇸

Saint George, Utah, United States

Sherif Khamis MD Inc

🇺🇸

Canoga Park, California, United States

Advanced Medical Research

🇺🇸

Lakewood, California, United States

Madera Family Medical Group

🇺🇸

Madera, California, United States

University of Iowa Hospitals and Clinics

🇺🇸

Iowa City, Iowa, United States

DePaul Health Center

🇺🇸

Bridgeton, Missouri, United States

Cyn3rgy Research

🇺🇸

Gresham, Oregon, United States

Foothill Family Clinic

🇺🇸

Salt Lake City, Utah, United States

Louisiana State University Health Sciences Center

🇺🇸

Shreveport, Louisiana, United States

Blue Ridge Pediatric and Adolescent Medicine Group

🇺🇸

Boone, North Carolina, United States

Dr Santiago Reyes

🇺🇸

Oklahoma City, Oklahoma, United States

First Med

🇺🇸

Salt Lake City, Utah, United States

Foothill Family Clinic South

🇺🇸

Salt Lake City, Utah, United States

Copperview Medical Center

🇺🇸

South Jordan, Utah, United States

Rockwood Clinic

🇺🇸

Spokane, Washington, United States

Rockwood North Clinic

🇺🇸

Spokane, Washington, United States

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