MedPath

Single Ascending Dose (SAD) and Multiple Ascending Dose (MAD) Study of M5049 in Healthy Participants

Phase 1
Completed
Conditions
Healthy
Interventions
Drug: Placebo
Registration Number
NCT03676322
Lead Sponsor
Merck KGaA, Darmstadt, Germany
Brief Summary

The study will evaluate the safety, tolerability, Pharmacokinetic (PK), Pharmacodynamics (PD), and explore the food effect of M5049 in healthy male and female participants.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
96
Inclusion Criteria
  • Body weight between 50 to 100 kilogram (kg)
  • Body mass index (BMI) between 18.5 and 29.9 kilogram per meter square (kg/m^2)
  • Other protocol defined inclusion criteria could apply
Exclusion Criteria
  • History of clinically relevant disease of any organ system that may interfere with the objectives of the study or provide a risk to the health of the participant
  • History of splenectomy
  • History of epilepsy, other neurological disorders, or neuropsychiatric conditions
  • Other protocol defined exclusion criteria could apply

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Part B: M5049M5049-
Part A: PlaceboPlacebo-
Part C: M5049M5049-
Part B: PlaceboPlacebo-
Part A: M5049M5049-
Primary Outcome Measures
NameTimeMethod
Part A: Occurrence and Severity of Treatment-emergent Adverse Events (TEAEs) and Serious AEs (SAEs)Day 1 up to Day 21
Part A: Number of Participants With Clinically Significant Changes in Vital Signs, Laboratory Parameters and 12-lead Electrocardiogram (ECG) FindingsDay 1 up to Day 21

Number of participants with clinically significant changes will be reported.

Part C: Apparent Terminal Half-life (t1/2) of M5049Pre-dose up to Day 6
Part C: Apparent Volume of Distribution (Vz/f) of M5049Pre-dose up to Day 6
Part C: Maximum Observed Plasma Concentration (Cmax) of M5049Pre-dose up to Day 6
Part C: Area Under the Concentration-Time Curve Over Entire Dosing Time Period From Time Zero Extrapolated to Infinity (AUC0-inf)Pre-dose up to Day 6
Part C: Area Under the Plasma Concentration-Time Curve From Time Zero to the Last Sampling Time (AUC 0-t) of M5049Pre-dose up to Day 6
Part B: Occurrence and Severity of TEAEs and SAEsDay 1 up to Day 33
Part B: Number of Participants With Clinically Significant Changes in Vital Signs, Laboratory Parameters and 12-lead Electrocardiogram (ECG) FindingsDay 1 up to Day 33

Number of participants with clinically significant changes will be reported.

Part C: Time to Reach Maximum Plasma Concentration (tmax) of M5049Pre-dose up to Day 6
Part C: Elimination Rate Constant (λz) of M5049Pre-dose up to Day 6
Part C: Total Body Clearance (CL/f) of M5049Pre-dose up to Day 6
Secondary Outcome Measures
NameTimeMethod
Part B: Dose Normalized Area Under the Concentration-Time Curve Over the Dosing Interval (AUCtau/D) of M5049Pre-dose up to Day 19
Part C: Occurrence and Severity of Treatment-emergent Adverse Events (TEAEs) and Serious AEs (SAEs)Day 1 up to Day 23
Part A: Time to Reach Maximum Plasma Concentration (tmax) of M5049Pre-dose up to Day 6
Part A: Area Under the Plasma Concentration-Time Curve From Time Zero to the Last Sampling Time (AUC 0-t) of M5049Pre-dose up to Day 6
Part A: Apparent Volume of Distribution (Vz/f) of M5049Pre-dose up to Day 6
Part A: Dose Normalized Maximum Observed Plasma Concentration (Cmax/D) of M5049Pre-dose up to Day 6
Part B: Maximum Observed Blood Concentration (Cmax) of M5049Pre-dose up to Day 19
Part B: Time to Reach Maximum Plasma Concentration (tmax) of M5049Pre-dose up to Day 19
Part A: Elimination Rate Constant (λz) of M5049Pre-dose up to Day 6
Part A: Total Body Clearance (CL/f) of M5049Pre-dose up to Day 6
Part B: Apparent Terminal Half-life (t1/2) of M5049Pre-dose up to Day 19
Part B: Apparent Volume of Distribution (Vz/f) of M5049Pre-dose up to Day 19
Part B: Accumulation Ratio for AUCtau(Racc AUCtau) of M5049Pre-dose up to Day 19
Part B: Plasma Concentration Prior to the Next Dose (C trough) of M5049Pre-dose up to Day 19
Part A: Apparent Terminal Half-life (t1/2) of M5049Pre-dose up to Day 6
Part C: Number of Participants With Clinically Significant Changes in Vital Signs, Laboratory Parameters and 12-lead Electrocardiogram (ECG) FindingsDay 1 up to Day 23

Number of participants with clinically significant changes will be reported.

Part A: Area Under the Concentration-Time Curve Over Entire Dosing Time Period From Time Zero Extrapolated to Infinity (AUC0-inf)Pre-dose up to Day 6
Part A: Change From Baseline in QT Interval Corrected Using Fridericia's Formula (QTcF) on Digital Holter Electrocardiograms (ECG) at Day 2Baseline, Day 2
Part B: Area Under the Plasma Concentration-Time Curve From Time Zero to the Last Sampling Time (AUC 0-t) of M5049Pre-dose up to Day 19
Part B: Area Under the Concentration-Time Curve Over Entire Dosing Time Period From Time Zero Extrapolated to Infinity (AUC0-inf)Pre-dose up to Day 19
Part A: Maximum Observed Blood Concentration (Cmax) of M5049Pre-dose up to Day 6
Part A: Time Matched Plasma Concentration of M5049Pre-dose up to Day 6
Part B: Elimination Rate Constant (λz) of M5049Pre-dose up to Day 19
Part B: Peak trough Ratio of M5049Pre-dose up to Day 19
Part B: Change From Baseline in QT Interval Corrected Using Fridericia's Formula (QTcF) on Digital Holter Electrocardiograms (ECG) at Day 2Baseline, Day 2
Part A: Dose Normalized Area Under the Plasma Concentration-Time Curve From Time Zero to the Last Sampling Time (AUC0-t/D) of M5049Pre-dose up to Day 6
Part B: Total Body Clearance (CL/f) of M5049Pre-dose up to Day 19
Part B: Area Under the Concentration-Time Curve Over the Dosing Interval (AUCtau)Pre-dose up to Day 19
Part B: Accumulation Ratio for Cmax (Racc Cmax) of M5049Pre-dose up to Day 19
Part B: Dose Normalized Maximum Observed Plasma Concentration at Steady State (Cmaxss/D) of M5049Pre-dose up to Day 19
Part B: Time Matched Plasma Concentration of M5049Pre-dose up to Day 19

Trial Locations

Locations (1)

Nuvisan GmbH

🇩🇪

Neu-Ulm, Germany

© Copyright 2025. All Rights Reserved by MedPath