MedPath

Non-interventional Study of Lenalidomide in the Clinical Routine Treatment of TD Patients With IPSS Low or Int-1 MDS and Isolated Del(5q)

Completed
Conditions
Myelodysplastic Syndrome
Interventions
Registration Number
NCT02279654
Lead Sponsor
Celgene
Brief Summary

This registry is a prospective, non-interventional, post authorisation safety study for patients diagnosed with Transfusion Dependent, IPSS low or intermediate-1-Risk Myelodysplastic Syndrome (MDS), associated to a single abnormality of the chromosome 5 \[del(5q)\].

The purpose of this study is to collect additional data about the safety of an oral drug (lenalidomide, Revlimid®) that may have been prescribed to relieve anemia and decrease the need of blood transfusions. However, also patients affected by the MDS del(5q) who receive other treatments different from lenalidomide can be included in this study, if they agree.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
389
Inclusion Criteria
  • Are ≥ 18 years old at the time of signing the Informed consent form (ICF)
  • Are transfusion dependent or have an history of transfusion dependence; for the purpose of the current Myelodysplastic syndromes (MDS) Post-authorization safety study (PASS), transfusion-dependence is defined as requiring ≥2 RBC units over an 8 week period prior to the date of signature on the ICF (due to MDS-related causes and not because of hemorrhage, trauma, or other acute cause)
  • Are on active treatment with lenalidomide (Lenalidomide Cohort) or have never been exposed to lenalidomide at the time of signing the ICF (Background Cohort)
  • Have confirmed diagnosis of IPSS low or intermediate-1-risk MDS with isolated del (5q) (with morphological and cytogenetic information) diagnosed on 15 June 2007 (date of Revlimid first approved in Europe) or later
Exclusion Criteria
  • Refuse to participate in the Myelodysplastic syndromes (MDS) Post-authorization safety study (PASS),
  • Are currently participating in an interventional therapeutic clinical trial for MDS (except for erythropoiesis-stimulating agents [ESAs] and granulocyte colonystimulating growth factors)
  • Receive any investigational agent the time of signing the ICF
  • Have previously been treated with lenalidomide and are no longer on active treatment with lenalidomide at the time of signing the ICF

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Arm && Interventions
GroupInterventionDescription
Lenalidomide PopulationLenalidomidePatients with transfusion-dependent, low- or intermediate (int)-1risk MDS and isolated del (5q) who receive at least 1 dose of lenalidomide after 15th June 2007 and have been followed up for on the registry for 3 years or until death/consent withdrawal
Background PopulationLenalidomideAll MDS patients who have been diagnosed on 15th June 2007 or later, have never been exposed to lenalidomide and have been followed up on the registry for 3 years or until death/consent withdrawal
Primary Outcome Measures
NameTimeMethod
Ascertain the Disease Progression to AML (through calculation of product limit estimators and incidence rates) for those with transfusion dependent Low to Intermediate 1 risk MDS del 5 q and have been treated with RevlimidUp to 3 years

Incidence, as well as the attributable risk (AR) and AR percent (%). Progressive Disease criteria includes increasing monoclonal paraprotein levels, bone marrow findings, worsening lytic bone disease, progressively enlarging extramedullary plasmacytomas, or hypercalcemia.

Overall Survival for patients with transfusion-dependent low to intermediate 1 risk MDS and isolated del (5q) and who have been treated with LenalidomideUp to 3 years

Number of MDS participants who survive

Secondary Outcome Measures
NameTimeMethod
Evaluate risk factors associated with progression of AMLUp to 3 years

Employ Cox proportional hazards models among MDS patients included in the primary population who have been treated with lenalidomide

Overall Survival for patients with transfusion-dependent low to intermediate 1 risk MDS and isolated del (5q) and who have been treated with LenalidomideUp to 3 years

Number of MDS participants who survive who have never been treated with Lenalidomide

Clinical practiceUp to 3 years

Provide insight into treatment regimens and therapy sequence in clinical practice as they relate to clinical outcomes (response, overall survival, progression-free survival) in patients in MDS participants

Adverse EventsUp to 3 years

Type, frequency, severity of advere events and relationship of adverse events to Lenalidomide. An adverse ecent is defined as any untoward medical occurrence in a patient administered a pharmaceutical product and which does not necessarily have a causal relationship with this treatment, ie, any unfavorable and unintended sign, symptom, or disease temporally associated with the use of a medicinal product whether or not considered related to the medicinal product

Trial Locations

Locations (146)

Local Institution - 0002

🇺🇸

Centre City, New Jersey, United States

Local Institution - France

🇺🇸

No City Provided, New Jersey, United States

Local Institution - 0001

🇺🇸

Centre City, New Jersey, United States

Local Institution - Denmark

🇺🇸

No City Provided, New Jersey, United States

Local Institution - Belgium

🇺🇸

No City Provided, New Jersey, United States

Local Institution - Germany

🇺🇸

No City Provided, New Jersey, United States

Local Institution - Greece

🇺🇸

No City Provided, New Jersey, United States

CHU Hôtel Dieu

🇫🇷

Angers, France

Hopital de L'archet I

🇫🇷

Nice, Alpes-Maritimes, France

Rokslide Hospital

🇩🇰

Roskilde, Denmark

CHU Nancy Brabois Adultes - 58 Allee dy morvan

🇫🇷

Vandoeuvre les Nancy, France

Gemeinschaftspraxis fur Hamatologie und Onkologie, Onkologisches zentrum Lebach

🇩🇪

Lebach, Germany

Innere Medizin II - Onkologie, Hämatologie, Univesitatklinikum Tubingen

🇩🇪

Tübingen, Germany

University Hospital of Alexandroupolis

🇬🇷

Alexandroupolis, Greece

Sahlgrenska University Hospital

🇸🇪

Göteborg, Sweden

Monkton, Wishaw and Hairmyres Hospitals

🇬🇧

East Kilbride, United Kingdom

Great Western Hospital

🇬🇧

Swindon, United Kingdom

University Hospital South Manc

🇬🇧

Manchester, United Kingdom

Hôpital St Louis

🇫🇷

Paris, France

Maidstone Hospital

🇬🇧

Maidstone, Kent, United Kingdom

U.O .C di Oncoematologia

🇮🇹

Mirano, Italy

Azienda Ospedaliera di Perugia

🇮🇹

Perugia, Italy

Univesita La Sapienza

🇮🇹

Roma, Italy

Ospedale Civile Santo Spirito

🇮🇹

Pescara, Italy

Presidio Ospedaliero "A. Torto

🇮🇹

Salerno, Italy

Policlinico "G.B. Rossi" Verona

🇮🇹

Veneto, Italy

Local Institution - Italy

🇺🇸

No City Provided, New Jersey, United States

Local Institution - Luxembourg

🇺🇸

No City Provided, New Jersey, United States

Local Institution - Norway

🇺🇸

No City Provided, New Jersey, United States

Århus University Hospital

🇩🇰

Aarhus, Denmark

Local Institution - Spain

🇺🇸

No City Provided, New Jersey, United States

Local Institution - Sweden

🇺🇸

No City Provided, New Jersey, United States

AZ Klina

🇧🇪

Brasschaat, Belgium

Local Institution - UK

🇺🇸

No City Provided, New Jersey, United States

AZ Sint Jan

🇧🇪

Brugge, Belgium

CHU Vésale

🇧🇪

Montigny- le- tilleul, Belgium

GHdCharleroi

🇧🇪

Charleroi, Belgium

Jessa Ziekenhuis

🇧🇪

Hasselt, Belgium

CHR Citadelle

🇧🇪

Liège, Belgium

Clinique Saint-Pierre Ottignie

🇧🇪

Ottignies, Belgium

Odense University Hospital

🇩🇰

Odense, Denmark

Aalborg Sygehus, Dept of Hematology

🇩🇰

Aalborg, Denmark

Herlev Hospital

🇩🇰

Herlev, Denmark

CHU Haut-Lévêque

🇫🇷

Pessac, Gironde, France

Institut Paoli Calmettes

🇫🇷

Marseille, Bouches-du-Rhône, France

Centre Hospitalier D'Avignon - Hopital Henri Duffaut

🇫🇷

Avignon, France

CH Chalon/Saone William Morey

🇫🇷

Chalon Sur Saone, France

CHU Grenoble

🇫🇷

La Tronche, France

CHRU De Lille - Hôpital Claude - Rue Michel Polonovski

🇫🇷

Lille, France

Centre Hospitalier Universitaire De Limoges - Hopital Dupuyt

🇫🇷

Limoges, France

CHU Hôtel Dieu - Place A Ricordeau

🇫🇷

Nantes, France

Centre Hospitalier Lyon-SUD [U

🇫🇷

Pierre- Bénite, France

Hopital de Hautepierre CHRU de Strasbourg

🇫🇷

Strasbourg, France

Hopital Purpan-Place du Dr. Baylac

🇫🇷

Toulouse, France

CHU Bretonneau

🇫🇷

Tours, France

Gemeinschaftspraxis Hämatologie-Onkologie

🇩🇪

Dresden, Germany

Onkologische Schwerpunktpraxis Bielefeld

🇩🇪

Bielefeld, Germany

Hämatologie und Onkologie, Klinikum Chemnitz gGmbH International Patient Center

🇩🇪

Chemnitz, Germany

HELIOS St. Johannes Klinik

🇩🇪

Duisburg, Germany

St Antonius Hospital (SAH)

🇩🇪

Eschweiler, Germany

Uniklinikum Düsseldorf, Klinik für Hämatologie, Onkologie und Klinische Immunologie

🇩🇪

Düsseldorf, Germany

Universitätsklinik Carl-Gustav

🇩🇪

Dresden, Germany

Marien Hospital Düsseldorf

🇩🇪

Düsseldorf, Germany

Kreiskrankenhaus St. Elisabeth - Von Werth-Str.

🇩🇪

Grevenbroich, Germany

Praxis, Onkologische Schwerpunktpraxis Dres. Verpoort

🇩🇪

Hamburg, Germany

Medizinische Hochschule Hannover

🇩🇪

Hannover, Germany

Institut für Versorgungsforschung in der Onkologie

🇩🇪

Koblenz, Germany

InVO Institut fur Versorgungsforschung

🇩🇪

Koblenz, Germany

Abteilung Hämatologie, Internistische Onkologie, Universitatklinikum Leipzig

🇩🇪

Leipzig, Germany

Gesellschaft für Medizinische

🇩🇪

Mönchengladbach, Germany

MLL Münchner Leukämielabor GmbH

🇩🇪

München, Germany

III. Medizinische Klinik, Hämatologie und internistische Onkologie , Univesitatsmedizin Mannheim

🇩🇪

Mannheim, Germany

III. Medizinische Klinik, Klinikum rechts der Isar der Technischen Universität München

🇩🇪

München, Germany

Klinik für Innere Medizin III

🇩🇪

Ulm, Germany

Rems-Murr-Klinikum Winnenden

🇩🇪

Winnenden, Germany

Gemeinschaftspraxis für Hämatologie und Onkologie

🇩🇪

Westerstede, Germany

General Hospital of Athens - LAIKO

🇬🇷

Athens, Greece

University General Hospital

🇬🇷

Athens, Greece

Universitätsklinikum Würzburg

🇩🇪

Würzburg, Germany

ZENTRUM FÜR INNERE MEDIZIN, Universitatklinikum Wurzburg

🇩🇪

Würzburg, Germany

University Hospital Of Herakli

🇬🇷

Herakleion - Crete, Greece

Georgios Gennimatos General Hospital

🇬🇷

Athens, Greece

University General Hospital of Ioannina

🇬🇷

Ioannina, Greece

University General Hospital of Larissa

🇬🇷

Larissa, Greece

G. Papanikolaou General Hospital

🇬🇷

Thessaloniki, Greece

Irccs Crob

🇮🇹

Rionero in Vulture, Potenza, Italy

University General Hospital of Patras

🇬🇷

Patras, Greece

AOU Ospedali Riuniti Umberto I G.M. Lancisi G. Salesi

🇮🇹

Ancona, Italy

Azienda Ospedaliera Papa Giovanni XX111 Piazza OMS

🇮🇹

Bergamo, Italy

AOU Careggi

🇮🇹

Firenze, Italy

U.O Ematologia con Trapianto

🇮🇹

Bari, Italy

Policlinico S.Orsola Malpighi, AOU di Bologna

🇮🇹

Bologna, Italy

Ospedale di Castelfranco Venet

🇮🇹

Castelfranco Veneto, Treviso, Italy

AO Spedali Civili di Brescia

🇮🇹

Brescia, Italy

Policlinico di Catania

🇮🇹

Catania, Italy

Azienda ospedaliero-universita

🇮🇹

Parma, Italy

Ospedale S. Luigi Gonzaga

🇮🇹

Orbassano, Italy

Arcispedale S.Maria Nuova

🇮🇹

Reggio Emilia, Italy

U.O Ematologia Azienda Ospedaliera

🇮🇹

Regio Calabria, Italy

Azienda Ospedaliera Universitaria di Sassari

🇮🇹

Sassari, Italy

AOU Policlinico Tor Vergata, Università Roma Tor Vergata

🇮🇹

Roma, Italy

A.O. Citta' della Salute e del

🇮🇹

Torino, Italy

Hospital Universitario de Gran Canaria Servicio de Hematología y

🇪🇸

Las Palmas de Gran Canaria, Canarias, Spain

Centre Hospitalier de Luxembourg

🇱🇺

Luxembourg, Luxembourg

H.U.Marq.Valdecilla, Hospital Universitario Marqués de Valdecilla. Hematología

🇪🇸

Santander, Cantabria, Spain

Haukeland Sykehus

🇳🇴

Bergen, Norway

Hospital costa del sol

🇪🇸

Marbella, Málaga, Spain

Hospital de Cruces

🇪🇸

Barakaldo, Spain

H.U. Ribera de Alzira

🇪🇸

Alzira, Spain

Instit Catalia D'Oncologia

🇪🇸

Barcelona, Spain

Hospital Virgen de Las Nieves

🇪🇸

Grenada, Spain

Department of Hematology, Hospital Duran i Reynals

🇪🇸

LLobregat, Spain

Hospital del Mar,Hematologia Hemotheropia

🇪🇸

Barcelona, Spain

Pauc Tauli

🇪🇸

Barcelona, Spain

Hospital Vall d'Hebron

🇪🇸

Barcelona, Spain

H. Clinic de Barcelona

🇪🇸

Barcelona, Spain

Hospital Reina Sofia

🇪🇸

Cordoba, Spain

Hospital Josep Trueta (ICO Girona)

🇪🇸

Girona, Spain

Hospital Universitario central de Asturias

🇪🇸

Oviedo, Spain

Hopsital Nuestra Senora de Valme

🇪🇸

Sevilla, Spain

Univesity Hospital de Salamanca

🇪🇸

Salamenca, Spain

Hospital Virgen Macarena

🇪🇸

Sevilla, Spain

Hospital Son Espaces

🇪🇸

Mallorca, Spain

Hospital Clinico Universitario de Valencia

🇪🇸

Valencia, Spain

Complejo Hospitalario Universitario de Santiago

🇪🇸

Santiago de Compostela, Spain

Hospital Virgen del Rocio

🇪🇸

Sevilla, Spain

Hospiral Universitario de la Fe

🇪🇸

Valencia, Spain

Länssjukhuset Kalmar

🇸🇪

Kalmar, Sweden

Karolinska University Hopsital

🇸🇪

Stockholm, Sweden

Lund University Hospital - Lasarettsgatan 23

🇸🇪

Lund, Sweden

Aberdeen Royal Infirmary - Foresterhill Road

🇬🇧

Aberdeen, United Kingdom

Queen Elizabeth Hospital

🇬🇧

Birmingham, United Kingdom

Pilgrim Hospital

🇬🇧

Boston, United Kingdom

Basildon and Thurrock Hospitals

🇬🇧

Essex, United Kingdom

Northwick Park Hospital

🇬🇧

Harrow, United Kingdom

Broomfield Hospital - Mid-Essex Hospitals NHS Trust

🇬🇧

Essex, United Kingdom

Aintree Hospital - Longmoor Lane

🇬🇧

Liverpool, United Kingdom

Lincoln county Hospital

🇬🇧

Lincoln, United Kingdom

Royal Oldham Hospital

🇬🇧

Oldham, United Kingdom

Radcliffe Hospitals and University - Headley Way, Headington

🇬🇧

Oxford, United Kingdom

Hospital Universitario Ramon Y Cajal

🇪🇸

Madrid, Spain

Hopsital Clinico San Carlos

🇪🇸

Madrid, Spain

Hospital Universitario fundacion Jiminez Diaz

🇪🇸

Madrid, Spain

Hospital Universitario 12 de Octobre

🇪🇸

Madrid, Spain

Hospital Universitario La Paz

🇪🇸

Madrid, Spain

H Universitario Puera de Hierro

🇪🇸

Madrid, Spain

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