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Pilot Compassionate Use Study of Thioctic Acid Treatment in Mitochondrial Myopathy

Not Applicable
Completed
Conditions
Mitochondrial Myopathy
Registration Number
NCT00004770
Lead Sponsor
National Center for Research Resources (NCRR)
Brief Summary

OBJECTIVES:

I. Assess the efficacy of thioctic acid in treating a single patient with mitochondrial myopathy.

Detailed Description

PROTOCOL OUTLINE: The patient receives one thioctic acid tablet 3 times a day. If patient experiences no side effects after 1 week, 2 tablets are administered and given 3 times a day over 3 months for compassionate use.

The patient is followed at weeks 3, 8, and 12.

Recruitment & Eligibility

Status
COMPLETED
Sex
Male
Target Recruitment
1
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Secondary Outcome Measures
NameTimeMethod
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